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MenC-CRM LIQ

Phase 2

Meningococcal Disease | Monoclonal antibody | Infectious Disease |Novartis AG|Last Updated: Apr 25, 2017

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedACTIVE_CONTROLLEDBiomarker
Total Trials1
Total Enrollment992
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT01434680Evaluating the Comparative Safety and Immunogenicity of Three Lots of Novartis Meningococcal C Conjugate Vaccine in Healthy ToddlersPHASE2 COMPLETED 992Sep 1, 2011Nov 1, 2012Apr 25, 201711 Poland
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Study Endpoints
Primary Endpoints
Geometric Mean Human Serum Bactericidal Activity Titers Against N Meningitidis Serogroup C 28 Days After Vaccination
1 month postvaccination (day 29)

Immunogenicity was measured by human serum bactericidal activity (hSBA) geometric mean titers (GMTs)against N meningitidis type C, at day 29 after a single vaccination when administered to toddlers to assess the equivalence of MenC-CRM LIQ to MenC-CRM EMV and MenC-CRM ROS to MenC-CRM EMV.

Secondary Endpoints
Geometric Mean hSBA Titers Against N Meningitidis Serogroup C 28 Days After Vaccination
1 month postvaccination (day 29)
Number Of Subjects Reporting Solicited Local And Systemic Adverse Events
From day 1 through day 7
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Study Design & Arms
AllocationRANDOMIZED
MaskingSINGLE
ModelPARALLEL
PurposePREVENTION
Treatment Arms
ArmTypeDescription
MenC-CRM LIQ (Liquid Formulation)EXPERIMENTALSubjects received 1 injection of MenC-CRM vaccine,liquid formulation.
MenC-CRM ROS (Rosia)EXPERIMENTALSubjects received 1 injection of MenC-CRM vaccine, lyophilized formulation produced with drug substance manufactured at Rosia, Italy
MenC-CRM EMV (Emeryville)ACTIVE_COMPARATORSubjects received 1 injection of MenC-CRM vaccine, lyophilized formulation produced with drug substance manufactured at Emeryville, USA
Interventions
NameTypeDescription
MenC-CRM LIQBIOLOGICALOne dose of MenC-CRM vaccine, liquid formulation
MenC-CRM ROSBIOLOGICALOne dose of MenC-CRM vaccine, lyophilized formulation produced with drug substance manufactured at Rosia, Italy.
MenC-CRM EMVBIOLOGICALOne dose of MenC-CRM vaccine, lyophilized formulation produced with drug substance manufactured at Emeryville, USA.
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Eligibility Criteria
Age Range12 Months — 23 Months
SexALL
Healthy VolunteersYes
Study Sites11

Inclusion Criteria: 1. Healthy 12 - 23 (inclusive) month-old male or female toddlers. 2. A parent/legal guardian was given written informed consent after the nature of the study has been explained. 3. Available for both the visits scheduled in the study. 4. In good health as determined by medical h...

Countries:Poland
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