Recent Updates
Recently added Catalysts

Ruxolitinib

Phase 1

Myelofibrosis | Small molecule | Oncology |Roche Holding AG|Last Updated: May 11, 2018

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedDouble-BlindACTIVE_CONTROLLEDDMC
Total Trials1
Total Enrollment10

FDA Designations

No designations recorded

Clinical trial landscape

Ruxolitinib · 1 trial · 1 indication

Phase 1 1
NCT02593760A Study to Evaluate the Efficacy and Safety of Vismodegib in Combination With Ruxolitinib for the Treatment of Intermediate- or High-Risk Myelofibrosis (MF)Myelofibrosis
COMPLETED10 Analytics
PHASE1COMPLETED
A Study to Evaluate the Efficacy and Safety of Vismodegib in Combination With Ruxolitinib for the Treatment of Intermediate- or High-Risk Myelofibrosis (MF)
MyelofibrosisUnlock trial analytics

Study Endpoints

Primary Endpoints

Percentage of Participants who Achieve a Greater Than or Equal to (>=) 35% Reduction in Spleen Volume from Baseline at Week 24
Week 24

Determined by an Independent Review Committee (IRC) Using International Working Group-Myeloproliferative Neoplasms Research and Treatment (IWG-MRT) Revised Response Criteria

Percentage of Participants with Complete Remission (CR) and Partial Remission (PR) at Week 24, as Determined by an IRC Using IWG-MRT Revised Response Criteria
Week 24

Secondary Endpoints

Plasma Vismodegib Concentration at Steady State
Predose (0 hour) on Weeks 6, 12, 24, 36, and 48
Unbound Vismodegib Concentration at Steady State
Predose (0 hour) on Weeks 6, 12, 24, 36, and 48
Alpha 1-Acid Glycoprotein Concentration at Steady State
Predose (0 hour) on Weeks 6, 12, 24, 36, and 48
Unlock Study Endpoints

Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Placebo + RuxolitinibACTIVE_COMPARATORParticipants will receive placebo (PO QD) in combination with ruxolitinib (dose will depend on the participant's baseline platelet count) for up to 48 weeks.
Vismodegib + RuxolitinibEXPERIMENTALParticipants will receive vismodegib (150 mg PO QD) in combination with ruxolitinib (dose will depend on the participant's baseline platelet count) for up to 48 weeks.

Interventions

NameTypeDescription
PlaceboOTHERPlacebo will be administered PO QD for up to 48 weeks.
RuxolitinibDRUGRuxolitinib will be administered PO BID at a starting dose depending on the participants's baseline platelet count for up to 48 weeks.
VismodegibDRUGVismodegib will be administered at a dose of 150 mg PO QD for up to 48 weeks.
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites13

Inclusion Criteria: * Pathologically confirmed diagnosis of primary MF, post-polycythemia vera MF, or post-essential thrombocythemia MF, according to the 2008 revised World Health Organization criteria * Intermediate-1, intermediate-2, or high-risk according to the IWG-MRT Dynamic International Pro...

Countries:United StatesCanadaGermanyItaly
Unlock Eligibility Criteria

Frequently asked questions about Ruxolitinib

What is Ruxolitinib used for in myelofibrosis?

Ruxolitinib is an investigational small molecule being studied for the treatment of intermediate- or high-risk myelofibrosis. It is currently in Phase 1 clinical development. The drug is being evaluated in combination with vismodegib in a completed clinical trial.

Who makes Ruxolitinib?

Ruxolitinib is being developed by Roche Holding AG, which trades under the ticker RHHBY. The company is conducting clinical research on the drug for the treatment of myelofibrosis, a type of bone marrow cancer.

What phase is Ruxolitinib in?

Ruxolitinib is in Phase 1 clinical development. It is an investigational drug and has not been approved by regulatory authorities. A Phase 1 trial evaluating the drug in combination with vismodegib for myelofibrosis has been completed.

What clinical trials is Ruxolitinib in?

Ruxolitinib has been studied in one clinical trial, identified as NCT02593760. This Phase 1 study evaluated the efficacy and safety of vismodegib in combination with ruxolitinib for intermediate- or high-risk myelofibrosis. The trial enrolled 10 participants and has been completed.

Is Ruxolitinib the same as any other drug?

Ruxolitinib is a distinct drug candidate developed by Roche Holding AG. No alternative names for this drug have been disclosed in the available information. It is being studied specifically for the treatment of myelofibrosis.