Recent Updates
Recently added Catalysts

AOC-1020

Phase 3

Facioscapulohumeral Muscular Dystrophy | Small molecule | Neurology |Atrium Therapeutics, Inc.|Last Updated: May 29, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
Premium
Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
Premium
Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment200
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07038200A Study to Evaluate Del-brax (Also Referred to as AOC 1020) in Participants With FSHDPHASE3 RECRUITING 200Jun 10, 2025Jul 1, 2028May 29, 202646 United States, Canada +8
Unlock Drug Trial Details
Study Endpoints
Primary Endpoints
Quantitative Muscle Testing (QMT) composite score
Baseline through Week 78
Secondary Endpoints
10-Meter Walk/Run Test (10MWRT)
Baseline through Week 78
Timed Up-and-Go (TUG)
Baseline through Week 78
Patient-Reported Outcomes Measurement Information System (PROMIS) Physical Function Item Bank v2.0-Physical Function-Short Form 20a Questionnaire
Baseline through Week 78
Unlock Study Endpoints
Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
del-braxEXPERIMENTALDel-brax (AOC 1020) will be administered 13 times
placeboPLACEBO_COMPARATORSaline will be administered 13 times
Interventions
NameTypeDescription
AOC-1020DRUGPlacebo
PlaceboDRUGPlacebo will be administered by intravenous (IV) infusion.
Unlock Study Design Details
Eligibility Criteria
Age Range16 Years — 70 Years
SexALL
Healthy VolunteersNo
Study Sites46

Inclusion Criteria: * Clinical and genetic diagnosis of FSHD1 or FSHD2 * Ability to walk independently at pre-specified walking speed (orthoses and ankle braces allowed) for at least 10 meters at screening * Adequate muscle strength based on QMT composite score Exclusion Criteria: * Breastfeeding...

Countries:United StatesCanadaDenmarkFranceGermanyItalyJapanNetherlandsSpainUnited Kingdom
Unlock Eligibility Criteria
Recent Changes (Last 90 Days)
LOWMay 29, 2026NCT07038200lastUpdatePostDate: changed
LOWMay 29, 2026NCT07038200lastUpdatePostDate: changed
LOWMay 29, 2026NCT07038200lastUpdatePostDate: changed
LOWMay 26, 2026NCT07038200primaryCompletionDate: changed
LOWMay 24, 2026NCT07038200studyFirstPostDate: changed