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GZ402668

Phase 1

Progressive Multiple Sclerosis | Small molecule | Immunology |Sanofi|Last Updated: Apr 25, 2022

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDBiomarker
Total Trials2
Total Enrollment68
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT02977533A Single Ascending Dose Study of GZ402668 in Patients With Progressive Multiple SclerosisPHASE1 COMPLETED 20Dec 1, 2016May 16, 2018Apr 25, 20221 Germany
NCT02282826A First-in-human, Single Ascending Dose Study of GZ402668 in Patients With Progressive Multiple SclerosisPHASE1 COMPLETED 48Oct 1, 2014Mar 1, 2016Apr 13, 20161 Germany
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Study Endpoints
Primary Endpoints
Number of participants with treatment emergent adverse events
4 weeks
Secondary Endpoints
Assessment of PK parameter: maximum concentration (Cmax)
4 weeks
Assessment of PK parameter: area under curve (AUC)
4 weeks
Number of participants with lymphocyte depletion
4 weeks
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
GZ402668EXPERIMENTALDose 1 (up to a maximum optional Dose 2) will be given as a single subcutaneous administration under fed conditions. Acyclovir will be given twice daily starting on Day 1 and continuing for 28 days after investigational medicinal product administration.
PlaceboPLACEBO_COMPARATORA dose of matching placebo will be given as a single subcutaneous administration under fed conditions. Acyclovir will be given twice daily starting on Day 1 and continuing for 28 days after investigational medicinal product administration.
Dose 1 IVEXPERIMENTALGZ402668 dose 1 intravenous, single administration. Acyclovir 200 mg twice daily for 28 days as prophylactic therapy
Dose 2 IVEXPERIMENTALGZ402668 dose 2 intravenous, single administration. Acyclovir 200 mg twice daily for 28 days as prophylactic therapy
Dose 3 IVEXPERIMENTALGZ402668 dose 3 intravenous, single administration. Acyclovir 200 mg twice daily for 28 days as prophylactic therapy
Dose 3 SCEXPERIMENTALGZ402668 dose 3 subcutaneous, single administration. Acyclovir 200 mg twice daily for 28 days as prophylactic therapy
Dose 4 SCEXPERIMENTALGZ402668 dose 4 subcutaneous, single administration. Acyclovir 200 mg twice daily for 28 days as prophylactic therapy
Dose 5 SCEXPERIMENTALGZ402668 dose 5 subcutaneous, single administration. Acyclovir 200 mg twice daily for 28 days as prophylactic therapy
Placebo SCPLACEBO_COMPARATORplacebo subcutaneous, single administration. Acyclovir 200 mg twice daily for 28 days as prophylactic therapy
Placebo IVPLACEBO_COMPARATORplacebo intravenous, single administration. Acyclovir 200 mg twice daily for 28 days as prophylactic therapy
Interventions
NameTypeDescription
GZ402668DRUGPharmaceutical form: solution Route of administration: subcutaneous
PlaceboDRUGPharmaceutical form: solution Route of administration: subcutaneous
AcyclovirDRUGPharmaceutical form: tablet Route of administration: oral
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Eligibility Criteria
Age Range18 Years — 65 Years
SexALL
Healthy VolunteersNo
Study Sites1

Inclusion criteria : * Male or female adult with a diagnosis of progressive multiple sclerosis (MS) including primary progressive MS, secondary progressive MS, or progressive relapsing MS. * Aged between 18 and 65 years, inclusive. * Body weight greater than 40.0 kg. * Female patients of child bear...

Countries:Germany
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