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REC-994

Phase 2

Cerebral Cavernous Malformation | Small molecule | Neurology |Recursion Pharmaceuticals, Inc.|Last Updated: Jun 23, 2026

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment62

FDA Designations

ORPHAN_DRUG

Clinical trial landscape

REC-994 · 1 trial · 1 indication

Phase 2 1
NCT05085561The Symptomatic Cerebral Cavernous Malformation Trial of REC-994Cerebral Cavernous Malformation
COMPLETED62 Analytics
PHASE2COMPLETED
The Symptomatic Cerebral Cavernous Malformation Trial of REC-994
Cerebral Cavernous MalformationUnlock trial analytics

Study Endpoints

Primary Endpoints

Incidence and severity of adverse events (AEs)
Up to 24 months

Secondary Endpoints

Change in patient reported outcomes (Cerebral Cavernous Malformation Health Index)
Up to 24 months
Change in patient reported outcomes (Modified Rankin Scale)
Up to 24 months
Change in patient reported outcomes (SymptoMScreen Score)
Up to 24 months
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Study Design & Arms

AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
REC-994 200 mgACTIVE_COMPARATORREC-994 200 mg po once daily (QD) (1 200 mg REC-994 tablet, 1 matching placebo tablet)
REC-994 400 mgACTIVE_COMPARATORREC-994 400 mg po QD (2 200 mg REC-994 tablets)
PlaceboPLACEBO_COMPARATORMatching Placebo po QD (2 matching placebo tablets)

Interventions

NameTypeDescription
REC-994DRUGREC-994 200 mg tablets
PlaceboDRUGPlacebo Tablets
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites15

Inclusion criteria: 1. 18 years of age or older with anatomic CCM lesions demonstrated by brain MRI 2. Have symptomatic CCM 3. Have provided written informed consent to participate in the study 4. Have not participated in a clinical trial utilizing an investigational agent within 28 days or within ...

Countries:United States
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Recent Changes (Last 90 Days)

MEDIUMJul 24, 2026NCT05085561TRIAL_REMOVED: changed
MEDIUMJul 24, 2026NCT05085561TRIAL_REMOVED: changed

Frequently asked questions about REC-994

What is REC-994 used for?

REC-994 is an investigational small molecule being developed for the treatment of Cerebral Cavernous Malformation (CCM), a neurological condition characterized by abnormal clusters of blood vessels in the brain and spinal cord. It is currently in Phase 2 clinical development.

Who makes REC-994?

REC-994 is being developed by Recursion Pharmaceuticals, Inc., a biopharmaceutical company traded on the Nasdaq under the ticker symbol RXRX. The company is conducting clinical trials to evaluate the drug's safety and efficacy in patients with Cerebral Cavernous Malformation.

What phase is REC-994 in?

REC-994 is in Phase 2 clinical development. It has completed a Phase 2 trial, and it is not yet approved by the FDA. The drug has received Orphan Drug designation from the FDA for the treatment of Cerebral Cavernous Malformation.

What clinical trials is REC-994 in?

REC-994 has one completed Phase 2 clinical trial with the identifier NCT05085561, titled 'The Symptomatic Cerebral Cavernous Malformation Trial of REC-994.' This randomized, double-blind, placebo-controlled study enrolled 62 participants in the United States.

Is REC-994 FDA approved?

REC-994 is not FDA approved. It is an investigational drug currently in Phase 2 clinical development for Cerebral Cavernous Malformation. The FDA has granted it Orphan Drug designation, which provides incentives to support its development, but it has not yet received marketing approval.