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Asciminib add-on

Phase 2

CML | Small molecule | Oncology |Novartis AG|Last Updated: Apr 21, 2026

Success Probability

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Trial Design

RandomizedACTIVE_CONTROLLED
Total Trials1
Total Enrollment104

FDA Designations

No designations recorded

Clinical trial landscape

Asciminib add-on · 1 trial · 4 indications

Phase 2 1
NCT03578367Study of Efficacy and Safety of Asciminib in Combination With Imatinib in Patients With Chronic Myeloid Leukemia in Chronic Phase (CML-CP) Who Have Been Previously Treated With Imatinib and Have Not Achieved Deep Molecular Response.CML
COMPLETED104 Analytics
PHASE2COMPLETED
Study of Efficacy and Safety of Asciminib in Combination With Imatinib in Patients With Chronic Myeloid Leukemia in Chronic Phase (CML-CP) Who Have Been Previously Treated With Imatinib and Have Not Achieved Deep Molecular Response.
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Study Endpoints

Primary Endpoints

Molecular Response (MR)^4.5 Rate at 48 Weeks and Difference in Rate Between Asciminib + Imatinib and Imatinib Alone
at Week 48

Percentage of participants still treated with the randomized treatment at 48 weeks and are in MR\^4.5 (BCR::ABL1 ratio of ≤ 0.0032%) at 48 weeks (± assessment window), among all participants in the asciminib add-on arms vs imatinib arm.

Secondary Endpoints

Rate of MR^4.5 at 48 Weeks (Asciminib add-on Arms vs Nilotinib)
at Week 48
Rate of MR^4.5 by 48 Weeks (Randomized Arms)
by 48 weeks
Rate of MR^4.5 at 96 Weeks (Randomized Arms) and Difference in Rate Between Asciminib + Imatinib and Nilotinib Alone
at Week 96
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Study Design & Arms

AllocationRANDOMIZED
MaskingNONE
ModelCROSSOVER
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Asciminib 60mg QD + Imatinib 400mg QDEXPERIMENTALAsciminib 60 mg taken once daily in combination with Imatinib 400 mg taken once daily
Asciminib 40mg QD + Imatinib 400mg QDEXPERIMENTALAsciminib 40 mg taken once daily in combination with Imatinib 400 mg taken once daily
Imatinib 400mg QDACTIVE_COMPARATORImatinib 400 mg taken once daily
Nilotinib 300mg BIDACTIVE_COMPARATORNilotinib 300 mg taken twice daily
Asciminib 80mg QD (ASAC)EXPERIMENTALAsciminib 80 mg taken once daily

Interventions

NameTypeDescription
Asciminib add-onDRUGAsciminib was supplied as 40 mg and 20 mg tablets and taken orally once daily.
ImatinibDRUGImatinib was supplied as 400 mg and 100 mg tablets and taken orally once daily.
NilotinibDRUGNilotinib was supplied as 150 mg and 200 mg hard gelatin capsules and taken orally twice daily.
Asciminib 80mg QD (asciminib single agent (ASAC))DRUGAsciminib was supplied as 40 mg and 20 mg tablets and taken orally once daily (in the fasted state) on a continuous schedule (QD).
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Eligibility Criteria

Age Range18 Years to 100 Years
SexALL
Healthy VolunteersNo
Study Sites30

Inclusion Criteria: * Male or female patients ≥ 18 years of age with a confirmed diagnosis of CML-CP. * Minimum of one year (12 calendar months) treatment with imatinib first line for CML-CP (patients have to be on imatinib 400 mg QD at randomization and had no dose change in the past three months)...

Countries:United StatesAustriaCanadaCzechiaDenmarkFranceGermanyItalyPolandPortugalRussiaSouth KoreaSpainTaiwanUnited Kingdom
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Frequently asked questions about Asciminib add-on

What is Asciminib add-on used for?

Asciminib add-on is used for chronic myeloid leukemia (CML), specifically for patients in chronic phase who have been previously treated with imatinib and have not achieved a deep molecular response. It is an investigational small molecule being studied in combination with imatinib.

Who makes Asciminib add-on?

Asciminib add-on is being developed by Novartis AG, which trades under the ticker NVS. The company is studying this small molecule as an add-on therapy to imatinib for chronic myeloid leukemia in chronic phase.

What phase is Asciminib add-on in?

Asciminib add-on is in Phase 2 clinical development. It is an investigational drug and has not been approved by regulatory authorities. The Phase 2 trial has been completed, and the drug remains under clinical investigation for chronic myeloid leukemia.

What clinical trials is Asciminib add-on in?

Asciminib add-on has one completed Phase 2 clinical trial, identified as NCT03578367. This study evaluated the efficacy and safety of asciminib in combination with imatinib in patients with chronic myeloid leukemia in chronic phase who had not achieved a deep molecular response after prior imatinib treatment.

Is Asciminib add-on the same as asciminib monotherapy?

Asciminib add-on refers to the combination of asciminib with imatinib, as studied in the Phase 2 trial NCT03578367. The trial specifically investigated this add-on regimen in patients with chronic myeloid leukemia who had not achieved a deep molecular response on imatinib alone.