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Mycophenolate Mofetil/Day

Phase 3

Pemphigus Vulgaris (PV) | Small molecule | Dermatology |Roche Holding AG|Last Updated: Jun 22, 2011

Target and mechanism

Molecular targetIMPDH1, IMPDH2
Target classInhibitor
ModalitySmall molecule

Also known as Mycophenolate Mofetil

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment96

FDA Designations

No designations recorded

Clinical trial landscape

Mycophenolate Mofetil/Day · 1 trial · 1 indication

Phase 3 1
NCT00683930A Study to Assess the Effect of CellCept (Mycophenolate Mofetil) and Reduced Corticosteroids in Patients With Active Pemphigus Vulgaris (PV)Pemphigus Vulgaris (PV)
COMPLETED96 Analytics
PHASE3COMPLETED
A Study to Assess the Effect of CellCept (Mycophenolate Mofetil) and Reduced Corticosteroids in Patients With Active Pemphigus Vulgaris (PV)
Pemphigus Vulgaris (PV)Unlock trial analytics

Study Endpoints

Primary Endpoints

Percentage of Patients Achieving Responder Status at Week 52
52 weeks

The proportion of subjects achieving responder status (defined as no new persistent lesions and prednisone dose of not more than 10 mg/day from Week 48 until study termination at Week 52) in the two active treatment groups combined (2 g/day and 3 g/day mycophenolate mofetil) compared with the placebo group

Secondary Endpoints

Time to Initial Response
up to 52 weeks
Time to Sustained Response
up to 52 weeks
Duration of Prednisone Maintenance Dosing
52 weeks
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Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Mycophenolate Mofetil (MMF) 2 g/DayEXPERIMENTALMycophenolate mofetil 500 mg tablets; 4 tablets twice daily for 52 weeks
Mycophenolate Mofetil (MMF) 3 g/DayEXPERIMENTALMycophenolate mofetil 500 mg tablets; 6 tablets twice daily for 52 weeks
PlaceboPLACEBO_COMPARATOR -

Interventions

NameTypeDescription
Mycophenolate Mofetil 2 g/DayDRUGMycophenolate mofetil 500 mg tablets; 4 tablets twice daily for 52 weeks
Mycophenolate Mofetil (MMF) 3 g/DayDRUGMycophenolate mofetil 500 mg tablets; 6 tablets twice daily for 52 weeks
PlaceboDRUGPlacebo for MMF 2 g/day group: 4 tablets orally twice daily for 52 weeks; placebo for MMF 3 g/day group: 6 tablets orally twice daily for 52 weeks
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Eligibility Criteria

Age Range18 Years to 70 Years
SexALL
Healthy VolunteersNo
Study Sites26

Inclusion Criteria: * Adult patients 18 to 70 years of age * Diagnosis of mild to moderate pemphigus vulgaris within the past 12 months, requiring high dose corticosteroids Exclusion Criteria: * Female patients who are pregnant, breastfeeding, or lactating * Regularly scheduled plasma exchange (P...

Countries:United StatesCanadaGermanyIsraelSwitzerlandTurkey (Türkiye)UkraineUnited Kingdom
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Frequently asked questions about Mycophenolate Mofetil/Day

What is Mycophenolate Mofetil used for?

Mycophenolate Mofetil is an immunosuppressant small molecule being studied for use in Pemphigus Vulgaris, Myelodysplastic Syndromes, Chronic Kidney Failure, Heart Transplantation, and Lung Transplantation. It is developed by Roche Holding AG (RHHBY) and is currently in Phase 3 clinical development for these indications.

What does Mycophenolate Mofetil target?

Mycophenolate Mofetil is an immunosuppressant that inhibits inosine monophosphate dehydrogenase, an enzyme crucial for the de novo synthesis of guanine nucleotides in lymphocytes. By blocking this enzyme, it selectively suppresses T and B cell proliferation, reducing the immune response that contributes to autoimmune and transplant-related conditions.

Who makes Mycophenolate Mofetil?

Mycophenolate Mofetil is developed by Roche Holding AG, a Swiss multinational healthcare company traded on the OTC market under the ticker RHHBY. Roche is conducting clinical trials to evaluate the drug's efficacy and safety in various conditions, including heart transplantation and myelodysplastic syndromes.

What phase is Mycophenolate Mofetil in?

Mycophenolate Mofetil is in Phase 3 clinical development. It has completed three trials, including two Phase 3 studies and one Phase 2 study, with a total enrollment of 640 participants. The drug is investigational and not yet approved for the studied indications.

What clinical trials is Mycophenolate Mofetil in?

Mycophenolate Mofetil has been studied in three completed trials: NCT00282347 (Phase 3, Lupus Nephritis, 144 participants), NCT00551291 (Phase 2, Myelodysplastic Syndromes, 10 participants), and NCT02091414 (Phase 3, Heart Transplantation, 36 participants). All trials are completed with no active studies ongoing.

Is Mycophenolate Mofetil the same as CellCept?

Yes, Mycophenolate Mofetil is the same as CellCept, a brand name used in clinical trials. In the study NCT00551291, the drug is referred to as CellCept, and in NCT02091414, it is also called CellCept. Both names refer to the same immunosuppressant compound developed by Roche.