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Patupilone

Phase 2

Brain Metastasis | Small molecule | Oncology |Novartis AG|Last Updated: Feb 21, 2021

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment50

FDA Designations

No designations recorded

Clinical trial landscape

Patupilone · 10 trials · 9 indications

Phase 2 3Phase 1 7
NCT00411528Efficacy and Safety of Patupilone in Men (≥18 Years) With Metastatic Hormone Refractory Prostate CancerMetastatic Hormone Refractory Prostate Cancer
COMPLETED185 Analytics
NCT00273312Patupilone Activity in Advanced/Metastatic Hepatocellular CarcinomaHepatocellular Carcinoma
COMPLETED25 Analytics
NCT00219297Study of Patupilone in Patients With Brain Metastasis From Non-small Cell Lung CancerBrain Metastasis
COMPLETED50 Analytics
PHASE2COMPLETED
Efficacy and Safety of Patupilone in Men (≥18 Years) With Metastatic Hormone Refractory Prostate Cancer
Metastatic Hormone Refractory Prostate CancerUnlock trial analytics
PHASE2COMPLETED
Patupilone Activity in Advanced/Metastatic Hepatocellular Carcinoma
Hepatocellular CarcinomaUnlock trial analytics
PHASE2COMPLETED
Study of Patupilone in Patients With Brain Metastasis From Non-small Cell Lung Cancer
Brain MetastasisUnlock trial analytics

Study Endpoints

Primary Endpoints

Antitumor response based on PSA decrease
Every 3 weeks
Tumor response as assessed by radiologic techniques and/or physical examination based on Response Evaluation Criteria in Solid Tumors (RECIST)
at screening and at completion of every 6 weeks prior to the next dose administration
To evaluate the effects of patupilone on the pharmacokinetics of warfarin in patients with advanced malignancies.
Dose-limiting Toxicity
18 months
To characterize the pharmacokinetic profile of patupilone including any potential metabolite(s) in blood/plasma as well as the total radioactivity in blood and plasma.
one week
Maximum tolerated dose (MTD) and dose-limiting toxicity (DLT) of patupilone in combination with carboplatin (AUC 6)
Every 3 weeks
Safety and tolerability in patients with hepatic impairment will be assessed by adverse events (AEs), serious adverse events (SAEs) and out of range lab values
at completion of the study
To evaluate the preliminary anti-tumor activity which will be assessed by radiological scans every 6 weeks
at completion of the study
To assess the effect of hepatic impairment on the pharmacokinetics of patupilone and its metabolite
After completion of the study (approximately 6 weeks from treatment)
To determine the maximum tolerated dose of patupilone in patients with hepatic impairment
After completion of the study (approximately 6 weeks from treatment)
Phase I: Number of Total Dose-limiting Toxicity (DLT) During Dose Escalation to Determine Maximum Tolerated Dose (MTD)
Cycle 1 (21 days)

The MTD was defined as the highest dose of patupilone administered every three weeks (q3w) where not more than one out of six patients experienced a DLT using a standard 3+3 design. Dose escalation started at 6.5 mg/m\^2 until MTD in steps of 0.5 mg/m\^2 until 12 mg/m\^2, then in steps of 1 mg/m\^2 till 13.0 mg/m\^2. DLTs were assessed during cycle 1. During this time frame, no more than one DLT occurred in any of the explored dose levels up to 13 mg/m\^2, thus, the MTD as defined by the protocol was not reached in this study.

Phase II: Number of Participants With Best Overall Response Rate (ORR) According to Response Evaluation Criteria in Solid Tumors (RECIST)
At baseline, then every second cycle (approximately every 6 weeks), until disease progression or discontinuation. Average 18 weeks.

Overall response is the number of participants who had a complete response (CR) or a partial response (PR) based on local investigator's assessment of RECIST criteria. Per RECIST: CR, all detectable tumor has disappeared; PR, a \>=30% decrease in the sum of the longest dimensions of the target lesions (TLs) taking as a reference the baseline sum, no worsening of non-TLs, and no new lesions; Progressive disease (PD), a \>=20% increase in TLs, clearly worsening of non-TLs, or emergence of new lesions; Stable Disease (SD), small changes that do not meet previously given criteria.

Secondary Endpoints

Measurable soft tissue response for both regimens
Every 6 weeks or every 12 weeks if patient has bone disease for bone scan
Time to progression
at screening and at completion of every 6 weeks prior to the next dose administration
Overall survival
at screening and at completion of every 6 weeks prior to the next dose administration
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
1: 8 mg/m2 study drug + prednisoneEXPERIMENTALPatupilone 8 mg/m2 + prednisone 5 mg bid daily
2: study drug + prednisone days 1 -8EXPERIMENTALPatupilone 10 mg/m2 + prednisone days 1 -8 at 25 mg bid, day 9 at 20 mg bid, day 10 at 15 mg bid, day 11 at 10 mg bid, day 12 - 21 at 5 mg bid
3: Study drug + prednisone days 1 - 4EXPERIMENTALPatupilone 10 mg/m2 + prednisone days 1 - 4 at 5 mg bid, days 5 -12 at 25 mg bid, day 13 at 20 mg bid, day 14 at 15 mg bid, day 15 at 10 mg bid, day 16 - 21 at 5 mg bid
4: Docetaxel 75 mg/m2 + prednisone 5 mg bid dailyACTIVE_COMPARATORDocetaxel 75 mg/m2 once every 3 weeks + prednisone 5 mg bid daily
PatupiloneEXPERIMENTALwas administered at 10 mg/m2, as a single intravenous infusion over 20 minutes, once every 3 weeks
Single ArmEXPERIMENTAL -
EPO906EXPERIMENTAL -
Patupilone onlyEXPERIMENTALCycle 1 patupilone alone Cycle 2 and onward patupilone and carboplatin
Carboplatin aloneACTIVE_COMPARATORCycle 1 Carboplatin alone Cycle 2 and onward patuilone and carboplatin
Arm A (Normal liver function)EXPERIMENTAL -
Arm B (Mild liver dysfunction)EXPERIMENTAL -
Arm C (Moderate liver dysfunction)EXPERIMENTAL -

Interventions

NameTypeDescription
PatupiloneDRUG -
prednisoneDRUG -
docetaxelDRUG -
Patupilone/EPO906DRUG -
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Eligibility Criteria

Age Range18 Years to N/A
SexMALE
Healthy VolunteersNo
Study Sites32

Inclusion criteria: * Must be ≥ 18 years of age * Confirmed and documented diagnosis of prostate cancer * Confirmed and documented evidence of progression of disease (hormone refractory) * Low testosterone levels * Chemotherapy-naïve Exclusion criteria: * Recent radiation therapy (within 4 weeks)...

Countries:United StatesAustraliaBelgiumFranceGermanyItalySingaporeSpainHong KongSouth KoreaTaiwanJapan
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Frequently asked questions about Patupilone

What is Patupilone used for?

Patupilone is an investigational small molecule being studied in oncology for several advanced cancers, including metastatic hormone refractory prostate cancer, advanced solid tumors, brain metastasis, carcinoma, and non-small-cell lung cancer. It is developed by Novartis AG and is currently in Phase 1 clinical development.

What does Patupilone target?

Patupilone is a small molecule in oncology. Its specific molecular target has not been disclosed in available information, so its mechanism of action is not detailed here. It is being investigated for its potential effects in advanced malignancies and solid tumors.

Who makes Patupilone?

Patupilone is developed by Novartis AG, a global pharmaceutical company listed on the New York Stock Exchange under the ticker NVS. The drug is currently in Phase 1 clinical trials for various oncology indications.

What phase is Patupilone in?

Patupilone is in Phase 1 clinical development. It is an investigational drug and has not been approved by regulatory authorities. All four clinical trials for Patupilone have been completed, with no active trials currently ongoing.

What clinical trials is Patupilone in?

Patupilone has completed four Phase 1 clinical trials: NCT00420524 and NCT00421044 studied the drug in patients with advanced solid tumors and varying degrees of hepatic function; NCT00426140 examined its pharmacokinetics after a single intravenous administration; and NCT00448396 evaluated its effects on warfarin pharmacokinetics and pharmacodynamics in advanced malignancies.

Is Patupilone the same as epothilone B?

Patupilone is also known as epothilone B, a natural product derived from the myxobacterium Sorangium cellulosum. It is being developed by Novartis AG as an anticancer agent and is currently in Phase 1 clinical trials for advanced solid tumors and other malignancies.