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Pertuzumab

Phase 2

Brain Metastases | Small molecule | Oncology |Pfizer, Inc.|Last Updated: Jun 23, 2026

Target and mechanism

Molecular targetERBB2
Target classInhibitor
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment48

FDA Designations

No designations recorded

Clinical trial landscape

Pertuzumab · 1 trial · 3 indications

Phase 2 1
NCT05323955Secondary BRain Metastases Prevention After Isolated Intracranial Progression on Trastuzumab/Pertuzumab or T-DM1 in Patients With aDvanced Human Epidermal Growth Factor Receptor 2+ brEast Cancer With the Addition of TucatinibBrain Metastases
ACTIVE NOT_RECRUITING48 Analytics
PHASE2ACTIVE NOT_RECRUITING
Secondary BRain Metastases Prevention After Isolated Intracranial Progression on Trastuzumab/Pertuzumab or T-DM1 in Patients With aDvanced Human Epidermal Growth Factor Receptor 2+ brEast Cancer With the Addition of Tucatinib
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Study Endpoints

Primary Endpoints

Progression Free Survival (PFS)
3 years

Evaluate the ability of tucatinib in combination with trastuzumab/pertuzumab or TDM-1 to prolong intracranial progression free survival (PFS) in patients compared to historical controls. PFS is defined as the time from the day of study treatment initiation until evidence of intracranial disease progression per RANO-BM or death from any cause.

Secondary Endpoints

Progression Free Survival by RECIST 1.1
3 years
Progression Free Survival of Extracranial Disease
3 years
Distant Versus Local Intracranial Progression Free Survival
3 years
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Experimental GroupEXPERIMENTALTrastuzumab/pertuzumab + tucatinib or T-DM1 + tucatinib 300mg of tucatinib taken orally twice a day. Taken on Days 1-21 of a 21 Day cycle (3 Weeks). Trastuzumab/Biosimilar administered per current package insert based on site standard of care guidelines Pertuzumab or Biosimilar administered per current package insert based on site standard of care guidelines Trastuzumab Emtansine (T-DM1) administered per current package insert based on site standard of care guidelines

Interventions

NameTypeDescription
TrastuzumabDRUGAdminister per current package insert based on site standard of care guidelines
Trastuzumab Emtansine (T-DM1)DRUGAdminister per current package insert based on site standard of care guidelines
PertuzumabDRUGAdminister per current package insert based on site standard of care guidelines
TucatinibDRUG300 mg orally twice daily (21 Day Cycle)
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites8

Inclusion Criteria: Subject must meet all of the following applicable inclusion criteria to participate in this study: * Written informed consent and HIPAA authorization for release of personal health information prior to registration. NOTE: HIPAA authorization may be included in the informed cons...

Countries:United States
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Frequently asked questions about Pertuzumab

What is Pertuzumab used for in Brain Metastases?

Pertuzumab is an investigational antibody being studied for the treatment of brain metastases in patients with advanced human epidermal growth factor receptor 2 positive breast cancer. It is being evaluated in a Phase 2 clinical trial for this indication, specifically in combination with trastuzumab and tucatinib.

What does Pertuzumab target?

Pertuzumab is a monoclonal antibody, indicated by its -mab suffix, that targets the human epidermal growth factor receptor 2, commonly known as HER2. It is being studied in patients with HER2 positive advanced breast cancer who have brain metastases.

Who makes Pertuzumab?

Pertuzumab is being developed by Pfizer, Inc., which is publicly traded under the ticker symbol PFE on the New York Stock Exchange. The company is conducting clinical research to evaluate the drug's safety and efficacy in patients with brain metastases.

What phase is Pertuzumab in?

Pertuzumab is currently in Phase 2 clinical development. It is an investigational drug and has not been approved by regulatory authorities. The ongoing Phase 2 trial is actively recruiting or has completed enrollment, with a total of 48 participants planned.

What clinical trials is Pertuzumab in?

Pertuzumab is being studied in a single Phase 2 clinical trial registered as NCT05323955. This trial is evaluating the prevention of secondary brain metastases after isolated intracranial progression on trastuzumab/pertuzumab or T-DM1, with the addition of tucatinib in patients with advanced HER2 positive breast cancer.

Is Pertuzumab the same as trastuzumab?

No, Pertuzumab is not the same as trastuzumab. While both are monoclonal antibodies targeting HER2, they are distinct drugs. In the clinical trial, Pertuzumab is being studied in combination with trastuzumab and tucatinib for the treatment of brain metastases in HER2 positive breast cancer patients.