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Bococizumab

Phase 3

Heterozygous Familial Hypercholesterolemia | Small molecule | Metabolic |Pfizer, Inc.|Last Updated: May 31, 2019

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials1
Total Enrollment370

FDA Designations

No designations recorded

Clinical trial landscape

Bococizumab · 8 trials · 3 indications

Phase 3 6Phase 2 1Phase 1 1
NCT02458287Efficacy, Safety, Tolerability And Actual Use Study Of Bococizumab And An Autoinjector (Pre-Filled Pen) In Subjects With Hyperlipidemia Or DyslipidemiaHyperlipidemia
COMPLETED299 Analytics
NCT02100514Randomized Clinical Trial of Bococizumab (PF-04950615; RN316) in Subjects With Primary Hyperlipidemia or Mixed Dyslipidemia At Risk Of Cardiovascular EventsHyperlipidemia
COMPLETED746 Analytics
NCT02135029Randomized Clinical Trial of Bococizumab (PF-04950615; RN316) in Subjects Who Are Intolerant to StatinsHyperlipidemia
COMPLETED184 Analytics
NCT01968967Randomized Clinical Trial of Bococizumab (PF-04950615; RN316) in Subjects With Hyperlipidemia or Mixed Dyslipidemia at Risk of Cardiovascular EventsHyperlipidemia
COMPLETED2,139 Analytics
NCT01968980A 52 Week Study To Assess The Use Of Bococizumab (PF-04950615; RN316) In Subjects With Heterozygous Familial HypercholesterolemiaHeterozygous Familial Hypercholesterolemia
COMPLETED370 Analytics
NCT01968954Randomized Clinical Trial Of Bococizumab (PF-04950615; RN316) In Subjects With Hyperlipidemia Or Mixed Dyslipidemia At Risk Of Cardiovascular EventsHyperlipidemia
COMPLETED711 Analytics
PHASE3COMPLETED
Efficacy, Safety, Tolerability And Actual Use Study Of Bococizumab And An Autoinjector (Pre-Filled Pen) In Subjects With Hyperlipidemia Or Dyslipidemia
HyperlipidemiaUnlock trial analytics
PHASE3COMPLETED
Randomized Clinical Trial of Bococizumab (PF-04950615; RN316) in Subjects With Primary Hyperlipidemia or Mixed Dyslipidemia At Risk Of Cardiovascular Events
HyperlipidemiaUnlock trial analytics
PHASE3COMPLETED
Randomized Clinical Trial of Bococizumab (PF-04950615; RN316) in Subjects Who Are Intolerant to Statins
HyperlipidemiaUnlock trial analytics
PHASE3COMPLETED
Randomized Clinical Trial of Bococizumab (PF-04950615; RN316) in Subjects With Hyperlipidemia or Mixed Dyslipidemia at Risk of Cardiovascular Events
HyperlipidemiaUnlock trial analytics
PHASE3COMPLETED
A 52 Week Study To Assess The Use Of Bococizumab (PF-04950615; RN316) In Subjects With Heterozygous Familial Hypercholesterolemia
Heterozygous Familial HypercholesterolemiaUnlock trial analytics
PHASE3COMPLETED
Randomized Clinical Trial Of Bococizumab (PF-04950615; RN316) In Subjects With Hyperlipidemia Or Mixed Dyslipidemia At Risk Of Cardiovascular Events
HyperlipidemiaUnlock trial analytics

Study Endpoints

Primary Endpoints

Percent Change From Baseline at Week 12 in Fasting Low Density Lipoprotein Cholesterol (LDL-C) Level for Bococizumab 150 mg Dose Group and Matched Placebo
Baseline, Week 12
Percentage of Injections That Met the Definition for Successful Assessment Using the Participant Assessment Tool (PAT) for Bococizumab 150 mg Dose Group at Week 0 (Day 1)
Week 0 (Day 1)

A successful injection based on PAT was an injection where the participant answered "yes" to all the three questions: "Were you able to inject your medicine?" "Has the blue bar moved across the window?" Was the medicine not flowing after needle withdrawn?"

Percentage of Injections That Met the Definition for Successful Assessment Using the Participant Assessment Tool (PAT) for Bococizumab 150 mg Dose Group at Week 2
Week 2

A successful injection based on PAT was an injection where the participant answered "yes" to all the three questions: "Were you able to inject your medicine?" "Has the blue bar moved across the window?" Was the medicine not flowing after needle withdrawn?"

Percentage of Injections That Met the Definition for Successful Assessment Using the Participant Assessment Tool (PAT) for Bococizumab 150 mg Dose Group at Week 4
Week 4

A successful injection based on PAT was an injection where the participant answered "yes" to all the three questions: "Were you able to inject your medicine?" "Has the blue bar moved across the window?" Was the medicine not flowing after needle withdrawn?"

Percentage of Injections That Met the Definition for Successful Assessment Using the Participant Assessment Tool (PAT) for Bococizumab 150 mg Dose Group at Week 6
Week 6

A successful injection based on PAT was an injection where the participant answered "yes" to all the three questions: "Were you able to inject your medicine?" "Has the blue bar moved across the window?" Was the medicine not flowing after needle withdrawn?"

Percentage of Injections That Met the Definition for Successful Assessment Using the Participant Assessment Tool (PAT) for Bococizumab 150 mg Dose Group at Week 8
Week 8

A successful injection based on PAT was an injection where the participant answered "yes" to all the three questions: "Were you able to inject your medicine?" "Has the blue bar moved across the window?" Was the medicine not flowing after needle withdrawn?"

Percentage of Injections That Met the Definition for Successful Assessment Using the Participant Assessment Tool (PAT) for Bococizumab 150 mg Dose Group at Week 10
Week 10

A successful injection based on PAT was an injection where the participant answered "yes" to all the three questions: "Were you able to inject your medicine?" "Has the blue bar moved across the window?" Was the medicine not flowing after needle withdrawn?"

Percent Change From Baseline in Fasting Low Density Lipoprotein Cholesterol (LDL-C) at Week 12
Baseline, Week 12
Percent Change From Baseline in Low Density Lipoprotein Cholesterol (LDL-C) at Week 12
Baseline, Week 12
Percent Change From Baseline in Low Density Lipoprotein-Cholesterol (LDL-C) at Week 12
Baseline, Week 12
Percent Change From Baseline in Fasting Low Density Lipoprotein-Cholesterol (LDL-C) at Day 85
Baseline, Day 85

LDL-C is cholesterol in the bloodstream that is carried by low density lipoprotein. Fasting was required at least 10 hours before blood sample collection. Baseline was defined as the mean of the last two non-missing measurements collected prior to the first dose of study treatment. Both measurements must be within 10 days prior to the first dose of study treatment; if only one measurement was available 10 days prior to the first dose of study treatment, then that measurement served as the baseline value. Percent change from baseline = (\[observed value divided by baseline value\] minus 1) multiplied by 100.

Percent Change From Baseline in Fasting Low Density Lipoprotein-Cholesterol (LDL-C) at Day 113
Baseline, Day 113

LDL-C is cholesterol in the bloodstream that is carried by low density lipoprotein. Fasting was required at least 10 hours before blood sample collection. Baseline was defined as the mean of the last two non-missing measurements collected prior to the first dose of study treatment. Both measurements must be within 10 days prior to the first dose of study treatment; if only one measurement was available 10 days prior to the first dose of study treatment, then that measurement served as the baseline value. Percent change from baseline = (\[observed value divided by baseline value\] minus 1) multiplied by 100.

Area Under the Plasma Concentration-Time Curve From Time 0 Extrapolated to Infinite Time (AUCinf)
Day 1 (Hour 0 pre-dose, Hours 1 and 8 post-dose), Day 2, Day 3, Day 4, Day 5, Day 6, Day 8, Day 15, Day 22, Day 29, Day 36, Day 43, Day 50, Day 57, Day 64, Day 71 and Day 85/Early Termination.

AUCinf is the area under the plasma concentration-time curve (AUC) from time zero (pre-dose) extrapolated to infinite time.

Maximum Observed Plasma Concentration (Cmax)
Day 1 (Hour 0 pre-dose, Hours 1 and 8 post-dose), Day 2, Day 3, Day 4, Day 5, Day 6, Day 8, Day 15, Day 22, Day 29, Day 36, Day 43, Day 50, Day 57, Day 64, Day 71 and Day 85/Early Termination.

Maximum observed concentration.

Secondary Endpoints

Percentage of Injections That Met the Definition for Successful Assessment Using the Participant Assessment Tool (PAT) for Bococizumab 75 mg Dose Group and Combined Bococizumab 150 mg and 75 mg Dose Group at Week 0 (Day 1), 2, 4, 6, 8 and 10
Week 0 (Day 1), 2, 4, 6, 8, 10
Percentage of Injections That Met the Definition for Successful Assessment Using the Observer Assessment Tool (OAT) for Bococizumab 150 mg Dose, Bococizumab 75 mg Dose Group and Combined Bococizumab 150 mg and 75 mg Dose Group at Week 0 (Day 1), 4 and 8
Week 0 (Day 1), 4, 8
Percent Change From Baseline at Week 12 in Fasting Low Density Lipoprotein Cholesterol (LDL-C) Level for Bococizumab 75 mg Dose Group and Matched Placebo
Baseline, Week 12
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Bococizumab 150mgEXPERIMENTALBococizumab 150mg autoinjector (pre-filled pen)
Bococizumab 75mgEXPERIMENTALBococizumab 75mg autoinjector (pre-filled pen)
Bococizumab 150mg placeboPLACEBO_COMPARATORBococizumab 150mg placebo autoinjector (pre-filled pen)
Bococizumab 75mg placeboPLACEBO_COMPARATORBococizumab 75mg autoinjector (pre-filled pen)
Bococizumab (PF-04950615; RN316)EXPERIMENTALBococizumab (PF-04950615; RN316)
placeboPLACEBO_COMPARATOR -
Bococizumab (PF-04950615;RN316)EXPERIMENTALBococizumab (PF-04950615;RN316)
AtorvastatinACTIVE_COMPARATOR -
Population AEXPERIMENTALA total of 9 groups in two population. Population A comprises hypercholesterolemic Japanese subjects whose LDL-C is not controlled by a stable dose of atorvastatin. A subject who is receiving a stable dose of atorvastatin will be randomized into one out of 5 dose groups.
Population BEXPERIMENTALA total of 9 groups in two population. Population B comprises hypercholesterolemic Japanese subjects who are naïve for a treatment by lipid lowering drug and whose fasting LDL-cholesterol is not controlled. A subject who is treatment naïve will be randomized into one out of 4 dose groups.
Single 150 mg PF-04950615 dose administered to the abdomenACTIVE_COMPARATOR -
Single 150 mg PF-04950615 dose administered to the upper armEXPERIMENTAL -
Single 150 mg PF-04950615 dose administered to the thighEXPERIMENTAL -

Interventions

NameTypeDescription
Bococizumab 150mgBIOLOGICALBococizumab autoinjector (pre-filled pen) combination Product. 150mg every 2 weeks for 10 weeks, subcutaneous injection.
Bococizumab 75mgBIOLOGICALBococizumab autoinjector (pre-filled pen) combination Product. 75mg every 2 weeks for 10 weeks, subcutaneous injection.
Bococizumab 150mg placeboBIOLOGICALBococizumab placebo autoinjector (pre-filled pen) combination Product. 150mg placebo every 2 weeks for 10 weeks, subcutaneous injection.
Bococizumab 75mg placeboBIOLOGICALBococizumab placebo autoinjector (pre-filled pen) combination product. 75mg placebo every 2 weeks for 10 weeks, subcutaneous injection.
Bococizumab (PF-04950615; RN316)DRUG150 mg every 2 weeks, subcutaneous injection for 52 weeks.
PlaceboOTHERSubcutaneous injection every 2 weeks for 52 weeks.
Bococizumab (PF-04950615;RN316)DRUG150 mg every 2 weeks by subcutaneous injection for 24 weeks
AtorvastatinDRUGAtorvastatin PO QD
Placebo for Bococizumab (PF-04950615;RN316)OTHER150 mg every 2 weeks by subcutaneous injection for 24 weeks
Placebo for atorvastatinOTHERPO QD
EzetimibeDRUGAtorvastatin plus Ezetimibe 10 mg oral administration once daily for 16 week (open)
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites30

Inclusion Criteria: * Treated with a statin - Fasting LDL-C \>=70mg/dL and triglycerides \<=400mg/dL Exclusion Criteria: * Pregnant or breastfeeding females - Cardiovascular or cerebrovascular event or procedures during the past 90 days - Congestive heart failure NYHA class IV - Poorly controlled...

Countries:United StatesCanadaCzechiaFinlandNetherlandsNorwayPolandPuerto RicoSingaporeSouth KoreaSwedenUnited KingdomColombiaFranceHungaryLithuaniaMexicoRomaniaRussiaSpainTaiwanBulgariaItalySouth AfricaAustraliaGermanyHong KongJapan
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Frequently asked questions about Bococizumab

What is Bococizumab used for?

Bococizumab is an investigational drug being studied for hyperlipidemia, heterozygous familial hypercholesterolemia, and hypercholesterolemia. It is a small molecule being developed by Pfizer, Inc. for metabolic conditions. As of the available data, it is in Phase 3 clinical development and has not been approved by the FDA.

What does Bococizumab target?

The specific molecular target of Bococizumab is not disclosed in the available information. It is being studied for its effects on lipid levels in conditions such as hyperlipidemia and hypercholesterolemia, but the exact mechanism of action has not been specified.

Who makes Bococizumab?

Bococizumab is being developed by Pfizer, Inc., a company traded on the New York Stock Exchange under the ticker symbol PFE. Pfizer is conducting clinical trials to evaluate the drug's safety and efficacy in patients with lipid disorders.

What phase is Bococizumab in?

Bococizumab is in Phase 3 clinical development. It has completed five clinical trials, including Phase 1, Phase 2, and Phase 3 studies. However, it remains investigational and is not FDA approved. The drug is not currently in any active trials, as all five studies have been completed.

What clinical trials is Bococizumab in?

Bococizumab has completed five clinical trials. Key studies include NCT01968967, a Phase 3 trial in hyperlipidemia with 2,139 participants, and NCT01968980, a Phase 3 trial in heterozygous familial hypercholesterolemia with 370 participants. Other trials include NCT02043301 (Phase 1) and NCT02055976 (Phase 2).

Is Bococizumab the same as PF-04950615 or RN316?

Yes, Bococizumab is also known as PF-04950615 and RN316. These alternative names appear in clinical trial records, such as NCT01968967, which refers to Bococizumab (PF-04950615; RN316). Researchers and investors may encounter these names when searching for information about the drug.