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RO4917523

Phase 2

Depression | Small molecule | Psychiatry |Roche Holding AG|Last Updated: Nov 2, 2016

Success Probability

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment46

FDA Designations

No designations recorded

Clinical trial landscape

RO4917523 · 11 trials · 4 indications

Phase 2 5Phase 1 6
NCT01750957A Study of RO4917523 in Pediatric Patients With Fragile X SyndromeFragile X Syndrome
COMPLETED47 Analytics
NCT01517698A Study of RO4917523 in Patients With Fragile X SyndromeFragile X Syndrome
COMPLETED185 Analytics
NCT01437657MARIGOLD Study: A Study of RO4917523 Versus Placebo as Adjunctive Therapy in Patients With Major Depressive Disorder and an Inadequate Response to Ongoing Antidepressant TherapyMajor Depressive Disorder
COMPLETED319 Analytics
NCT01015430A Study With RO4917523 in Patients With Fragile X SyndromeFragile X Syndrome
COMPLETED40 Analytics
NCT00809562A Study of RO4917523 in Patients With Treatment Resistant DepressionDepression
COMPLETED46 Analytics
PHASE2COMPLETED
A Study of RO4917523 in Pediatric Patients With Fragile X Syndrome
Fragile X SyndromeUnlock trial analytics
PHASE2COMPLETED
A Study of RO4917523 in Patients With Fragile X Syndrome
Fragile X SyndromeUnlock trial analytics
PHASE2COMPLETED
MARIGOLD Study: A Study of RO4917523 Versus Placebo as Adjunctive Therapy in Patients With Major Depressive Disorder and an Inadequate Response to Ongoing Antidepressant Therapy
Major Depressive DisorderUnlock trial analytics
PHASE2COMPLETED
A Study With RO4917523 in Patients With Fragile X Syndrome
Fragile X SyndromeUnlock trial analytics
PHASE2COMPLETED
A Study of RO4917523 in Patients With Treatment Resistant Depression
DepressionUnlock trial analytics

Study Endpoints

Primary Endpoints

Safety: Incidence of adverse events
15 weeks
Change in Anxiety Depression and Mood Scale (ADAMS) total score
12 weeks
Safety (incidence of adverse events)
12 weeks
Change in Montgomery Asberg Depression Rating Scale (MADRS)
From baseline to Week 6
Safety, Tolerability and Pharmacokinetics: AEs, laboratory parameters
AEs throughout study; laboratory assessments: days 1, 8, 15, 29, 43
Safety and tolerability: Adverse events, ECGs, laboratory parameters,vital signs
Throughout study
Pharmacokinetics: Area under the concentration-time curve (AUC)
Pre-dose and up to 144 hours post-dose
Pharmacokinetics: Maximum concentration (Cmax)
Pre-dose and up to 144 hours post-dose
Pharmacokinetics: Area under the concentration time curve
Period 1: Pre-dose and up to Day 14, Period 2: Pre-dose and up to Day 29
Elimination: urinary and fecal recovery of total radioactivity
Pre-dose and up to approximately Day 18 post-dose
Plasma concentrations of RO4917523
Pre-dose and up to approximately Day 18 post-dose
Part I: mGlu5 receptor binding of [11C]-RO5011232 radiotracer in human brain, assessed by positron emission tomography (PET)
approximately 6 months
Part II: Dosimetry/radiation safety of [11C]-RO5011232 assessments by whole body PET scan
approximately 6 months
Part III: Measurement of test-retest precision of PET images of regions of interest in the human brain
approximately 6 months
Part IV: Correlation between RO4917523 plasma concentration and R04917523 binding to mGlu5 receptor in brain
approximately 6 months
Part 1: Pharmacokinetics: Area under the concentration - time curve (AUC) (single/multiple oral dose in healthy Japanese subjects)
approximately 12 weeks
Part 2: Comparison of pharmacokinetics (area under the concentration - time curve [AUC]) between healthy Caucasian and Japanese subjects after 14 days of daily oral dosing
approximately 9 weeks
Safety: Incidence of adverse events in Japanese an Caucasian subjects
approximately 21 weeks
To evaluate the ability of fMRI to detect and characterize the effect of the three drugs on brain activity at rest and during emotional stimuli
8 weeks

Secondary Endpoints

Efficacy: Neuropsychological/behavioral assessment scales (ADAMS/Clinical Global Impressions CGI-S, CGI-I/ GBAS/Aberrant Behavior Checklist ABC/Repeatable Battery for the Assessment of Neuropsychological Status RBANS/VAS behavior)
15 weeks
Pharmacokinetics: Clearance (CL/F)
up to Week 12
Pharmacokinetics: Volume of distribution at steady-state (Vss/F)
up to Week 12
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Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
PlaceboPLACEBO_COMPARATOR -
RO4917523 Dose AEXPERIMENTAL -
RO4917523 Dose BEXPERIMENTAL -
RO4917523 0.5 mgEXPERIMENTAL -
RO4917523 1.5 mgEXPERIMENTAL -
Placebo (for RO4917523 ascending doses)PLACEBO_COMPARATOR -
Placebo (for RO4917523 fixed dose)PLACEBO_COMPARATOR -
RO4917523 ascending dosesEXPERIMENTAL -
RO4917523 fixed doseEXPERIMENTAL -
1EXPERIMENTAL -
2PLACEBO_COMPARATOR -
Fast release MR capsuleEXPERIMENTAL -
Slow release MR capsuleEXPERIMENTAL -
Target release MR capsuleEXPERIMENTAL -
Dosing Period 1EXPERIMENTAL -
Dosing Period 2EXPERIMENTAL -
[14C]-labeled RO4917523EXPERIMENTAL -
Concept ProofACTIVE_COMPARATOR -
Receptor OccupancyEXPERIMENTAL -
Part 1EXPERIMENTAL -
Part 2EXPERIMENTAL -

Interventions

NameTypeDescription
PlaceboDRUGorally daily, 12 weeks
RO4917523DRUGDose A orally daily, 12 weeks
RO4917523 0.5 mgDRUG0.5 mg orally once a day for 12 weeks
RO4917523 1.5 mgDRUG1.5 mg orally once a day for 12 weeks
Placebo (for RO4917523 ascending doses)DRUGPlacebo daily po
Placebo (for RO4917523 fixed dose)DRUGPlacebo daily po
CarbamazepineDRUGMultiple doses of carbamazepine
RO5011232DRUG\[11C\]-RO5011232 intravenously
escitalopramDRUGOral single dose
methylphenidateDRUGOral single dose
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Eligibility Criteria

Age Range5 Years to 13 Years
SexALL
Healthy VolunteersNo
Study Sites20

Inclusion Criteria: * Children and adolescents, 5 to 13 years of age * Diagnosis of fragile X syndrome based on prior DNA testing confirming Fragile X Mental Retardation 1 (FMR1) full mutation and qualifying scores on the ABC and CGI-S Exclusion Criteria: * Previous treatment with another mGlu5 r...

Countries:United StatesArgentinaCanadaChileFranceMexicoPeruSpainSwedenUnited KingdomGermanyJapanPolandRomaniaRussiaTaiwanNetherlands
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Frequently asked questions about RO4917523

What is RO4917523 used for?

RO4917523 is an investigational small molecule being studied for Fragile X Syndrome and Major Depressive Disorder. It has been evaluated in Phase 2 clinical trials as an adjunctive therapy in patients with Major Depressive Disorder who had an inadequate response to ongoing antidepressant therapy, and in patients with Fragile X Syndrome.

Who makes RO4917523?

RO4917523 is being developed by Roche Holding AG, which trades under the ticker RHHBY. The company has sponsored multiple clinical trials of this investigational drug in Fragile X Syndrome and Major Depressive Disorder.

What phase is RO4917523 in?

RO4917523 is in Phase 2 clinical development. All six trials listed for this drug are Phase 2 studies, and all have been completed. The drug is investigational and has not been approved by regulatory authorities.

What clinical trials is RO4917523 in?

RO4917523 has been studied in several completed Phase 2 trials, including NCT01015430 and NCT01517698 in Fragile X Syndrome, NCT01750957 in pediatric Fragile X Syndrome, and NCT01437657, the MARIGOLD study, in Major Depressive Disorder. These trials enrolled a total of 319 participants.

Is RO4917523 the same as basimglurant?

RO4917523 is also known as basimglurant. It is an investigational small molecule developed by Roche. The drug has been evaluated in clinical trials for Fragile X Syndrome and Major Depressive Disorder, but it is not approved for any indication.