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LMT

Phase 3

Heterozygous Familial Hypercholesterolemia | Small molecule | Metabolic |Regeneron Pharmaceuticals, Inc.|Last Updated: Oct 28, 2015

Success Probability

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials1
Total Enrollment249

FDA Designations

No designations recorded

Clinical trial landscape

LMT · 1 trial · 1 indication

Phase 3 1
NCT01709500Study of Alirocumab (REGN727/SAR236553) in Patients With heFH (Heterozygous Familial Hypercholesterolemia) Who Are Not Adequately Controlled With Their LMT (Lipid-Modifying Therapy)Heterozygous Familial Hypercholesterolemia
COMPLETED249 Analytics
PHASE3COMPLETED
Study of Alirocumab (REGN727/SAR236553) in Patients With heFH (Heterozygous Familial Hypercholesterolemia) Who Are Not Adequately Controlled With Their LMT (Lipid-Modifying Therapy)
Heterozygous Familial HypercholesterolemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Percent Change From Baseline in Calculated LDL-C at Week 24 - Intent--to--Treat (ITT) Analysis
From Baseline to Week 52

Calculated LDL-C values were obtained using the Friedewald formula. Adjusted Least- squares (LS) means and standard errors at Week 24 were obtained from a mixed -effect model with repeated measures (MMRM) to account for missing data. All available post -baseline data from Week 4 to Week 52 regardless of status on- or off-treatment were used in the model.

Secondary Endpoints

Percent Change From Baseline in Calculated LDL-C at Week 24 - On-Treatment Analysis
From Baseline to Week 52
Percent Change From Baseline in Calculated LDL-C at Week 12 - ITT Analysis
From Baseline to Week 52
Percent Change From Baseline in Calculated LDL-C at Week 12 - On- Treatment Analysis
From Baseline to Week 52
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Alirocumab 75 mg/up to 150 mgEXPERIMENTALAlirocumab 75 mg every two weeks (Q2W) added to stable dose of statin with or without LMT for 78 weeks. Alirocumab dose up-titrated to 150 mg Q2W from Week 12 when LDL-C levels ≥70 mg/dL at Week 8.
PlaceboPLACEBO_COMPARATORPlacebo matched to alirocumab SC injection for 78-week treatment duration.

Interventions

NameTypeDescription
LMT (atorvastatin, simvastatin, or rosuvastatin)DRUG -
alirocumabDRUGAlirocumab administered as a subcutaneous (SC) injection of 1 mL into the abdomen, thigh, or outer area of the upper arm.
PlaceboDRUGPlacebo matched to alirocumab administered as a SC injection of 1 mL into the abdomen, thigh, or outer area of the upper arm.
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites24

Inclusion Criteria: 1. Patients with heFH\* who are not adequately controlled\*\* with a maximally-tolerated daily dose\*\*\* of statin with or without other LMT, at a stable dose prior to the screening visit (week -2). \*Diagnosis of heFH must be made either by genotyping or by clinical criter...

Countries:CzechiaNetherlandsNorwayUnited Kingdom
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Frequently asked questions about LMT

What is LMT used for?

LMT is a small molecule being studied for the treatment of heterozygous familial hypercholesterolemia (HeFH), a genetic condition causing high cholesterol. It is intended for patients who are not adequately controlled with their current lipid-modifying therapy. LMT is currently in Phase 3 clinical development and is not yet approved.

What does LMT target?

LMT is a lipid-modifying therapy, as indicated by its full name in the clinical trial. It is being studied in patients with heterozygous familial hypercholesterolemia who are not adequately controlled with their current lipid-modifying therapy. The specific molecular target of LMT is not disclosed in the available information.

Who makes LMT?

LMT is being developed by Regeneron Pharmaceuticals, Inc., a biopharmaceutical company traded on the NASDAQ under the ticker symbol REGN. Regeneron is conducting clinical trials to evaluate LMT for the treatment of heterozygous familial hypercholesterolemia.

What phase is LMT in?

LMT is in Phase 3 clinical development. It has completed one Phase 3 trial, and it is not yet approved by regulatory authorities. The drug is being investigated for use in patients with heterozygous familial hypercholesterolemia who are not adequately controlled with their current lipid-modifying therapy.

What clinical trials is LMT in?

LMT has one completed Phase 3 clinical trial with the identifier NCT01709500. This trial studied LMT in patients with heterozygous familial hypercholesterolemia who were not adequately controlled with their lipid-modifying therapy. The trial enrolled 249 participants and was conducted in Czechia, Netherlands, Norway, and the United Kingdom.