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RO7062931

Phase 1

Chronic Hepatitis B | Small molecule | Infectious Disease |Roche Holding AG|Last Updated: Dec 24, 2020

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindCONTROLLED
Total Trials1
Total Enrollment119

FDA Designations

No designations recorded

Clinical trial landscape

RO7062931 · 2 trials · 2 indications

Phase 1 2
NCT03505190A Study to Evaluate the Safety, Tolerability and Pharmacokinetics of RO7062931 in Healthy Chinese Volunteers.Healthy Participants
COMPLETED41 Analytics
NCT03038113A Study to Evaluate the Safety, Tolerability and Pharmacokinetics and Pharmacodynamics of RO7062931in Healthy Volunteers and Subjects With Chronic Hepatitis BChronic Hepatitis B
COMPLETED119 Analytics
PHASE1COMPLETED
A Study to Evaluate the Safety, Tolerability and Pharmacokinetics of RO7062931 in Healthy Chinese Volunteers.
Healthy ParticipantsUnlock trial analytics
PHASE1COMPLETED
A Study to Evaluate the Safety, Tolerability and Pharmacokinetics and Pharmacodynamics of RO7062931in Healthy Volunteers and Subjects With Chronic Hepatitis B
Chronic Hepatitis BUnlock trial analytics

Study Endpoints

Primary Endpoints

Percentage of Participants With Adverse Events and AEs of Special Interest
Up to 16 weeks

Adverse events of special interest for this study include the following: * Cases of an elevated ALT or AST in combination with either an elevated bilirubin or clinical jaundice * Suspected transmission of an infectious agent by the study drug * Severe injection site reactions * Renal adverse events

Percentage of Participants With Marked Laboratory Abnormalities Based on Hematology, Blood Chemistry, Coagulation and Urinalysis Test Results
Baseline, Day 2, 8, 15, 29, 85

Marked reference range has been predefined for each laboratory parameter. The marked reference range is broader than the standard reference range. Values falling outside the marked reference range that also represent a defined change from baseline will be considered marked laboratory abnormalities (i.e., potentially clinically relevant). If a baseline value is not available for a study subject, the midpoint of the standard reference range will be used as the study participant baseline value for the purposes of determining marked laboratory abnormalities.

Percentage of Participants With Electrocardiogram (ECG) Abnormalities
Baseline; pre-dose, 1 hour (h), 4, 8, 12h post-dose Day 1, 24h post-dose Day 2, 8, 15, 29, 85

Table entries provide the percentage of Participants with a during treatment assessment abnormality in the direction specified regardless of this abnormality at baseline. Abnormalities reported in Participants with missing baseline values are included. Baseline is the Participant's last observation prior to initiation of study drug.

Percentage of Participants With T-wave Abnormalities
Baseline; pre-dose, 1 hour (h), 4, 8, 12h post-dose Day 1, 24h post-dose Day 2, 8, 15, 29, 85

Table entries provide the percentage of Participants with a during treatment assessment abnormality in the direction specified regardless of this abnormality at baseline. Abnormalities reported in Participants with missing baseline values are included. Baseline is the Participant's last observation prior to initiation of study drug.

Percentage of Participants With U-wave Abnormalities
Baseline; pre-dose, 1 hour (h), 4, 8, 12h post-dose Day 1, 24h post-dose Day 2, 8, 15, 29, 85

Table entries provide the percentage of Participants with a during treatment assessment abnormality in the direction specified regardless of this abnormality at baseline. Abnormalities reported in Participants with missing baseline values are included. Baseline is the Participant's last observation prior to initiation of study drug.

Percentage of Participants With Adverse Events (AEs) and AEs of Special Interest
Up to day 113

An adverse event is any untoward medical occurrence in a participant administered a pharmaceutical product and which does not necessarily have to have a causal relationship with the treatment. An adverse event can therefore be any unfavorable and unintended sign (including an abnormal laboratory finding, for example), symptom, or disease temporally associated with the use of a pharmaceutical product, whether or not considered related to the pharmaceutical product. Preexisting conditions which worsen during a study are also considered as adverse events. AEs of Special Interest were defined as: i.) elevated ALT/AST in combination with elevated bilirubin/clinical jaundice, ii.) suspected transmission of infectious agent by the study drug, iii.) severe injection site reactions, iv.) ALT elevation ≥10x ULN, v.) creatinine elevation ≥1.5x ULN or ≥50% from baseline.

Percentage of Participants With Laboratory Abnormalities Based on Hematology, Blood Chemistry, Coagulation, and Urinalysis Test Results - Part 1
Screening, Days -1, 2, 8, 15, 29, 85

Marked reference range has been predefined for each laboratory parameter. The marked reference range is broader than the standard reference range. Values falling outside the marked reference range that also represent a defined change from baseline will be considered marked laboratory abnormalities (i.e., potentially clinically relevant). If a baseline value is not available for a study subject, the midpoint of the standard reference range will be used as the study participant baseline value for the purposes of determining marked laboratory abnormalities.

Percentage of Participants With Laboratory Abnormalities Based on Hematology, Blood Chemistry, Coagulation, and Urinalysis Test Results - Part 2
Screening, Days -1, 2, 8, 15, 29, at discontinuation, Days 36, 43, 57, 85, 113

Marked reference range has been predefined for each laboratory parameter. The marked reference range is broader than the standard reference range. Values falling outside the marked reference range that also represent a defined change from baseline will be considered marked laboratory abnormalities (i.e., potentially clinically relevant). If a baseline value is not available for a study subject, the midpoint of the standard reference range will be used as the study participant baseline value for the purposes of determining marked laboratory abnormalities.

Percentage of Participants With Electrocardiogram (ECG) Abnormalities Based on ECG Interpretation - Part 1
Day 1 (1,4,8,12h), Days 2 and 8, Follow Up Days 15, 29, 85

Participants were monitored for clinically-significant RO7062931-related ECG changes, defined as QTcF \> 500 msec, or \> 60 msec longer than the pre-dose baseline, within the first 48 hours post-dose.

Percentage of Participants With Electrocardiogram (ECG) Abnormalities Based on ECG Interpretation - Part 2
Day 1 (1,4,8h), Days 2,8,15,22 (1h and 8h), Day 23, Day 29 (1,4,8h), Day 30, Follow Up Days 36, 43, 50, 57, 78, 85, 106, 113

Participants were monitored for clinically-significant RO7062931-related ECG changes, defined as QTcF \> 500 msec, or \> 60 msec longer than the pre-dose baseline, within the first 48 hours post-dose.

Percentage of Participants With T-Wave Abnormalities Based on T-Wave Assessment - Part 1
Day 1 (1,4,8,12h), Days 2 and 8, Follow Up Days 15, 29, 85

Table entries provide the percentage of participants with abnormalities during treatment assessment. Abnormalities reported in participants with missing baseline values are included. Baseline is the Participant's last observation prior to initiation of study drug.

Percentage of Participants With U-Wave Abnormalities Based on U-Wave Assessment - Part 1
Day 1 (1,4,8,12h), Days 2 and 8, Follow Up Days 15, 29, 85

Table entries provide the percentage of participants with abnormalities during treatment assessment. Abnormalities reported in participants with missing baseline values are included. Baseline is the Participant's last observation prior to initiation of study drug.

Percentage of Participants With T-Wave Abnormalities Based on T-Wave Assessment - Part 2
Day 1 (1,4,8h), Days 2,8,15,22 (1h and 8h), Day 23, Day 29 (1,4,8h), Day 30, Follow Up Days 36, 43, 50, 57, 78, 85, 106, 113

Table entries provide the percentage of participants with abnormalities during treatment assessment. Abnormalities reported in participants with missing baseline values are included. Baseline is the Participant's last observation prior to initiation of study drug.

Percentage of Participants With U-Wave Based on U-Wave Assessment - Part 2
Day 1 (1,4,8h), Days 2,8,15,22 (1h and 8h), Day 23, Day 29 (1,4,8h), Day 30, Follow Up Days 36, 43, 50, 57, 78, 85, 106, 113

Table entries provide the percentage of participants with abnormalities during treatment assessment. Abnormalities reported in participants with missing baseline values are included. Baseline is the Participant's last observation prior to initiation of study drug.

Percentage of Participants With QTcF Values Between 450 Msec - 480 Msec - Part 2
Day 1 (1,4,8h), Days 2,8,15,22 (1h and 8h), Day 23, Day 29 (1,4,8h), Day 30, Follow Up Days 36, 43, 50, 57, 78, 85, 106, 113

Table entries provide the percentage of participants with abnormalities during treatment assessment. Abnormalities reported in participants with missing baseline values are included. Baseline is the Participant's last observation prior to initiation of study drug.

Secondary Endpoints

Maximum Plasma Concentration (Cmax) for RO7062931
Pre-dose, 0.25, 0.5, 1, 1.5, 2, 3, 4, 6, 8, 12, 18h post-dose Day 1, 24, 30, 36h post-dose Day 2, Day 3, 4, 5, 6, 8
Time to Reach Maximum Plasma Concentration (Tmax) for RO7062931
Pre-dose, 0.25, 0.5, 1, 1.5, 2, 3, 4, 6, 8, 12, 18h post-dose Day 1, 24, 30, 36h post-dose Day 2, Day 3, 4, 5, 6, 8
Area Under the Plasma Concentration-Time Curve From Time Zero to Infinity (AUC0-inf) for RO7062931
Pre-dose, 0.25, 0.5, 1, 1.5, 2, 3, 4, 6, 8, 12, 18h post-dose Day 1, 24, 30, 36h post-dose Day 2, Day 3, 4, 5, 6, 8
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Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
RO7062931 0.3mg/kgEXPERIMENTALParticipants will receive subcutaneously (SC) 0.3 milligram per kilogram (mg/kg) of RO7062931.
RO7062931 1.0mg/kgEXPERIMENTALParticipants will receive subcutaneously (SC) 1.0 milligram per kilogram (mg/kg) of RO7062931.
RO7062931 2.0mg/kgEXPERIMENTALParticipants will receive subcutaneously (SC) 2.0 milligram per kilogram (mg/kg) of RO7062931.
RO7062931 4.0mg/kgEXPERIMENTALParticipants will receive subcutaneously (SC) 4.0 milligram per kilogram (mg/kg) of RO7062931.
PlaceboPLACEBO_COMPARATORParticipants will receive matching placebo.
Part 1: Single-Ascending Dose (SAD)EXPERIMENTALHealthy volunteers will be enrolled in up to 8 cohorts with doses starting from 0.1 mg/kg and escalating sequentially after review of safety and pharmacokinetic (PK) data.
Part 2: Multiple Ascending DoseEXPERIMENTALParticipants with Chronic Hepatitis B will enrolled in Part 2. In Part 2a, participants will receive two monthly injections of either 3 doses equivalent to a multiple of the saturation dose or placebo in a 1:1:1:1 ratio. In Part 2b, a dose selected from Part 2a will be administered to participants randomized into 4 cohorts where they will be dosed weekly (QW) or bi-weekly (Q2W). Each of the cohorts in Part 2b will include participants receiving active drug or placebo in a 3:1 ratio. In Part 2c, NUC-suppressed CHB participants will receive either RO7062931+NUC for up to 24 weeks, or RO7062931+NUC+an immune modulator for up to 48 weeks, at a dose determined from Part 2a and 2b. Part 2c may also enroll treatment-naive immune-active CHB participants.

Interventions

NameTypeDescription
RO7062931DRUGRO7062931 will be administered SC in single ascending doses with starting of 0.3 mg/kg and subsequent doses of 1.0 mg/kg, 2.0 mg/kg and 3.0 mg/kg, respectively. Additional (optional) dose of 4.0 mg/kg may be administered based on safety, tolerability and PK data.
PlaceboDRUGMatching placebo will be administered subcutaneously (SC).
Immune ModulatorDRUGParticipants in Part 2c will receive an immune modulator subcutaneously QW for up to 48 weeks.
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Eligibility Criteria

Age Range18 Years to 60 Years
SexALL
Healthy VolunteersYes
Study Sites2

Inclusion Criteria: * Chinese healthy male and female (of non-childbearing potential) volunteers. * A Body Mass Index (BMI) between 19 to 27 kilogram per square meter (kg/m2) inclusive and a body weight of at least 45 kg. * Women should be of non-childbearing potential. These include those who have...

Countries:Hong KongAustraliaNew ZealandSingaporeSouth KoreaTaiwanThailand
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Frequently asked questions about RO7062931

What is RO7062931 used for?

RO7062931 is an investigational small molecule being studied for use in chronic hepatitis B and in healthy participants. It is in Phase 1 clinical development by Roche Holding AG (ticker: RHHBY). The drug is not approved and remains under investigation for safety, tolerability, and pharmacokinetics.

Who makes RO7062931?

RO7062931 is being developed by Roche Holding AG, which trades under the ticker RHHBY. The drug is an investigational small molecule in Phase 1 clinical development for chronic hepatitis B and healthy participants. Roche is conducting clinical trials to evaluate its safety and pharmacokinetics.

What phase is RO7062931 in?

RO7062931 is in Phase 1 clinical development. It is an investigational small molecule being studied for chronic hepatitis B and in healthy participants. The drug is not FDA approved and remains in early-stage clinical trials to assess safety, tolerability, and pharmacokinetics.

What clinical trials is RO7062931 in?

RO7062931 has been studied in two completed Phase 1 trials. NCT03038113 evaluated safety, tolerability, pharmacokinetics, and pharmacodynamics in healthy volunteers and subjects with chronic hepatitis B across multiple countries. NCT03505190 evaluated safety, tolerability, and pharmacokinetics in healthy Chinese volunteers in Hong Kong.

Is RO7062931 the same as any other drug?

RO7062931 is the primary name for this investigational small molecule being developed by Roche Holding AG. No alternative names have been reported for this drug. It is being studied in Phase 1 clinical trials for chronic hepatitis B and in healthy participants.