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CFZ533 active

Phase 2

Primary Sjögren's Syndrome | Small molecule | Immunology |Novartis AG|Last Updated: Jan 5, 2021

Target and mechanism

ModalitySmall molecule

Also known as CFZ533 active - Cohort 1, CFZ533 active- Cohort 1

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment69

FDA Designations

No designations recorded

Clinical trial landscape

CFZ533 active · 1 trial · 1 indication

Phase 2 1
NCT02291029Safety, Pharmacokinetics and Preliminary Efficacy Study of CFZ533 in Patients With Primary Sjögren's SyndromePrimary Sjögren's Syndrome
COMPLETED69 Analytics
PHASE2COMPLETED
Safety, Pharmacokinetics and Preliminary Efficacy Study of CFZ533 in Patients With Primary Sjögren's Syndrome
Primary Sjögren's SyndromeUnlock trial analytics

Study Endpoints

Primary Endpoints

Change From Baseline in EULAR Sjögren's Syndrome Disease Activity Index (ESSDAI)
Baseline and Week 12

The effect of CFZ533 on clinical disease activity was measured by the change in ESSDAI (EULAR Sjögren's syndrome disease activity index) between baseline and week 12. The instrument contains 12 organ-specific domains contributing to disease activity. For each domain, features of disease activity are scored in 3 or 4 levels according to their severity. These scores are then summed across the 12 domains in a weighted manner to provide the total score (range 0-123). A reduction from baseline indicates improvement in patients.

Secondary Endpoints

Change From Baseline in EULAR Sjögren's Syndrome Patient Reported Intensity (ESSPRI)
Baseline and Week 12
Change From Baseline in Physician Global Assessment of the Patient's Overall Disease Activity (VAS)
Baseline and Week 12
Change From Baseline in Patient's Global Assessment of Their Disease Activity (VAS)
Baseline and Week 12
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Study Design & Arms

AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
CFZ533 active- Cohort 2EXPERIMENTALmultiple doses of CFZ533 intravenous infusion
CFZ533 placebo- Cohort 2PLACEBO_COMPARATORmultiple doses of placebo intravenous infusion
CFZ533 active - Cohort 1EXPERIMENTALmultiple doses of CFZ533 s.c. injection
CFZ533 placebo - Cohort 1PLACEBO_COMPARATORmultiple doses of placebo s.c. injection
CFZ533 Treatment Arm 1 - Cohort 3EXPERIMENTALmultiple doses of CFZ533 s.c. injection
CFZ533 Treatment Arm 2 - Cohort 3EXPERIMENTALSingle dose of CFZ533 i.v. infusion and multiple doses of CFZ533 s.c. injection

Interventions

NameTypeDescription
CFZ533 active - Cohort 1DRUGmultiple doses of CFZ533 s.c. injection
CFZ533 placebo- Cohort 1DRUGmultiple doses of placebo s.c. injection
CFZ533 active - Cohort 2DRUGmultiple doses of CFZ533 intravenous infusion
CFZ533 placebo - Cohort 2DRUGmultiple doses of placebo intravenous infusion
CFZ533 active -Cohort 3DRUGmultiple doses of CFZ533 s.c. injection
CFZ533 active - Cohort 3DRUGSingle dose of CFZ533 i.v. infusion and multiple doses of CFZ533 s.c. injection
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Eligibility Criteria

Age Range18 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites9

Inclusion Criteria: * Diagnosis of primary Sjögren's syndrome * ESSDAI score ≥ 6 Exclusion Criteria: * Secondary Sjögren's syndrome * Receiving cyclosphosphamide, corticosteroid bolus with dose over 1 mg/kg, rituximab, belimunab, other immunosuppressives. * At significant risk for thromboembolic ...

Countries:United StatesGermanyHungarySwitzerlandUnited Kingdom
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