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RO7428731

Phase 1

Glioblastoma | Small molecule | Oncology |Roche Holding AG|Last Updated: May 22, 2025

Success Probability

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Market & Valuation

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Trial Design

CONTROLLED
Total Trials1
Total Enrollment36

FDA Designations

No designations recorded

Clinical trial landscape

RO7428731 · 1 trial · 1 indication

Phase 1 1
NCT05187624A Study Evaluating the Safety, Pharmacokinetic and Anti-tumor Activity of RO7428731 in Participants With GlioblastomaGlioblastoma
COMPLETED36 Analytics
PHASE1COMPLETED
A Study Evaluating the Safety, Pharmacokinetic and Anti-tumor Activity of RO7428731 in Participants With Glioblastoma
GlioblastomaUnlock trial analytics

Study Endpoints

Primary Endpoints

Percentage of Participants with Adverse Events (AEs)
Up to the safety follow-up visit 60 days after the last treatment (up to approximately 15 months)
Percentage of Participants with Dose Limiting Toxicities (DLTs)
Cycle 1 (each cycle is 21 days)

Secondary Endpoints

Serum Concentration of RO7428731
Up to the safety follow-up visit 60 days after the last treatment (up to approximately 15 months)
Percentage of Participants With RO7428731 Anti-drug Antibodies (ADAs)
From baseline up to the safety follow-up visit 60 days after the last treatment (up to approximately 15 months)
Objective Response Rate (ORR)
From start of study treatment up to approximately 3 years
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Part I: Dose EscalationEXPERIMENTALParticipants with newly diagnosed GBM will receive RO7428731, intravenously (IV), up to one year or until disease progression, withdrawal of consent, unacceptable toxicity, or death, whichever occurs first.
Part II: Dose-Expansion(s)EXPERIMENTALParticipants with newly diagnosed GBM will receive RO7428731, IV, in maximum of two dose expansion cohorts at a dose(s) not exceeding the maximum tolerated dose (MTD) established in Part I.
Part III: Safety Run-inEXPERIMENTALParticipants with recurrent GBM will receive RO7428731, IV in a dosing schedule determined in Part I. At the end of the Safety Run-in period, a decision will be made as to whether to open the Dose-Expansion Cohort Part IVA or open a second Safety Run-in Cohort at a lower dose.
Part IV A: Dose-Expansions CohortEXPERIMENTALParticipants with recurrent GBM will receive RO7428731, IV at specified doses and dosing schedules.

Interventions

NameTypeDescription
RO7428731DRUGParticipants will receive RO7428731 as described.
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites8

Inclusion Criteria: Inclusion criteria for all participants: * Life expectancy of greater than or equal to 12 weeks, in the opinion of the Investigator * Diagnosis of GBM based on World Health Organization (WHO) classification of central nervous system (CNS) tumors, 5th edition * Participants must...

Countries:United StatesAustraliaCanadaDenmarkSpain
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Frequently asked questions about RO7428731

What is RO7428731 used for in glioblastoma?

RO7428731 is an investigational small molecule being studied for the treatment of glioblastoma, a type of brain cancer. It is currently in Phase 1 clinical development and has not been approved by regulatory authorities. The drug is being evaluated for its safety, pharmacokinetics, and anti-tumor activity in adult patients with glioblastoma.

Who makes RO7428731?

RO7428731 is being developed by Roche Holding AG, a multinational healthcare company. Roche's stock is traded under the ticker symbol RHHBY on the OTC market. The company is conducting clinical trials to evaluate the drug's potential as a treatment for glioblastoma.

What phase is RO7428731 in?

RO7428731 is in Phase 1 clinical development. A Phase 1 study has been completed, which focused on evaluating the safety, pharmacokinetics, and anti-tumor activity of the drug in participants with glioblastoma. The drug is still investigational and has not received FDA approval.

What clinical trials is RO7428731 in?

RO7428731 has one completed clinical trial registered under NCT05187624. This Phase 1 study evaluated the safety, pharmacokinetic, and anti-tumor activity of RO7428731 in participants with glioblastoma. The trial enrolled 36 participants across the United States, Australia, Canada, Denmark, and Spain.

Is RO7428731 FDA approved?

RO7428731 is not FDA approved. It is an investigational drug currently in Phase 1 clinical development for the treatment of glioblastoma. A Phase 1 study has been completed, but the drug has not yet received regulatory approval for any indication.

What is the mechanism of action of RO7428731?

RO7428731 is a small molecule being developed for the treatment of glioblastoma. The specific molecular target of this drug has not been disclosed in available information. It is currently in Phase 1 clinical trials to evaluate its safety and anti-tumor activity in patients with glioblastoma.