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RGLS4326

Phase 1

Polycystic Kidney Disease, Autosomal Dominant | Small molecule | Nephrology |Regulus Therapeutics Inc.|Last Updated: Dec 15, 2021

Success Probability

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Market & Valuation

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Trial Design

CONTROLLED
Total Trials1
Total Enrollment19

FDA Designations

No designations recorded

Clinical trial landscape

RGLS4326 · 1 trial · 1 indication

Phase 1 1
NCT04536688A Study of RGLS4326 in Patients With Autosomal Dominant Polycystic Kidney DiseasePolycystic Kidney Disease, Autosomal Dominant
COMPLETED19 Analytics
PHASE1COMPLETED
A Study of RGLS4326 in Patients With Autosomal Dominant Polycystic Kidney Disease
Polycystic Kidney Disease, Autosomal DominantUnlock trial analytics

Study Endpoints

Primary Endpoints

Changes in primary biomarker levels from baseline
Baseline to Day 44

Changes in polycystin-1 (PC-1) and polycystin-2 (PC-2) protein levels in urinary exosomes from baseline to Day 44

Secondary Endpoints

Changes in secondary biomarker levels from baseline
Baseline to Day 44
Pharmacokinetics (Cmax)
Baseline to Day 44
Pharmacokinetics (Tmax)
Baseline to Day 71
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
RGLS4326 1 mg/kg Q2WEXPERIMENTALEligible participants will receive subcutaneous injection of 1 mg/kg of RGLS4326 every other week for 4 doses
RGLS4326 0.3 mg/kg Q2WEXPERIMENTALEligible participants will receive subcutaneous injection of 0.3 mg/kg of RGLS4326 every other week for 4 doses
RGLS4326 0.1 or 0.5 mg/kg Q2WEXPERIMENTALEligible participants will receive subcutaneous injection of 0.1 or 0.5 mg/kg of RGLS4326 every other week for 4 doses

Interventions

NameTypeDescription
RGLS4326DRUGSolution for subcutaneous injection
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Eligibility Criteria

Age Range18 Years to 70 Years
SexALL
Healthy VolunteersNo
Study Sites12

Inclusion Criteria: * Male or female ADPKD patients 18 to 70 years old * Class 1C, 1D, or 1E Mayo Imaging Classification of ADPKD (based upon prior MRI or CT Scan or MRI obtained during screening) * Estimated GFR at Screening between 30 to 90 mL/min/1.73 m\^2 calculated by the investigator using th...

Countries:United States
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Frequently asked questions about RGLS4326

What is RGLS4326 used for?

RGLS4326 is an investigational small molecule being developed for the treatment of autosomal dominant polycystic kidney disease (ADPKD), a genetic disorder characterized by the growth of cysts in the kidneys. It is currently in clinical development for this condition.

Who makes RGLS4326?

RGLS4326 is being developed by Regulus Therapeutics Inc., a biopharmaceutical company traded on the NASDAQ under the ticker symbol RGLS. The company is conducting clinical research on this investigational drug for autosomal dominant polycystic kidney disease.

What phase is RGLS4326 in?

RGLS4326 is in Phase 1 clinical development. It is an investigational drug and has not been approved by the FDA. A Phase 1 study of RGLS4326 in patients with autosomal dominant polycystic kidney disease has been completed.

What clinical trials is RGLS4326 in?

RGLS4326 has one completed clinical trial, NCT04536688, titled "A Study of RGLS4326 in Patients With Autosomal Dominant Polycystic Kidney Disease." This Phase 1 study enrolled 19 participants in the United States and included adults aged 18 years and older.

Is RGLS4326 the same as other names?

RGLS4326 is the primary name for this investigational drug. No alternative names have been reported for this compound in the available clinical trial information. It is identified by its code name RGLS4326 in clinical research.