Recent Updates
Recently added Catalysts

SB-728-T

Phase 1

HIV | Gene therapy | Infectious Disease |Sangamo Therapeutics, Inc.|Last Updated: May 24, 2021

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
CONTROLLEDDMCBiomarker
Total Trials2
Total Enrollment47
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01543152Dose Escalation Study of Cyclophosphamide in HIV-Infected Subjects on HAART Receiving SB-728-TPHASE1 COMPLETED 26Dec 1, 2011Jul 7, 2017May 24, 202111 United States, Puerto Rico
NCT01252641Study of Autologous T-cells Genetically Modified at the CCR5 Gene by Zinc Finger Nucleases in HIV-Infected SubjectsPHASE1 COMPLETED 21Nov 1, 2010May 1, 2015Sep 20, 20194 United States
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
Treatment-emergent Adverse Events
28 days after the SB-728-T infusion of the last subject in each Cohort and up to 12 months

Number of Participants with Treatment related Adverse Events in subjects who received any portion of the SB-728-T infusion

Evaluate the safety and tolerability of SB-728-T cells infusion in HIV-1 positive subjects
12 months

Evaluate the safety and tolerability of a single infusion of 5-30 billion SB-728-T cells in HIV-1 positive subjects

Secondary Endpoints
Effect of Escalating Doses of Cyclophosphamide on SB-728-T Engraftment as Measured by CCR5 Modified CD4 Cells in Blood.
Up to 12 months after the last SB-728-T infusion
Effect of SB-728-T on Plasma HIV-1 RNA Levels Following HAART Interruption
Up to 12 months after the last SB-728-T infusion
Change From Baseline to Month 12 in CD4+ T-cell Counts in Peripheral Blood After Repeat Treatments With SB-728-T. (i.e. Month 12 Value - Baseline Value)
Up to 12 months after the last SB-728-T infusion
Unlock Study Endpoints
Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Cohort 1 - IV cyclophosphamide 200 mgEXPERIMENTAL -
Cohort 2 - IV cyclophosphamide 0.5 g/m2EXPERIMENTAL -
Cohort 3 - IV cyclophosphamide 1.0 g/m2EXPERIMENTAL -
Cohort 4 - IV cyclophosphamide 2.0 g/m2EXPERIMENTAL -
Cohort 5 - IV cyclophosphamide 1.5 g/m2EXPERIMENTAL -
SB-728-TEXPERIMENTALSubjects will receive one intravenous infusion of SB-728-T
Interventions
NameTypeDescription
SB-728-TGENETICInfusion will be 5 to 30 billion ZFN modified CD4+ T cells 1 day following IV cyclophosphamide 200 mg
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites11

Inclusion Criteria: * Male or female, 18 years of age or older with documented HIV diagnosis within 10 years of screening. * Must be willing to comply with study-mandated evaluations; including discontinuation of current antiretroviral therapy during the treatment interruption. * Must have received...

Countries:United StatesPuerto Rico
Unlock Eligibility Criteria