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YTB323

Phase 1

Generalized Myasthenia Gravis | Gene therapy | Neurology |Novartis AG|Last Updated: Sep 4, 2026

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMC
Total Trials1
Total Enrollment15

FDA Designations

No designations recorded

Clinical trial landscape

YTB323 · 2 trials · 3 indications

Phase 1 2
NCT06704269Study to Assess Safety, Efficacy, and Cellular Kinetics of YTB323 in Generalized Myasthenia GravisGeneralized Myasthenia Gravis
ACTIVE NOT_RECRUITING15 Analytics
NCT05798117An Open-label, Study to Assess Safety, Efficacy and Cellular Kinetics of YTB323 in Severe, Refractory Systemic Lupus ErythematosusSystemic Lupus Erythematosus
ACTIVE NOT_RECRUITING21 Analytics
PHASE1ACTIVE NOT_RECRUITING
Study to Assess Safety, Efficacy, and Cellular Kinetics of YTB323 in Generalized Myasthenia Gravis
Generalized Myasthenia GravisUnlock trial analytics
PHASE1ACTIVE NOT_RECRUITING
An Open-label, Study to Assess Safety, Efficacy and Cellular Kinetics of YTB323 in Severe, Refractory Systemic Lupus Erythematosus
Systemic Lupus ErythematosusUnlock trial analytics

Study Endpoints

Primary Endpoints

Occurrence, severity, and frequency of Adverse Events (AEs) and Serious Adverse Events (SAEs)
Baseline up to 2 years

Incidence of AE's, including Cytokine Release Syndrome (CRS) and Immune Effector Cell-Associated Neurotoxicity Syndrome (ICANs), changes in Vital Signs, Laboratory parameters, ECG, and neurological status qualifying and reported as AEs.

Number of participants with AEs and SAEs
Day 1 to 2 years

Long term safety follow up

Secondary Endpoints

Plasma Pharmacokinetics (PK) of YTB323 - CMAX
Pre-dose Day 1 up to 2 years
Plasma Pharmacokinetics (PK) of YTB323 - AUC
Pre-dose Day 1 up to 2 years
Plasma Pharmacokinetics (PK) of YTB323 - Tmax
Pre-dose Day 1 up to 2 years
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
YTB323EXPERIMENTALYTB323 single intravenous (i.v.) infusion

Interventions

NameTypeDescription
YTB323GENETICCAR-T cell suspension for intravenous infusion
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Eligibility Criteria

Age Range18 Years to 65 Years
SexALL
Healthy VolunteersNo
Study Sites11

Inclusion Criteria: 1. Confirmed gMG diagnosis supported by the following: * Documented report of positive serology testing for either AChR antibodies or MuSK antibodies at screening AND at least one of the following: * History of abnormal neuromuscular transmission test demonstrated by repe...

Countries:United StatesFranceJapanUnited KingdomAustraliaGermanySpainSwitzerland
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Recent Changes (Last 90 Days)

LOWAug 21, 2026NCT05798117lastUpdatePostDate: changed
LOWAug 21, 2026NCT05798117lastUpdatePostDate: changed
LOWJul 24, 2026NCT05798117lastUpdatePostDate: changed
LOWJul 24, 2026NCT05798117lastUpdatePostDate: changed
LOWJun 26, 2026NCT06704269lastUpdatePostDate: changed
LOWJun 26, 2026NCT06704269lastUpdatePostDate: changed

Frequently asked questions about YTB323

What is YTB323 used for?

YTB323 is an investigational gene therapy being developed for severe, refractory Systemic Lupus Erythematosus (SLE) and Generalized Myasthenia Gravis (gMG). It is currently in Phase 1 clinical trials for these autoimmune conditions, with studies enrolling adult patients aged 18 years and older.

Who makes YTB323?

YTB323 is being developed by Novartis AG, a multinational pharmaceutical company traded on the New York Stock Exchange under the ticker symbol NVS. The company is conducting Phase 1 clinical trials to evaluate the safety, efficacy, and cellular kinetics of YTB323 in patients with Systemic Lupus Erythematosus and Generalized Myasthenia Gravis.

What phase is YTB323 in?

YTB323 is in Phase 1 clinical development. It is an investigational gene therapy that has not yet been approved by regulatory authorities. Two Phase 1 trials are ongoing: one for Systemic Lupus Erythematosus and one for Generalized Myasthenia Gravis, with a combined planned enrollment of 36 participants.

What clinical trials is YTB323 in?

YTB323 is being evaluated in two Phase 1 clinical trials. The first, NCT05798117, is an open-label study in severe, refractory Systemic Lupus Erythematosus with 21 participants, active but not recruiting. The second, NCT06704269, is a study in Generalized Myasthenia Gravis with 15 participants, currently recruiting in the United States, France, Japan, and the United Kingdom.

Is YTB323 FDA approved?

YTB323 is not FDA approved. It is an investigational gene therapy currently in Phase 1 clinical trials for Systemic Lupus Erythematosus and Generalized Myasthenia Gravis. The trials are designed to assess safety, efficacy, and cellular kinetics, and the drug remains in clinical development.