Recent Updates
Recently added Catalysts

AQW051

Phase 2

Dyskinesias | Small molecule | Neurology |Novartis AG|Last Updated: Dec 24, 2020

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment71

FDA Designations

No designations recorded

Clinical trial landscape

AQW051 · 6 trials · 5 indications

Phase 2 3Phase 1 3
NCT01730768A Study to Evaluate the Effects of Once Daily Doses of AQW051 on Cognition, in Stable Schizophrenia PatientsSchizophrenia
COMPLETED147 Analytics
NCT01474421Safety and Efficacy of AQW051 in L-dopa Induced Dyskinesias in Patients With Parkinson's DiseaseDyskinesias
COMPLETED71 Analytics
NCT01163227Effect of AQW051 on Cognitive Function in Patients With Chronic Stable SchizophreniaSchizophrenia Disorders
COMPLETED57 Analytics
PHASE2COMPLETED
A Study to Evaluate the Effects of Once Daily Doses of AQW051 on Cognition, in Stable Schizophrenia Patients
SchizophreniaUnlock trial analytics
PHASE2COMPLETED
Safety and Efficacy of AQW051 in L-dopa Induced Dyskinesias in Patients With Parkinson's Disease
DyskinesiasUnlock trial analytics
PHASE2COMPLETED
Effect of AQW051 on Cognitive Function in Patients With Chronic Stable Schizophrenia
Schizophrenia DisordersUnlock trial analytics

Study Endpoints

Primary Endpoints

Visual learning and memory at 4 weeks
4 weeks

The primary objective is to evaluate the pro-cognitive effects of AQW051 in a chronic stable schizophrenic patient population at week 4 as measured by the absolute change from baseline in CPAL number of errors (CogState battery) at week 4.

Change in Modified Abnormal Involuntary Movement Scale (mAIMS)score
Baseline, Day 28

Dyskinesia with a maximal score of 24.

Change in Unified Parkinson's Disease Rating Scale (UPDRS) - Part III score
Baseline, Day 28

Anti-parkinsonian effect in PD patients.

Safety and tolerability
Up to Day 42

Safety and tolerability of AQW051 as measured by the number of participants with adverse events, any clinically significant abnormalities in safety labs or electrocardiograms (ECGs), and relevant orthostatic changes in blood pressure

Effects of single oral doses of AQW051 versus placebo on cognitive function as measured by selected CogState tests
132 days Part A, 121 days Part B (screening to study completion)
Part 1: Assess BOLD response in key brain areas in schizophrenia patients during the performance of tasks as measured by (fMRI) in people with schizophrenia.
2 years (Part 1: 1 year)
Part 2: Assess safety and tolerability of multiple doses of AQW051 schizophrenia patients.
Part 2: 8 months
Safety and tolerability of single oral doses of AQW051 in Japanese healthy male subjects at the end of the study
Safety and tolerability.

Secondary Endpoints

Effect on cognitive function after 12 weeks of treatment - CogState test battery.
Baseline, 12 weeks
Effect on cognitive function after 12 weeks of treatment - MCCB
Baseline, 12 weeks
Number of patients with adverse events
12 weeks
Unlock Study Endpoints

Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
AQW051 10 mg/dayEXPERIMENTALTwo 5mg AQW051 capsules will be taken orally daily by patients from Day 1 until Day 84.
Placebo to AQW051PLACEBO_COMPARATORMatching placebo administered orally.
AQW051 High DoseEXPERIMENTALAQW051 high dose daily given orally for 28 days.
AQW051 Low DoseEXPERIMENTALAQW051 low dose daily given orally for 28 days.
PlaceboPLACEBO_COMPARATORPlacebo daily given orally for 28 days.
AQW051 Dose 1EXPERIMENTAL -
AQW051 Dose 2EXPERIMENTAL -
AQW051 Dose 3EXPERIMENTAL -
AQW051EXPERIMENTAL -

Interventions

NameTypeDescription
AQW051DRUG -
PlaceboDRUG -
Placebo (single and multiple doses)DRUG -
AQW051 2 mg (single and multiple doses)DRUG -
AQW051 15mg (single and multiple doses)DRUG -
AQW051 100mg (single dose), and 50mg (multiple doses)DRUG -
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to 55 Years
SexALL
Healthy VolunteersNo
Study Sites13

Inclusion Criteria: * Diagnosis of schizophrenia * Symptomatically stable and currently treated with a stable regimen for at least 3 (three) months prior to dosing with one of the following second generation of antipsychotics: risperidone, paliperidone, quetiapine, ziprasidone, aripiprazole. * Spec...

Countries:United StatesFranceGermanyItalyJapanUnited Kingdom
Unlock Eligibility Criteria

Frequently asked questions about AQW051

What is AQW051 used for?

AQW051 is an investigational small molecule being studied for schizophrenia, schizophrenia disorders, and L-dopa induced dyskinesias in Parkinson's disease. It has been evaluated in clinical trials for its effects on cognitive function in stable schizophrenia patients and for safety and efficacy in dyskinesias. AQW051 is not approved and remains in clinical development.

Who makes AQW051?

AQW051 is being developed by Novartis AG, a multinational pharmaceutical company traded on the New York Stock Exchange under the ticker NVS. Novartis has sponsored clinical trials of AQW051 in the United States and several European countries.

What phase is AQW051 in?

AQW051 has completed Phase 2 clinical trials. These trials investigated its effects on cognitive function in schizophrenia and on L-dopa induced dyskinesias in Parkinson's disease. AQW051 is an investigational drug and has not been approved by regulatory authorities.

What clinical trials has AQW051 been in?

AQW051 has been studied in several completed trials. NCT00825539 was a Phase 1 pharmacodynamic and pharmacokinetic study in schizophrenia. NCT01163227 and NCT01730768 were Phase 2 trials evaluating cognitive function in stable schizophrenia patients. NCT01474421 was a Phase 2 trial in L-dopa induced dyskinesias in Parkinson's disease.

Is AQW051 the same as any other drug?

AQW051 is the code name used by Novartis for this investigational compound. No alternative brand names or chemical names have been publicly associated with AQW051 in the clinical trial records. It is identified solely by the code AQW051 in all registered studies.