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ALN-HSD

Phase 2

Metabolic Dysfunction-Associated SteatoHepatitis (MASH) | Small molecule | Metabolic |Regeneron Pharmaceuticals, Inc.|Last Updated: Jul 8, 2026

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials1
Total Enrollment120

FDA Designations

No designations recorded

Clinical trial landscape

ALN-HSD · 1 trial · 1 indication

Phase 2 1
NCT05519475A Precision Medicine Approach Using Gene Silencing to Treat a Chronic Liver Disease Called Metabolic Dysfunction-Associated Steatohepatitis (MASH) in Adult Participants at Increased Genetic Risk for This ConditionMetabolic Dysfunction-Associated SteatoHepatitis (MASH)
RECRUITING120 Analytics
PHASE2RECRUITING
A Precision Medicine Approach Using Gene Silencing to Treat a Chronic Liver Disease Called Metabolic Dysfunction-Associated Steatohepatitis (MASH) in Adult Participants at Increased Genetic Risk for This Condition
Metabolic Dysfunction-Associated SteatoHepatitis (MASH)Unlock trial analytics

Study Endpoints

Primary Endpoints

Change in quantitative liver Fibrosis (qFibrosis)
Baseline to week 52

Change in the continuous qFibrosis score measured by second harmonic generation/two-photon excitation microscopy

Secondary Endpoints

Improvement of Non-Alcoholic Steatohepatitis Clinical Research Network (NASH-CRN) Fibrosis (F) stage by ≥1 stage without worsening of MASH on liver biopsy
Baseline to week 52
Resolution of MASH with no worsening of NASH-CRN fibrosis on liver biopsy
Baseline to week 52
Change in serum ALanine aminoTransferase (ALT)
Baseline to week 52
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
ALN-HSDEXPERIMENTALRandomized 1:1
PlaceboPLACEBO_COMPARATORRandomized 1:1

Interventions

NameTypeDescription
ALN-HSDDRUGAdministered per the protocol
PlaceboDRUGAdministered per the protocol
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Eligibility Criteria

Age Range18 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites71

Key Inclusion Criteria: 1. Adult male or female ≥18 years (or country's legal age of adulthood) 2. A diagnosis of MASH with Fibrosis (F) stage 2 or 3, according to the NASH-CRN 3. NAS score ≥3, as defined in the protocol 4. Meets genotype criteria for study enrollment, as defined in the protocol 5....

Countries:United StatesJapanPuerto RicoSouth Korea
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Recent Changes (Last 90 Days)

LOWJul 8, 2026NCT05519475lastUpdatePostDate: changed
LOWJul 8, 2026NCT05519475lastUpdatePostDate: changed

Frequently asked questions about ALN-HSD

What is ALN-HSD used for in MASH?

ALN-HSD is an investigational small molecule being developed for Metabolic Dysfunction-Associated SteatoHepatitis (MASH), a chronic liver disease. It is being studied in adult participants who are at increased genetic risk for this condition. The drug is currently in Phase 2 clinical development and is not yet approved by regulatory authorities.

Who makes ALN-HSD?

ALN-HSD is being developed by Regeneron Pharmaceuticals, Inc., a biopharmaceutical company traded on the Nasdaq under the ticker symbol REGN. The company is conducting a Phase 2 clinical trial to evaluate the drug's safety and efficacy in patients with Metabolic Dysfunction-Associated SteatoHepatitis (MASH).

What phase is ALN-HSD in?

ALN-HSD is currently in Phase 2 clinical development. It is an investigational drug, meaning it has not been approved by regulatory agencies. The ongoing Phase 2 trial is recruiting participants and is designed to evaluate the drug in adults with Metabolic Dysfunction-Associated SteatoHepatitis (MASH) who have an increased genetic risk for the condition.

What clinical trials is ALN-HSD in?

ALN-HSD is being studied in one active Phase 2 clinical trial with the identifier NCT05519475. This randomized, double-blind, placebo-controlled trial is recruiting 120 participants across the United States, Japan, Puerto Rico, and South Korea. The study is evaluating the drug in adults aged 18 years and older with Metabolic Dysfunction-Associated SteatoHepatitis (MASH).

How does ALN-HSD work?

ALN-HSD is a small molecule designed to treat Metabolic Dysfunction-Associated SteatoHepatitis (MASH) through a gene silencing approach. The drug targets the underlying genetic factors that increase a person's risk for developing this chronic liver condition. By silencing specific genes, ALN-HSD aims to address the disease process in genetically susceptible individuals.