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TOBI

Phase 3

Treatment of Early Pulmonary Infections With P. Aeruginosa in Cystic Fibrosis Patients | Small molecule | Respiratory |Novartis AG|Last Updated: Jul 15, 2016

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment50

FDA Designations

No designations recorded

Clinical trial landscape

TOBI · 1 trial · 1 indication

Phase 3 1
NCT01082367Randomized, Controlled Study of CF Patients Between 3 Months and Less Than 7 YearsTreatment of Early Pulmonary Infections With P. Aeruginosa in Cystic Fibrosis Patients
COMPLETED50 Analytics
PHASE3COMPLETED
Randomized, Controlled Study of CF Patients Between 3 Months and Less Than 7 Years
Treatment of Early Pulmonary Infections With P. Aeruginosa in Cystic Fibrosis PatientsUnlock trial analytics

Study Endpoints

Primary Endpoints

Percentage of Participants P Aeruginosa-free After Completion of the First Treatment Cycle
Day 29

Sputum/throat swab cultures were assessed.

Secondary Endpoints

Percentage of Participants Free From P. Aeruginosa 28 Days After Termination of the Second Treatment Cycle
Day 91
Percentage of Participants P Aeruginosa-free at Termination of the Double Blind Period
Day 91
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelCROSSOVER
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
TOBI (tobramycin inhaled solution)/PlaceboEXPERIMENTALParticipants randomized to TOBI received the investigational treatment for 28 days twice daily (bi)d in the first treatment cycle. At the end of first treatment cycle, participants who were positive for P. aeruginosa entered the open label (OL) phase of the study and received TOBI for 28 days bid. Participants who were negative for P. aeruginosa at the end of first treatment cycle and agreed to participate in the cross-over treatment period received placebo for 28 days bid (second treatment cycle).
Placebo/TOBIPLACEBO_COMPARATORParticipants randomized to placebo group received 0.9 % saline (NaCl) for 28 days bid in the first treatment cycle. At the end of first treatment cycle, participants who were positive for P. aeruginosa entered the OL phase of the study and received TOBI for 28 days bid. Participants who were negative for P. aeruginosa at the end of first treatment cycle and agreed to participate in the cross-over treatment period received TOBI for 28 days bid (second treatment cycle).

Interventions

NameTypeDescription
TOBIDRUGTOBI (tobramycin inhaled solution)
PlaceboDRUGPlacebo
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Eligibility Criteria

Age Range3 Months to 6 Years
SexALL
Healthy VolunteersNo
Study Sites19

Inclusion Criteria: * Diagnosis of cystic fibrosis * Early lower respiratory tract infection with P. aeruginosa, Exclusion Criteria: * Known local or systemic hypersensitivity to aminoglycosides or inhaled antibiotics. * Administration of loop diuretics within 7 days prior to study drug administr...

Countries:CanadaEgyptFranceGermanyGreeceHungaryItalyRomaniaRussiaSwitzerland
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Frequently asked questions about TOBI

What is TOBI used for in cystic fibrosis?

TOBI is used for the treatment of early pulmonary infections with P. aeruginosa in cystic fibrosis patients. It is a small molecule respiratory therapy being developed by Novartis AG for this indication, specifically studied in patients between 3 months and less than 7 years of age.

What does TOBI target?

TOBI targets P. aeruginosa, the bacterium that causes early pulmonary infections in cystic fibrosis patients. It is an antibiotic designed to treat these infections, which are a common complication in cystic fibrosis. The drug is administered to reduce the bacterial load in the lungs of affected patients.

Who makes TOBI?

TOBI is developed by Novartis AG, a multinational pharmaceutical company listed on the stock exchange under the ticker NVS. Novartis is conducting clinical trials to evaluate the safety and efficacy of TOBI in treating early pulmonary infections with P. aeruginosa in cystic fibrosis patients.

What phase is TOBI in?

TOBI is in Phase 3 clinical development. It has completed a Phase 3 trial (NCT01082367) that enrolled 50 patients. The drug is investigational and has not been approved by regulatory authorities based on the available information. It remains in clinical development for the treatment of early pulmonary infections in cystic fibrosis.

What clinical trials is TOBI in?

TOBI has one completed Phase 3 clinical trial, NCT01082367, titled 'Randomized, Controlled Study of CF Patients Between 3 Months and Less Than 7 Years'. This double-blind, placebo-controlled trial enrolled 50 patients across multiple countries including Canada, Egypt, France, Germany, Greece, Hungary, Italy, Romania, Russia, and Switzerland.

Is TOBI the same as tobramycin?

TOBI is a brand name for a formulation of tobramycin, an aminoglycoside antibiotic. It is specifically developed for inhalation to treat pulmonary infections in cystic fibrosis patients. The drug is being studied for early P. aeruginosa infections, and the clinical trial data supports its use in this patient population.