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AMN107, STI571

Phase 2

Gastrointestinal Stromal Tumors | Small molecule | Oncology |Novartis AG|Last Updated: Dec 8, 2020

Target and mechanism

ModalitySmall molecule

Also known as AMN107

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLED
Total Trials2
Total Enrollment94

FDA Designations

No designations recorded

Clinical trial landscape

AMN107, STI571 · 3 trials · 2 indications

Phase 2 2Phase 1 1
NCT00718562Efficacy and Safety of AMN107 in Patients With GastroIntestinal Stromal Tumors (GIST) Who Have Failed Both Imatinib and SunitinibGastrointestinal Stromal Tumors
COMPLETED35 Analytics
NCT00264160Efficacy and Safety of Oral AMN107 in Adults With Chronic Myelogenous Leukemia Resistant and/or Intolerant to Imatinib Mesylate TherapyLeukemia, Myeloid, Chronic
COMPLETED36 Analytics
PHASE2COMPLETED
Efficacy and Safety of AMN107 in Patients With GastroIntestinal Stromal Tumors (GIST) Who Have Failed Both Imatinib and Sunitinib
Gastrointestinal Stromal TumorsUnlock trial analytics
PHASE2COMPLETED
Efficacy and Safety of Oral AMN107 in Adults With Chronic Myelogenous Leukemia Resistant and/or Intolerant to Imatinib Mesylate Therapy
Leukemia, Myeloid, ChronicUnlock trial analytics

Study Endpoints

Primary Endpoints

Disease Control Rate (DCR) in all patients with either sunitinib-resistant GIST or in patients with GIST who are intolerant of sunitinib
24 weeks
Cytogenetic response within 12 months
Every 6 months for 12 months
To determine the MTD which will be the Phase II dose of AMN107 when given in combination with Imatinib. The MTD is defined to be the highest dose of AMN107 in combination with Imatinib given for at least 21 days in the first treatment cycle
From day 1 cycle 1 until at least six subjects have been treated at the recommended dose level and observed for at least 21 days

MTD is defined to be the highest dose of AMN in combination with imatinib given for at least 21 days in the first treatment cycle

Secondary Endpoints

DCR in patients with sunitinib-resistant GIST, Progression free survival (PFS), overall survival (OS), Objective response rate (ORR)
24 weeks
Safety
24 weeks
PK profile
24 weeks
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
NilotinibEXPERIMENTAL -
AMN107EXPERIMENTAL -
AMN107 + STI571EXPERIMENTAL -

Interventions

NameTypeDescription
AMN107DRUG -
AMN107, STI571DRUG -
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Eligibility Criteria

Age Range20 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites8

Inclusion Criteria: * Documented disease progression during imatinib and sunitinib therapy OR intolerance to imatinib and/or sunitinib * At least one measurable site of disease on CT/MRI scan * PS≤2 * Normal organ, electrolyte, and bone marrow function Exclusion Criteria: * Previous treatment wit...

Countries:JapanIsraelUnited StatesFranceGermanyItaly
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Frequently asked questions about AMN107, STI571

What is AMN107 used for?

AMN107 is an investigational small molecule studied in gastrointestinal stromal tumors and chronic myeloid leukemia. It has been evaluated in patients whose disease failed prior imatinib and sunitinib therapy for GIST, and in adults with chronic myelogenous leukemia resistant or intolerant to imatinib mesylate. It is not approved and remains in clinical development.

Who is developing AMN107?

AMN107 is being developed by Novartis AG, which trades under the ticker NVS. Novartis sponsored the clinical trials evaluating AMN107 in gastrointestinal stromal tumors and chronic myeloid leukemia. The drug is an investigational small molecule and has not received regulatory approval.

What phase is AMN107 in?

AMN107 is in Phase 2 development. Two completed Phase 2 trials evaluated the drug in gastrointestinal stromal tumors and chronic myeloid leukemia, and one completed Phase 1 trial studied AMN107 with imatinib in GIST. No active trials are ongoing, and the drug is not approved.

What clinical trials is AMN107 in?

AMN107 has been studied in three completed trials. NCT00718562 was a Phase 2 trial in Japan in GIST patients who failed imatinib and sunitinib. NCT00264160 was a Phase 2 trial in Israel in chronic myelogenous leukemia patients resistant or intolerant to imatinib. NCT00135005 was a Phase 1 trial of AMN107 with imatinib in GIST across the United States, France, Germany, and Italy.

Is AMN107 the same as STI571?

AMN107 is also known as AMN107, and STI571 is a separate designation. AMN107 is the investigational compound developed by Novartis, while STI571 refers to imatinib mesylate, which is used as a comparator or prior therapy in the AMN107 trials. They are distinct agents.