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SNDX-5613

Phase 1

Acute Myeloid Leukemias | Small molecule | Oncology |Syndax Pharmaceuticals, Inc.|Last Updated: Feb 17, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment76
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT06226571A Study of SNDX-5613 in Combination With Intensive Chemotherapy in Participants With Acute Myeloid LeukemiasPHASE1 RECRUITING 76May 21, 2024Feb 1, 2027Feb 17, 202646 United States, Australia +4
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Study Endpoints
Primary Endpoints
Dose Escalation: Number of Participants with Dose-limiting Toxicities
Up to Day 42
Number of Participants with Treatment-emergent Adverse Events (TEAEs)
Day 1 through 30 days after final dose (up to approximately 3 years)
Secondary Endpoints
Maximum Plasma Concentration (Cmax) of SNDX-5613 and Relevant Metabolites
Predose through Day 15
Area Under the Plasma Concentration Versus Time Curve From Time 0 to t (AUC0-t) of SNDX-5613 and Relevant Metabolites
Predose through Day 15
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
SNDX-5613EXPERIMENTALDose Escalation: * Induction: Sequential cohorts of escalating dose levels of SNDX-5613 with chemotherapy regimen. * Consolidation: Cohorts will receive high-dose cytarabine (HiDAC) chemotherapy followed by SNDX-5613. * Maintenance Monotherapy: Cohorts will receive SNDX-5613. Dose Expansion: * Induction: SNDX-5613 at tolerated dose level with chemotherapy regimen. * Consolidation: Cohorts will receive SNDX-5613 with chemotherapy regimen and HiDAC. * Maintenance Monotherapy: Cohorts will receive SNDX-5613.
Interventions
NameTypeDescription
SNDX-5613DRUGParticipants will receive SNDX-5613 orally during Induction, Consolidation, and Maintenance until meeting criteria for discontinuation.
Chemotherapy RegimenDRUGInduction: Participants will receive an intravenous (IV), 2-drug combination of cytarabine and either daunorubicin or idarubicin.
HiDACDRUGConsolidation: Participants will receive HiDAC IV.
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Eligibility Criteria
Age Range18 Years — 75 Years
SexALL
Healthy VolunteersNo
Study Sites46

Inclusion Criteria: * Established, pathologically confirmed diagnosis of AML by World Health Organization 2022 criteria. * Previously untreated AML and eligible to receive intensive chemotherapy. * KMT2Ar, NPM1c, or NUP98r mutations identified by local laboratory prior to the first dose of SNDX-561...

Countries:United StatesAustraliaCanadaNetherlandsSpainUnited Kingdom
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT06226571primaryCompletionDate: changed
LOWMay 24, 2026NCT06226571studyFirstPostDate: changed