Recent Updates
Recently added Catalysts

PIM447

Phase 1

Myelofibrosis | Small molecule | Oncology |Novartis AG|Last Updated: Feb 9, 2022

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

CONTROLLED
Total Trials1
Total Enrollment15

FDA Designations

No designations recorded

Clinical trial landscape

PIM447 · 1 trial · 1 indication

Phase 1 1
NCT02370706Study of the Safety of PIM447 in Combination With Ruxolitinib (INC424) and LEE011 in Patients With MyelofibrosisMyelofibrosis
COMPLETED15 Analytics
PHASE1COMPLETED
Study of the Safety of PIM447 in Combination With Ruxolitinib (INC424) and LEE011 in Patients With Myelofibrosis
MyelofibrosisUnlock trial analytics

Study Endpoints

Primary Endpoints

Incidence of dose limiting toxicities during the first cycle of study treatment
Cycle 1 (28 days)

To estimate the maximum tolerated dose and/or recommended dose for expansion for each of the following three treatment arms in patients with myelofibrosis (MF): PIM447 plus ruxolitinib (doublet), LEE011 plus ruxolitinib (doublet), PIM447 plus ruxolitinib and LEE 011 (triple combination).

Secondary Endpoints

Number of participants with adverse events/serious adverse events
Approximately 27 months (end of study)
Proportion of patients achieving ≥ 35% reduction in spleen volume by magnetic resonance imaging (MRI) at Week 24
24 weeks
Changes in ratio of mutant to wild type JAK2 alleles (i.e. allele burden)
Approximately 27 months (end of study)
Unlock Study Endpoints

Study Design & Arms

AllocationNA
MaskingNONE
ModelPARALLEL
PurposeHEALTH_SERVICES_RESEARCH

Treatment Arms

ArmTypeDescription
Dose Escalation Arm 1EXPERIMENTAL -
Dose Escalation Arm 2EXPERIMENTAL -
Dose Escalation Arm 3EXPERIMENTAL -
Dose Expansion Arm 1EXPERIMENTAL -
Dose Expansion Arm 2EXPERIMENTAL -
Dose Expansion Arm 3EXPERIMENTAL -

Interventions

NameTypeDescription
PIM447DRUGpan-pim inhibitor
RuxolitinibDRUGJAK1/JAK2 inhibitor
LEE011DRUGCDK4/6 inhibitor
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites9

Inclusion Criteria: * Eastern Cooperative Oncology Group (ECOG) performance status 0 to 2. * Patient must be diagnosed with JAK2V617F-positive primary or secondary MF. * Dose-escalation and Expansion parts: Patients with a \< 35% reduction in spleen volume by MRI/CT or \< 50% reduction in spleen si...

Countries:AustraliaCanadaFranceGermanyItalyNetherlandsSingaporeUnited Kingdom
Unlock Eligibility Criteria

Frequently asked questions about PIM447

What is PIM447 used for in myelofibrosis?

PIM447 is an investigational small molecule being studied for the treatment of myelofibrosis. It is a targeted therapy that has been evaluated in a Phase 1 clinical trial in combination with other agents. The drug is not approved and remains in clinical development for this condition.

What does PIM447 target?

PIM447 is a small molecule that targets PIM kinases, which are enzymes involved in cell survival and proliferation. By inhibiting these kinases, the drug aims to interfere with cancer cell growth. This mechanism is being explored in the context of myelofibrosis, a type of bone marrow disorder.

Who makes PIM447?

PIM447 is being developed by Novartis AG, a global pharmaceutical company listed on the New York Stock Exchange under the ticker symbol NVS. Novartis is conducting clinical research to evaluate the safety and efficacy of this investigational drug in patients with myelofibrosis.

What phase is PIM447 in?

PIM447 is in Phase 1 clinical development. A Phase 1 study has been completed to assess the safety of PIM447 when used in combination with other drugs for myelofibrosis. The drug is investigational and has not received regulatory approval for any indication.

What clinical trials is PIM447 in?

PIM447 has been studied in one clinical trial, identified as NCT02370706. This was a Phase 1 study titled 'Study of the Safety of PIM447 in Combination With Ruxolitinib (INC424) and LEE011 in Patients With Myelofibrosis.' The trial enrolled 15 participants and has been completed.

Is PIM447 the same as any other drug?

PIM447 is a distinct investigational compound developed by Novartis. It is not known to have alternative names or be identical to other approved drugs. In clinical trials, it has been studied in combination with ruxolitinib and LEE011, but it is a separate therapeutic agent.