Recent Updates
Recently added Catalysts

LJM716

Phase 1

Advanced HER2-positive Breast Cancer or Gastric Cancer | Small molecule | Oncology |Novartis AG|Last Updated: Dec 19, 2020

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment64

FDA Designations

No designations recorded

Clinical trial landscape

LJM716 · 3 trials · 6 indications

Phase 1 3
NCT01822613Study of Safety & Efficacy of the Combination of LJM716 & BYL719 in Patients With Previously Treated Esophageal Squamous Cell Carcinoma (ESCC)Esophageal Squamous Cell Carcinoma
COMPLETED48 Analytics
NCT01602406Phase I Study LJM716 Combined With Trastuzumab in Patients With HER2 Overexpressing Metastatic Breast or Gastric CancerAdvanced HER2-positive Breast Cancer or Gastric Cancer
COMPLETED64 Analytics
NCT01598077A Phase I Study of LJM716 in Squamous Cell Carcinoma of Head and Neck, or HER2+ Breast Cancer or Gastric CancerHER2 + Breast Cancer, HER2 + Gastric Cancer, Squamous Cell Carcinoma of Head and Neck, Esophageal Squamous Cell Carcinoma
COMPLETED54 Analytics
PHASE1COMPLETED
Study of Safety & Efficacy of the Combination of LJM716 & BYL719 in Patients With Previously Treated Esophageal Squamous Cell Carcinoma (ESCC)
Esophageal Squamous Cell CarcinomaUnlock trial analytics
PHASE1COMPLETED
Phase I Study LJM716 Combined With Trastuzumab in Patients With HER2 Overexpressing Metastatic Breast or Gastric Cancer
Advanced HER2-positive Breast Cancer or Gastric CancerUnlock trial analytics
PHASE1COMPLETED
A Phase I Study of LJM716 in Squamous Cell Carcinoma of Head and Neck, or HER2+ Breast Cancer or Gastric Cancer
HER2 + Breast Cancer, HER2 + Gastric Cancer, Squamous Cell Carcinoma of Head and Neck, Esophageal Squamous Cell CarcinomaUnlock trial analytics

Study Endpoints

Primary Endpoints

Phase Ib primary outcome measure: Incidence rate of dose limiting toxicities (DLTs).
approximately 8 months

The open-label dose escalation part of the study will be guided by a well-established statistical method/model to estimate the maximum tolerated dose(s) and/or Recommended Phase II Dose (s) guided by the safety (incidence of dose limiting toxicities), efficacy, pharmacokinetics and pharmacodynamics data.

Phase II primary outcome measure: Progression free survival (PFS)
Every 6 weeks from the date of the baseline computed-tomography (CT) scan until the date of first documented evidence of disease progression or date of death, whichever comes first, assessed up to 24 months.

Progression-free survival is the time from date of start of treatment to the date of event defined as the first documented progression or death due to any cause. If a patient has not had an event, progression-free survival is censored at the date of last adequate assessment.

Incidence rate of Dose Limiting Toxicities
4 weeks

Incidence of dose-limiting toxicities (DLTs)

Dose-limiting toxicities (DLTs)
4 weeks

Secondary Endpoints

Safety and tolerability of the LJM716-BYL719
Every 21 days from the date of the baseline visit until the end of study visit (about 5 months)
Best overall response (BOR), per RECIST 1.1 (Ph 1b )
Every 21 days from the date of baseline computed tomography (CT) scan until end of treatment visit (about 4 months)
Plasma concentration versus time profiles Plasma PK parameters of LJM716, BYL719
Baseline, 2hr,4hr,8hr,24hr,48hr,96hr, 168 hr, every 21 days for 10 cycles (21 days each) and at end of treatment (about 4 months)
Unlock Study Endpoints

Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
LJM716-BYL719 armEXPERIMENTALapproximately 42 previously treated esophageal squamous cell carcinoma (ESCC) patients will be enrolled to the LJM716-BYL719 combination arm to evaluate the anti-tumor activity and further assess the safety, tolerability and anti-tumor activity of the combination versus current therapies (physician's choice of paclitaxel, docetaxel or irinotecan).
Paclitaxel, Docetaxel or Irinotecan armACTIVE_COMPARATORapproximately 42 previously treated esophageal squamous cell carcinoma (ESCC) patients will be enrolled to the Paclitaxel, Docetaxel or Irinotecan arm (physician's choice arm) to evaluate the anti-tumor activity and further assess the safety, tolerability and anti-tumor activity of the LJM716-BYL719 combination versus current therapies (physician's choice of paclitaxel, docetaxel or irinotecan).
LJM716 in combination with trastuzumabEXPERIMENTAL -
Dose escalation and dose expansionEXPERIMENTAL -

Interventions

NameTypeDescription
LJM716DRUGLJM716 (10-40 mg/kg) will be given as a once weekly infusion beginning on cycle 1 day 1. The doses of LJM716 will be increased as dose escalation proceeds until a maximum tolerated dose (MTD) and/or recommended phase II dose (RP2D) is established.
BYL719DRUGBYL719 (200-400 mg) will be administered orally on a once daily schedule starting cycle 1 day 1. The doses of BYL719 will be increased as dose escalation proceeds until a maximum tolerated dose (MTD) and/or recommended phase II dose (RP2D) is established.
PaclitaxelDRUGIn the Phase II portion of the study Paclitaxel is one of the 3 physician's choice drug which allows single-agent paclitaxel to be used per manufacturer's label.
DocetaxelDRUGIn the Phase II portion of the study Docetaxel is one of the 3 physician's choice drug which allows single-agent docetaxel to be used per manufacturer's label.
IrinotecanDRUGIn the Phase II portion of the study Irinotecan is one of the 3 physician's choice drug which allows single-agent irinotecan to be used per manufacturer's label
TrastuzumabDRUGTrastuzumab
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites13

Inclusion Criteria: * Histologically confirmed esophageal squamous cell carcinoma (ESCC) * No more than one prior chemotherapy regimen for recurrent or metastatic ESCC (for Phase II only). * Progression during or after platinum-based therapy for recurrent or metastatic ESCC, or recurrence within 6 ...

Countries:United StatesBelgiumCanadaHong KongSingaporeSouth KoreaSpainTaiwanUnited KingdomFranceItalyNetherlands
Unlock Eligibility Criteria

Frequently asked questions about LJM716

What is LJM716 used for?

LJM716 is an investigational drug being studied for the treatment of HER2-positive breast cancer, HER2-positive gastric cancer, squamous cell carcinoma of the head and neck, and esophageal squamous cell carcinoma. It is being developed by Novartis AG and is currently in Phase 1 clinical development.

How does LJM716 work?

LJM716 is a small molecule being developed by Novartis AG for the treatment of HER2-positive cancers. It is being studied in combination with other therapies for the treatment of HER2-positive breast cancer and gastric cancer, as well as squamous cell carcinoma of the head and neck and esophageal squamous cell carcinoma.

Who makes LJM716?

LJM716 is being developed by Novartis AG, a multinational pharmaceutical company. Novartis is conducting clinical trials to evaluate the safety and efficacy of LJM716 in patients with HER2-positive breast cancer, HER2-positive gastric cancer, squamous cell carcinoma of the head and neck, and esophageal squamous cell carcinoma.

What phase is LJM716 in?

LJM716 is in Phase 1 clinical development. It is an investigational drug and has not been approved by regulatory authorities. Clinical trials are ongoing to evaluate its safety and efficacy in patients with HER2-positive breast cancer, HER2-positive gastric cancer, squamous cell carcinoma of the head and neck, and esophageal squamous cell carcinoma.

What clinical trials is LJM716 in?

LJM716 has been studied in several Phase 1 clinical trials, including NCT01598077, NCT01602406, and NCT01822613. These trials evaluated LJM716 alone or in combination with other therapies in patients with HER2-positive breast cancer, HER2-positive gastric cancer, squamous cell carcinoma of the head and neck, and esophageal squamous cell carcinoma.

Is LJM716 the same as BYL719?

No, LJM716 is not the same as BYL719. LJM716 is being studied in combination with BYL719 in a clinical trial for the treatment of esophageal squamous cell carcinoma. LJM716 is a separate investigational drug developed by Novartis AG.