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R348, 0.2%

Phase 2

Chronic Graft-versus-host Disease | Small molecule | Immunology |Rigel Pharmaceuticals, Inc.|Last Updated: Oct 10, 2016

Target and mechanism

ModalitySmall molecule

Also known as R348 Ophthalmic Solution, 0.2%

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment35

FDA Designations

No designations recorded

Clinical trial landscape

R348, 0.2% · 3 trials · 2 indications

Phase 2 2Phase 1 1
NCT02040623Safety and Efficacy Study of R932348 Ophthalmic Solution in Chronic Ocular Graft Versus Host Disease Patients(DROPS-2)Chronic Graft-versus-host Disease
COMPLETED35 Analytics
NCT01900249To Assess the Safety and Efficacy of R932348 Ophthalmic Solutions in Patients With Keratoconjunctivitis SiccaKeratoconjunctivitis Sicca
COMPLETED204 Analytics
PHASE2COMPLETED
Safety and Efficacy Study of R932348 Ophthalmic Solution in Chronic Ocular Graft Versus Host Disease Patients(DROPS-2)
Chronic Graft-versus-host DiseaseUnlock trial analytics
PHASE2COMPLETED
To Assess the Safety and Efficacy of R932348 Ophthalmic Solutions in Patients With Keratoconjunctivitis Sicca
Keratoconjunctivitis SiccaUnlock trial analytics

Study Endpoints

Primary Endpoints

Change From Baseline (Visit 1) of Total Corneal Fluorescein Staining Score at 12 Weeks.
Baseline to 12 weeks

Change from baseline (Visit 1) of total CFS score at 12 weeks. Total CFS score range 0-20, where '0' represents no fluorescein staining of any region and '20' represents severe staining the entire cornea.

Change of Corneal Fluorescein Staining of the Inferior Cornea Region.
Baseline to Week 12

Change from baseline (Visit 3) of inferior region CFS score at 12 weeks. Inferior region CFS score range 0-4, where '0' represents no fluorescein staining and '4' represents severe staining on the cornea.

Change in corneal fluorescein staining
Baseline and Visits 4, 8 and 12

Secondary Endpoints

Change in conjunctival lissamine green staining
Baseline and Visits 4, 8 and 12
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
R348 Ophthalmic Solution, 0.2%ACTIVE_COMPARATORR348 Ophthalmic Solution 0.2% 2 drops per eye twice a day
R348 Ophthalmic Solution, 0.5%ACTIVE_COMPARATORR348 Ophthalmic Solution, 0.5% 2 drops per eye twice a day
PlaceboPLACEBO_COMPARATORPlacebo Ophthalmic Solution 2 drops per eye twice a day
R348 Ophthalmic Solution, 1.0%ACTIVE_COMPARATORR348 Ophthalmic Solution, 1.0%, single (1 day) and multiple ascending dose (13 days) followed by a single dose on the fourteenth day.

Interventions

NameTypeDescription
R348 Ophthalmic Solution, 0.2%DRUGR348 Ophthalmic Solution 0.2% 2 drops per eye twice a day
R348 Ophthalmic Solution, 0.5%DRUGR348 Ophthalmic Solution, 0.5% 2 drops per eye twice a day
Placebo Ophthalmic SolutionOTHERPlacebo Ophthalmic Solution 2 drops per eye twice a day
PlaceboDRUGPlacebo Ophthalmic Solution 1 drop per eye twice a day for 12 weeks.
R348 Ophthalmic Solution, 1.0%DRUGR348 Ophthalmic Solution, 1.0%, single and multiple ascending dose
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Eligibility Criteria

Age Range18 Years to 85 Years
SexALL
Healthy VolunteersNo
Study Sites2

Inclusion Criteria: * Received an Allogeneic hematologic stem cell transplantation at least 3 months prior. * Subjects with post Allogeneic hematologic stem cell transplantation onset or worsening of dry eye symptoms for at least 1 month prior. * Use of over-the-counter and/or prescription eye drop...

Countries:United States
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Frequently asked questions about R348, 0.2%

What is R348, 0.2% used for?

R348, 0.2% is an investigational ophthalmic solution being studied for chronic graft-versus-host disease of the eye and keratoconjunctivitis sicca, also known as dry eye disease. Both are inflammatory conditions affecting the ocular surface. It is not approved for any indication and remains in clinical development.

Who is developing R348, 0.2%?

R348, 0.2% is being developed by Rigel Pharmaceuticals, Inc., which trades on the Nasdaq under the ticker RIGL. The company sponsored the Phase 1 and Phase 2 clinical trials of the ophthalmic solution in patients with ocular surface disease.

What phase is R348, 0.2% in?

R348, 0.2% has completed Phase 2 clinical development. Two Phase 2 trials and one Phase 1 trial have been completed, and no trials are currently active. The program has not advanced to Phase 3, and the drug is not approved for any indication.

What clinical trials is R348, 0.2% in?

R348, 0.2% has been evaluated in three completed trials: NCT02040623, a Phase 2 study in chronic ocular graft-versus-host disease; NCT01900249, a Phase 2 study in keratoconjunctivitis sicca; and NCT01733992, a Phase 1 safety, tolerability, and pharmacokinetics study in dry eye disease.

Is R348, 0.2% the same as R348 Ophthalmic Solution, 0.2%?

Yes, R348, 0.2% and R348 Ophthalmic Solution, 0.2% refer to the same investigational product. The trial records also list it as R932348 ophthalmic solution. All of these names describe the same Rigel Pharmaceuticals eye drop formulation evaluated in the completed Phase 1 and Phase 2 studies.

How was R348, 0.2% studied in clinical trials?

The R348, 0.2% trials were randomized, double-blind, and placebo-controlled, enrolling a total of 240 participants across the completed studies. Participants were adults 18 years and older, and the trials were conducted in the United States. The studies enrolled patients with chronic ocular graft-versus-host disease and keratoconjunctivitis sicca.