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vormatrogine

Phase 3

Epilepsy, Tonic-Clonic | Small molecule | Neurology |Praxis Precision Medicines, Inc.|Last Updated: Aug 3, 2026

Target and mechanism

Molecular targetVGSCs
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment700

FDA Designations

No designations recorded

Clinical trial landscape

vormatrogine · 1 trial · 3 indications

Phase 3 1
NCT07287163Clinical Trial of Vormatrigine in Adult Patients With EpilepsyEpilepsy, Tonic-Clonic
ENROLLING BY_INVITATION700 Analytics
PHASE3ENROLLING BY_INVITATION
Clinical Trial of Vormatrigine in Adult Patients With Epilepsy
Epilepsy, Tonic-ClonicUnlock trial analytics

Study Endpoints

Primary Endpoints

To assess the safety and tolerability of vormatrigine in adults with focal or primary generalized tonic-clonic seizures
Up to 2 years

Incidence and severity of TEAEs including discontinuation of study drug due to TEAEs

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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Open-label 30 mg/day vormatrogine for up to 2 yearsEXPERIMENTALParticipants who meet all eligibility criteria will receive 30 mg of vormatrogine for up to 2 years.

Interventions

NameTypeDescription
vormatrogineDRUGOnce daily oral
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Eligibility Criteria

Age Range18 Years to 85 Years
SexALL
Healthy VolunteersNo
Study Sites36

Inclusion Criteria: * Participant who completed an eligible clinical trial (unless agreed by the sponsor medical monitor), including PRAX-628-212, PRAX-628-321 or other vormatrigine trials, or participant who has received vormatrigine outside of an eligible clinical trial (such as an expanded acces...

Countries:United StatesBrazilGermanyItalyPolandSpain
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Recent Changes (Last 90 Days)

LOWAug 3, 2026NCT07287163lastUpdatePostDate: changed
LOWAug 3, 2026NCT07287163lastUpdatePostDate: changed

Frequently asked questions about vormatrogine

What is vormatrogine used for?

Vormatrogine is an investigational small molecule being developed for epilepsy, specifically for tonic-clonic seizures. It is currently in Phase 3 clinical development for this indication.

What does vormatrogine target?

Vormatrogine targets voltage-gated sodium channels (VGSCs), which are involved in the generation and propagation of action potentials in neurons. By modulating these channels, vormatrogine aims to reduce abnormal electrical activity associated with seizures.

Who is developing vormatrogine?

Vormatrogine is being developed by Praxis Precision Medicines, Inc., a biopharmaceutical company. The company's stock is traded under the ticker symbol PRAX.

What phase is vormatrogine in?

Vormatrogine is currently in Phase 3 clinical development. It is an investigational drug and has not yet been approved by regulatory authorities.

What clinical trials is vormatrogine in?

Vormatrogine is being evaluated in a Phase 3 clinical trial (NCT07287163) enrolling adult patients with epilepsy, including those with tonic-clonic seizures. The trial is enrolling by invitation and aims to enroll approximately 700 participants across multiple countries.