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Genotropin

Phase 3

Growth Disorders | Small molecule | Endocrine |Pfizer, Inc.|Last Updated: Aug 10, 2026

Success Probability

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Market & Valuation

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Trial Design

RandomizedUNCONTROLLED
Total Trials1
Total Enrollment110

FDA Designations

No designations recorded

Clinical trial landscape

Genotropin · 3 trials · 3 indications

Phase 3 2Phase 1 1
NCT00396097Individualized, Target-Driven Treatment Of Children With Idiopathic Short StatureIdiopathic Short Stature
COMPLETED316 Analytics
NCT00174408Treatment Of Children With Short Stature At An Age Of 3-7 Years Who Were Born Small For Gestational AgeGrowth Disorders
COMPLETED110 Analytics
PHASE3COMPLETED
Individualized, Target-Driven Treatment Of Children With Idiopathic Short Stature
Idiopathic Short StatureUnlock trial analytics
PHASE3COMPLETED
Treatment Of Children With Short Stature At An Age Of 3-7 Years Who Were Born Small For Gestational Age
Growth DisordersUnlock trial analytics

Study Endpoints

Primary Endpoints

Absolute On-target Difference (AOTD) at 24 Months
2 years

This was defined as an absolute difference between the 24-month height standard deviation score (SDS) and targeted 24-month height SDS (10th percentile (%), or -1.3 SDS). SDS indicates how similar the participant was to the reference population. These were calculated using 2000 Center for the Disease Control (CDC) growth reference tables (by age and gender).

Height, height velocity
Area Under the Concentration-time Curve From Time Zero Extrapolated to Infinity (AUCinf) of Somatropin
At pre-dose -24, -18, -12, -8, 0 and 1, 2, 3, 4, 6, 8, 10, 12, 16 and 24 hours post-dose on day 1 of each period

AUCinf = Area under the plasma concentration versus time curve (AUC) from time zero (pre-dose) to extrapolated infinite time (0-inf). It is obtained from AUC (0-t) plus AUC (t-inf).

Maximum Observed Plasma Concentration (Cmax) for Somatropin
At pre-dose -24, -18, -12, -8, 0 and 1, 2, 3, 4, 6, 8, 10, 12, 16 and 24 hours post-dose on day 1 of each period

Secondary Endpoints

Variability of Height SDS at 24 Months
2 years
Time Cost (Months Until >= -2 SDS)
2 years
Computed Cost of Height Gain at 48 Months
4 years
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
StandardACTIVE_COMPARATORStandard daily HGH treatment
Formula-basedACTIVE_COMPARATORFormula-based dose regimen
Sequence 1EXPERIMENTALSingle dose of 4 milligrams (mg) subcutaneous genotropin via marketed genotropin pen 12 (Reference) followed by single dose of 4mg subcutaneous genotropin via new genotropin injector pen (Test)
Sequence 2EXPERIMENTALSingle dose of 4mg subcutaneous genotropin via new genotropin injector pen (Test) followed by single dose of 4mg subcutaneous genotropin via marketed genotropin pen 12 (Reference)

Interventions

NameTypeDescription
GenotropinDRUGCompare daily injections of formula-based HGH treatment to daily injections of standard HGH treatment in subjects with Idiopathic Short Stature over 24 months period followed by an exploratory 24 months period.
Marketed Genotropin Pen 12DEVICEGrowth Hormone Delivery Device for use with Somatropin for injection
New Genotropin Injector PenDEVICEGrowth Hormone Delivery Device for use with Somatropin for injection
Genotropin 4mgDRUG4mg subcutaneous
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Eligibility Criteria

Age Range3 Years to 10 Years
SexALL
Healthy VolunteersNo
Study Sites43

Inclusion Criteria: * Prepubertal children with bone ages between 3 and 10 years of age for males and 3 and 9 years of age for females * Naive to Growth Hormone treatment Exclusion Criteria: * Abnormal karyotype. Small Gestational Age and Skeletal dysplasia.

Countries:United StatesBelgium
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Competitive Landscape -Growth Disorders 4 trials

Recent Changes (Last 90 Days)

HIGHAug 11, 2026NCT07542886Status: RECRUITING → COMPLETED
HIGHAug 11, 2026NCT07542886Status: RECRUITING → COMPLETED
HIGHAug 11, 2026NCT07542886Status: RECRUITING → COMPLETED

Frequently asked questions about Genotropin

What is Genotropin used for?

Genotropin is used for growth disorders, growth hormone deficiency, and idiopathic short stature. It is an endocrine therapy being developed by Pfizer, Inc. for conditions related to growth in children. The drug is currently in Phase 3 clinical development and is not yet approved by the FDA.

Who makes Genotropin?

Genotropin is developed by Pfizer, Inc., a biopharmaceutical company traded on the New York Stock Exchange under the ticker symbol PFE. Pfizer is conducting clinical trials to evaluate the drug's safety and efficacy in treating growth-related conditions.

What phase is Genotropin in?

Genotropin is in Phase 3 clinical development. It is an investigational drug and has not been approved by the FDA. Pfizer has completed multiple Phase 3 trials studying its use in children with growth hormone deficiency and idiopathic short stature.

What clinical trials is Genotropin in?

Genotropin has been studied in several completed clinical trials. NCT00396097 evaluated individualized treatment in 316 children with idiopathic short stature. NCT00965484 assessed an injection pen in 136 patients with growth hormone deficiency or idiopathic short stature. NCT03831880 compared treatment burden in 87 children with growth hormone deficiency.

Is Genotropin the same as somatropin?

Genotropin is a brand name for somatropin, which is a recombinant human growth hormone. In clinical trials, it is referred to as Genotropin (somatropin), indicating that somatropin is the active ingredient. The drug is being studied for its effects on growth in children with various growth disorders.