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GME751

Phase 3

Metastatic NSCLC | Small molecule | Oncology |Novartis AG|Last Updated: Apr 9, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindACTIVE_CONTROLLEDBiomarker
Total Trials1
Total Enrollment218
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT06159790A Study to Compare Efficacy, Safety, and Immunogenicity of GME751 and EU-authorized Keytruda in Adult Participants With Untreated Metastatic Non-squamous Non-small Cell Lung Cancer (NSCLC)PHASE3 COMPLETED 218Apr 29, 2024Mar 16, 2026Apr 9, 202662 United States, Bosnia and Herzegovina +14
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Study Endpoints
Primary Endpoints
Best Overall Response (BOR)
up to 9 months from date of randomization

Best Overall Response (BOR) of either Complete Response (CR) or Partial Response (PR) up to 9 months according to RECIST 1.1 as assessed by Blinded Central Imaging

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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
GME751 + pemetrexed + carboplatin or cisplatinEXPERIMENTALParticipants will receive GME751 + pemetrexed + carboplatin or cisplatin via intravenous (IV) infusion.
Keytruda-EU + pemetrexed + carboplatin or cisplatinACTIVE_COMPARATORParticipants will receive Keytruda-EU + pemetrexed + carboplatin or cisplatin via intravenous (IV) infusion.
Interventions
NameTypeDescription
GME751DRUGDrug: GME751 Concentrate for solution for infusion, Biologic, Liquid in vial, 100 mg, 200 mg every 3 weeks, i.v. infusion Drug: Pemetrexed (i.v. infusion) Drug: Carboplatin or Cisplatin (i.v. infusion)
Keytruda-EUDRUGDrug: Keytruda-EU Concentrate for solution for infusion, biologic, liquid in vial, 100 mg, 200mg every 3 weeks, i.v. infusion Drug: Pemetrexed (i.v. infusion) Drug: Carboplatin or Cisplatin (i.v. infusion)
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites62

Inclusion Criteria: * At least 18 years of age * Untreated metastatic NSCLC * Absence of tumor activating EGFR mutations and absence of ALK gene rearrangements * Measurable disease according to RECIST 1.1 * Adequate organ function * Eastern Cooperative Oncology Group (ECOG) performance status score...

Countries:United StatesBosnia and HerzegovinaBrazilGeorgiaGermanyIndiaJapanMalaysiaPhilippinesRomaniaSerbiaSpainTaiwanThailandTurkey (Türkiye)Vietnam
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Recent Changes (Last 90 Days)
MEDIUMApr 8, 2026NCT06159790TRIAL_REMOVED: changed
MEDIUMApr 8, 2026NCT06159790TRIAL_REMOVED: changed