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Bempikibart

Phase 2

Alopecia Areata | Small molecule | Dermatology |Q32 Bio Inc.|Last Updated: May 8, 2026

Target and mechanism

Molecular targetIL-7Rα
Target classProtein
ModalitySmall molecule

Also known as ADX-914, bempikibart (ADX-914)

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment75

FDA Designations

FAST_TRACK

Clinical trial landscape

Bempikibart · 3 trials · 3 indications

Phase 2 2Phase 1 1
NCT06018428A Phase 2a Proof-of-Concept Trial of Bempikibart (ADX-914) for the Treatment of Severe Alopecia Areata (SIGNAL-AA)Alopecia Areata
ACTIVE NOT_RECRUITING75 Analytics
NCT05509023Evaluating Safety and Efficacy of ADX-914 in Patients With Moderate to Severe Atopic Dermatitis (SIGNAL-AD)Atopic Dermatitis
ACTIVE NOT_RECRUITING102 Analytics
PHASE2ACTIVE NOT_RECRUITING
A Phase 2a Proof-of-Concept Trial of Bempikibart (ADX-914) for the Treatment of Severe Alopecia Areata (SIGNAL-AA)
Alopecia AreataUnlock trial analytics
PHASE2ACTIVE NOT_RECRUITING
Evaluating Safety and Efficacy of ADX-914 in Patients With Moderate to Severe Atopic Dermatitis (SIGNAL-AD)
Atopic DermatitisUnlock trial analytics

Study Endpoints

Primary Endpoints

Part A: Mean relative percent change in SALT score
24 Weeks

Part A: Mean relative percent change in SALT score at 24 weeks compared with baseline

Part B: Mean percent change from baseline in SALT score
36 weeks

Part B: Mean percent change from baseline in SALT score at Week 36

Part A only: Safety parameters including incidence of serious adverse events and adverse events of special interest
14 Weeks
Part A and B: Mean percentage change from baseline in Eczema Area and Severity Index (EASI) score at Week 14 for ADX-914 vs placebo
14 Weeks

Severity score is based on evaluation of severity of atopic dermatitis in 4 body regions (head and neck, trunk, upper limbs, and lower limbs). The minimum score is 0 (less severe) and maximum score is 72 (most severe).

Number of subjects with adverse events
Screening to end of study, up to 18 weeks

Listing and summary of AE incidence

Number of subjects with Physical exam findings
Screening to end of study, up to 18 weeks

Listing of clinically significant changes in PE findings

Number of subjects with Clinical safety lab changes
Screening to end of study, up to 18 weeks

Listing and change from baseline to end of study

Number of subjects with Systolic blood pressure changes
Screening to end of study, up to 18 weeks

Listing and change from baseline to end of study

Number of subjects with Heart rate changes
Screening to end of study, up to 18 weeks

Listing and change from baseline to end of study

Number of subjects with 12 Lead ECG changes
Screening to end of study, up to 18 weeks

Change in 12-lead ECG parameters from baseline to end of study

Secondary Endpoints

Part A: Mean relative percentage change SALT score compared with baseline at Weeks 6,12, and 18.
18 Weeks
Part A: Mean relative percentage change in SALT score at 24 weeks compared with treatment nadir.
24 Weeks
Part A: Absolute change in SALT score compared with baseline at Weeks 6, 12, 18, and 24.
24 Weeks
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Experimental: bempikibart (ADX-914)EXPERIMENTAL200mg dose of bempikibart (ADX-914) administered via injection under the skin
ADX-914EXPERIMENTAL -
PlaceboPLACEBO_COMPARATOR -
Experimental: Cohort 1:1 - 1:6 ADX-914EXPERIMENTALADX-914 single SC dose
Placebo Comparator: Cohort 1:1 - 1:6 placeboPLACEBO_COMPARATORPlacebo single SC dose
Experimental: Cohort 2:1- 2:3EXPERIMENTALADX-914 multiple SC dose once every 2 weeks for 6 weeks
Placebo Comparator: Cohort 2:1- 2:3PLACEBO_COMPARATORPlacebo multiple SC dose once every 2 weeks for 6 weeks

Interventions

NameTypeDescription
bempikibart (ADX-914)DRUGSubcutaneous administration of bempikibart (ADX-914)
ADX-914DRUGSubcutaneous administration of ADX-914
PlaceboDRUGSubcutaneous administration of Placebo
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Eligibility Criteria

Age Range18 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites33

Key Inclusion Criteria: 1. Adult men and women, aged 18 to 75 years, inclusive, at the time of informed consent. 2. Clinical diagnosis of severe to very severe alopecia areata, defined as the presence of ≥50% total scalp hair loss at screening and baseline as measured by the SALT score. Key Exclus...

Countries:United StatesCanadaAustralia
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Frequently asked questions about Bempikibart

What is bempikibart used for?

Bempikibart is an investigational small molecule being developed for the treatment of severe alopecia areata, a dermatologic condition. It is currently in Phase 2 clinical development and has not been approved by the FDA. The drug is being studied in a proof-of-concept trial for this indication.

What does bempikibart target?

Bempikibart targets IL-7Rα, a protein involved in immune signaling. By targeting this receptor, the drug is designed to modulate immune responses relevant to alopecia areata. It is a small molecule therapeutic being investigated for its potential to treat severe forms of this condition.

Who makes bempikibart?

Bempikibart is being developed by Q32 Bio Inc., a biopharmaceutical company. The company is conducting clinical trials to evaluate the drug's safety and efficacy in patients with severe alopecia areata. Q32 Bio is advancing this asset through Phase 2 clinical development.

What phase is bempikibart in?

Bempikibart is currently in Phase 2 clinical development. It is being studied in a Phase 2a proof-of-concept trial for severe alopecia areata. The drug has received Fast Track designation from the FDA, but it remains investigational and is not yet approved for any use.

What clinical trials is bempikibart in?

Bempikibart is being evaluated in a single active clinical trial, NCT06018428, titled 'A Phase 2a Proof-of-Concept Trial of Bempikibart (ADX-914) for the Treatment of Severe Alopecia Areata (SIGNAL-AA)'. This trial is enrolling 75 participants in the United States and Canada and is currently active but not recruiting.

Is bempikibart the same as ADX-914?

Yes, bempikibart is also known as ADX-914. The drug is referred to by both names in clinical research, with the Phase 2a trial using the name 'Bempikibart (ADX-914)' in its title. This alternative name may appear in scientific literature and trial registries.