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PRAX-628

Phase 2

Focal Onset Seizure | Small molecule | Neurology |Praxis Precision Medicines, Inc.|Last Updated: Aug 3, 2026

Target and mechanism

Molecular targetsodium-channels
Target classIon Channel
ModalitySmall molecule

Also known as 30mg PRAX-628

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment50

FDA Designations

No designations recorded

Clinical trial landscape

PRAX-628 · 2 trials · 3 indications

Phase 2 1Phase 1 1
NCT06908356An Open Label Trial to Evaluate the Efficacy and Safety of PRAX-628 in Adults With Focal Onset or Tonic-Clonic SeizuresFocal Onset Seizure
RECRUITING50 Analytics
PHASE2RECRUITING
An Open Label Trial to Evaluate the Efficacy and Safety of PRAX-628 in Adults With Focal Onset or Tonic-Clonic Seizures
Focal Onset SeizureUnlock trial analytics

Study Endpoints

Primary Endpoints

To evaluate the efficacy of PRAX-628 on seizure frequency in adults with FOS or PGTCS currently taking ASMs
8 weeks

Median percent change in monthly (28 days) seizure frequency from the Screening/Observation Period to the Treatment Period for PRAX-628

To assess the relative bioavailability of single 40 mg oral doses of PRAX-628 tablet as compared to PRAX-628 capsules
28 days

Geometric mean ratio (90% CI) for maximum observed plasma concentration (Cmax)

Secondary Endpoints

To evaluate the efficacy of PRAX 628 on seizure frequency in adults with FOS or PGTCS currently taking ASMs
8 weeks
CGI-S Change from Baseline
8 weeks
PGI-S Change from Baseline
8 weeks
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Open-label 30mg/day PRAX-628 for 8 weeksEXPERIMENTALParticipants who meet all eligibility criteria will receive 30mg of PRAX-628 for 8 weeks.
Single Oral Dose 40mg PRAX-628 tablet then 4x10mg PRAX-628 capsulesEXPERIMENTAL40 mg PRAX-628 tablet followed by 4×10 mg PRAX-628 capsules administered orally.
Single Oral Dose 4x10mg PRAX-628 capsules then 40mg PRAX-628 tabletEXPERIMENTAL4×10 mg PRAX-628 capsules followed by 40 mg PRAX-628 tablet administered orally.

Interventions

NameTypeDescription
30mg PRAX-628DRUGOnce daily oral
PRAX-628DRUGOnce daily oral
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Eligibility Criteria

Age Range18 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites11

Inclusion Criteria: * A diagnosis of focal onset seizures or idiopathic generalized tonic clonic seizures. * Evidence by computed tomography (CT) or magnetic resonance imaging (MRI) in the past that has ruled out a progressive cause of epilepsy. * Participant must have been receiving stable doses o...

Countries:United StatesAustraliaSpain
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Recent Changes (Last 90 Days)

MEDIUMSep 3, 2026NCT06840925TRIAL_REMOVED: changed
MEDIUMSep 3, 2026NCT06840925TRIAL_REMOVED: changed
MEDIUMSep 3, 2026NCT06840925TRIAL_REMOVED: changed
HIGHAug 3, 2026NCT06840925Status: NOT_YET_RECRUITING → COMPLETED
HIGHAug 3, 2026NCT06840925Status: NOT_YET_RECRUITING → COMPLETED

Frequently asked questions about PRAX-628

What is PRAX-628 used for?

PRAX-628 is an investigational small molecule being developed by Praxis Precision Medicines, Inc. for the treatment of focal onset seizures and primary generalized epilepsy. It is currently being evaluated in a Phase 2 open-label clinical trial in adults with these conditions. The drug is also being studied in healthy volunteers for bioavailability purposes.

What does PRAX-628 target?

PRAX-628 targets sodium channels, which are ion channels involved in the generation and propagation of electrical signals in neurons. By modulating these channels, the drug is intended to reduce abnormal neuronal activity that leads to seizures. This mechanism is being investigated for its potential to treat focal onset seizures and primary generalized epilepsy.

Who makes PRAX-628?

PRAX-628 is being developed by Praxis Precision Medicines, Inc., a biopharmaceutical company focused on neurological diseases. The company's stock is listed under the ticker symbol PRAX. Praxis is conducting clinical trials to evaluate the safety, efficacy, and bioavailability of PRAX-628 in patients with seizure disorders.

What phase is PRAX-628 in?

PRAX-628 is currently in Phase 2 clinical development for the treatment of focal onset seizures and primary generalized epilepsy. A Phase 2 open-label trial is actively recruiting participants to evaluate the efficacy and safety of the drug in adults. Additionally, a Phase 1 trial has been completed to assess its relative bioavailability in healthy volunteers.

What clinical trials is PRAX-628 in?

PRAX-628 is being studied in two clinical trials. The first, NCT06840925, is a completed Phase 1 trial in healthy volunteers to evaluate relative bioavailability. The second, NCT06908356, is an actively recruiting Phase 2 open-label trial in adults with focal onset seizures or primary generalized epilepsy, conducted in the United States, Australia, and Spain.

Is PRAX-628 the same as 30mg PRAX-628?

Yes, PRAX-628 is also known as 30mg PRAX-628, which refers to a specific dosage strength of the drug. This alternative name may be used in clinical contexts to specify the dose being administered. The drug is being developed by Praxis Precision Medicines under the primary name PRAX-628.