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ST-503

Phase 1

Chronic Neuropathic Pain | Gene therapy | Neurology |Sangamo Therapeutics, Inc.|Last Updated: Jun 1, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindSHAM_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment27
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT06980948Safety and Tolerability Study of ST-503 for Refractory Pain Due to Peripheral Neuropathy (Small Fiber Predominant, SFN)PHASE1 RECRUITING 27Dec 4, 2025Jul 1, 2028Jun 1, 202611 United States
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Study Endpoints
Primary Endpoints
Incidence and severity of treatment emergent adverse events (TEAEs)
12 weeks

To assess safety and tolerability of ST-503 over a 12-week post-dosing observation period.

Secondary Endpoints
Percentage of subjects with pain intensity reduction from baseline at Week 12
12 weeks
Percentage of subjects at Week 12
12 weeks
Columbia Suicide Severity Rating Scale (CSSRS) Rating
12 weeks
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Sham Controlled StudySHAM_COMPARATOR -
Investigational AgentEXPERIMENTAL -
Interventions
NameTypeDescription
ST-503GENETICGenomic Medicine
Sham (No Treatment)PROCEDURESham Procedure
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites11

Inclusion Criteria 1. Diagnostic characterization of Small Fiber Neuropathy (SFN) according to the Analgesic, Anesthetic, and Addiction Clinical Trial Translations, Innovations, Opportunities and Networks (ACTTION) criteria. 2. Medical record documentation that pain is refractory to 2 of 3 categori...

Countries:United States
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Recent Changes (Last 90 Days)
LOWJun 2, 2026NCT06980948lastUpdatePostDate: changed
LOWJun 2, 2026NCT06980948lastUpdatePostDate: changed
LOWJun 2, 2026NCT06980948lastUpdatePostDate: changed
LOWMay 26, 2026NCT06980948primaryCompletionDate: changed
LOWMay 24, 2026NCT06980948studyFirstPostDate: changed