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Nucleoside

Phase 2

Hepatitis B, Chronic | Small molecule | Infectious Disease |Roche Holding AG|Last Updated: Sep 19, 2025

Success Probability

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Market & Valuation

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Trial Design

RandomizedACTIVE_CONTROLLED
Total Trials1
Total Enrollment281

FDA Designations

No designations recorded

Clinical trial landscape

Nucleoside · 1 trial · 1 indication

Phase 2 1
NCT04225715A Trial To Evaluate The Efficacy And Safety Of Multiple Combination Therapies In Participants With Chronic Hepatitis BHepatitis B, Chronic
COMPLETED281 Analytics
PHASE2COMPLETED
A Trial To Evaluate The Efficacy And Safety Of Multiple Combination Therapies In Participants With Chronic Hepatitis B
Hepatitis B, ChronicUnlock trial analytics

Study Endpoints

Primary Endpoints

Percentage of Participants With Hepatitis B Surface Antigen (HBsAg) Loss at 24 Weeks Post-End of Treatment (EOT)
Follow-up Week (FUW) 24

HBsAg loss was defined as quantitative HBsAg \<0.05 international units/milliliters (IU/mL). The percentage of participants with HBsAg loss was calculated as number of participants with HBsAg loss / total number of participants \*100. 95% confidence interval (CI) was calculated using the Clopper-Pearson method. Percentages have been rounded off.

Secondary Endpoints

Percentage of Participants With HBsAg Loss
Combos 1 and 5: Weeks 24, 36, 48 and FUW 48; Combos 2, 3, 4, 6 and NUC Arm: Week 48 and FUW 48; Combo 7: Week 24; Combo 8: Week 36
Percentage of Participants With HBsAg Seroconversion
Combos 1 and 5: Weeks 24, 36, 48, FUW 24 and FUW 48; Combos 2, 3, 4, 6 and NUC Arm: Week 48, FUW 24 and FUW 48; Combo 7: Week 24 and FUW 24; Combo 8: Week 36 and FUW 24
Percentage of Participants With Hepatitis B Early Antigen (HBeAg) Loss in Baseline HBeAg-positive Participants
Weeks 12, 24, 36, and 48; FUW 12, 24, 36, and 48
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Nucleos(t)ide (NUC) Control ArmACTIVE_COMPARATORParticipants will continue their background NUC therapy for the 48-week treatment period. At the end of the treatment period, in line with current CHB treatment guidelines, participants will continue NUC treatment during the follow-up unless the NUC discontinuation criteria have been met.
Core Protein Allosteric Modulator (CpAM; RO7049389) + Toll-like Receptor 7 (TLR7;RO7020531) + NUCEXPERIMENTALParticipants will receive RO7049389 (600 mg once daily \[QD\]) in addition to their background NUC therapy for the 48-week treatment period. RO7020531 (150 mg once every other day \[QOD\]) will be administered during Weeks 1-12 and Weeks 25-36. At the end of the treatment period, participants will continue NUC treatment during the follow-up unless the NUC discontinuation criteria have been met.
Short Interfering Ribonucleic acid (siRNA; RO7445482) (Dose1) + NUCEXPERIMENTALParticipants will receive RO7445482 (Dose 1) in addition to their background NUC therapy for the 48-week treatment period. At the end of the treatment period, participants will continue NUC treatment during the follow-up unless the NUC discontinuation criteria have been met.
siRNA (RO7445482) (Dose 2) + NUCEXPERIMENTALParticipants will receive RO7445482 (Dose 2) in addition to their background NUC therapy for the 48-week treatment period. At the end of the treatment period, participants will continue NUC treatment during the follow-up unless the NUC discontinuation criteria have been met.
siRNA (RO7445482) + Pegylated Interferon (PEG-IFN) + NUCEXPERIMENTALParticipants will receive RO7445482 (Dose 2) in addition to their background NUC therapy for the 48-week treatment period. PEG-IFN will be administered at a dose of 180 μg once weekly (QW) for 48 weeks. At the end of the treatment period, participants will continue NUC treatment during the follow-up unless the NUC discontinuation criteria have been met.
siRNA (RO7445482) + CpAM (RO7049389) + NUCEXPERIMENTALParticipants will receive RO7445482 (Dose 2) and RO7049389 (600 mg QD) in addition to their background NUC therapy for the 48-week treatment period. At the end of the treatment period, participants will continue NUC treatment during the follow-up unless the NUC discontinuation criteria have been met.
siRNA (RO7445482) + TLR7 (RO7020531) + NUCEXPERIMENTALParticipants will receive RO7445482 (Dose 2) in addition to their background NUC therapy for the 48-week treatment period. RO7020531 (150 mg QOD) will be administered during Weeks 13-24 and Weeks 37-48 (i.e., 2 treatment cycles of 12 weeks' duration each and 42 doses of RO7020531 for each cycle). At the end of the treatment period, participants will continue NUC treatment during the follow-up unless the NUC discontinuation criteria have been met.
siRNA(RO7445482)+ Programmed Death Ligand-1 Locked Nucleic Acid (PD-L1 LNA; RO7191863) + NUC [1]EXPERIMENTALParticipants will receive RO7445482 (Dose 2) during Weeks 1-24 and RO7191863 (Dose 1) will be administered during Weeks 13-24, in addition to their background NUC therapy for the 24-week treatment period. At the end of the treatment period, participants will continue NUC treatment during the follow-up unless the NUC discontinuation criteria have been met.
siRNA (RO7445482) + PD-L1 LNA (RO7191863) + NUC [2]EXPERIMENTALParticipants will receive RO7445482 (Dose 2) during Weeks 1-24 and RO7191863 (Dose 1) will be administered during Weeks 25-36, in addition to their background NUC therapy for the 36-week treatment period. At the end of the treatment period, participants will continue NUC treatment during the follow-up unless the NUC discontinuation criteria have been met.

Interventions

NameTypeDescription
Nucleos(t)ide (NUC)DRUGNucleos(t)ide (NUC) will be administered orally
CpAM (RO7049389)DRUGCpAM (RO7049389) will be administered orally
TLR7 (RO7020531)DRUGTLR7 (RO7020531) will be administered orally
siRNA (RO7445482)DRUGsiRNA (RO7445482) will be administered subcutaneously
PEG-IFNDRUGPEG-IFN will be administered subcutaneously
PD-L1 LNA (RO7191863)DRUGPD-L1 LNA (RO7191863) will be administered subcutaneously
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Eligibility Criteria

Age Range18 Years to 65 Years
SexALL
Healthy VolunteersNo
Study Sites33

Inclusion Criteria: * Body mass index between 18 and 32 kg/m2 inclusive. * Participants with Chronic Hepatitis B (CHB) infection (HBsAg positive for \>=6 months) who are on established NUC (entecavir or tenofovir alafenamide/disoproxil fumarate) monotherapy for \>=12 months, having received the sam...

Countries:BulgariaCanadaChileChinaFranceHong KongNew ZealandRomaniaSouth KoreaSpainTaiwanThailandUnited Kingdom
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Frequently asked questions about Nucleoside

What is Nucleoside used for in chronic hepatitis B?

Nucleoside is an investigational small molecule being studied for the treatment of chronic hepatitis B. It is being developed by Roche Holding AG (ticker: RHHBY) and is currently in Phase 2 clinical development. The drug is intended to address the infectious disease, which affects the liver.

Who makes Nucleoside?

Nucleoside is being developed by Roche Holding AG, a pharmaceutical company traded under the ticker RHHBY. The drug is currently in Phase 2 clinical trials for the treatment of chronic hepatitis B. Roche is conducting research to evaluate the efficacy and safety of this investigational small molecule.

What phase is Nucleoside in?

Nucleoside is in Phase 2 clinical development. It is an investigational small molecule being studied for the treatment of chronic hepatitis B. The drug has not yet been approved and remains in clinical trials to assess its safety and efficacy in patients with this condition.

What clinical trials is Nucleoside in?

Nucleoside was studied in a Phase 2 clinical trial registered as NCT04225715. This completed trial evaluated the efficacy and safety of multiple combination therapies in participants with chronic hepatitis B. The study enrolled 281 participants across 13 countries, including Bulgaria, Canada, Chile, China, France, Hong Kong, New Zealand, Romania, South Korea, Spain, Taiwan, Thailand, and the United Kingdom.

Is Nucleoside the same as any other drug?

Nucleoside is the drug name used in clinical development by Roche Holding AG. No alternative names have been reported for this investigational compound. It is being studied specifically for chronic hepatitis B and is currently in Phase 2 trials.