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AMN107, STI571

Phase 2

Gastrointestinal Stromal Tumors | Small molecule | Oncology |Novartis AG|Last Updated: Dec 8, 2020

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
UNCONTROLLED
Total Trials2
Total Enrollment94
FDA Designations
No designations recorded
Clinical Trials (2)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00718562Efficacy and Safety of AMN107 in Patients With GastroIntestinal Stromal Tumors (GIST) Who Have Failed Both Imatinib and SunitinibPHASE2 COMPLETED 35Sep 1, 2008Jul 1, 2013Feb 23, 20178 Japan
NCT00135005Study of AMN107 With Imatinib in Gastrointestinal Stromal Tumors (GIST)PHASE1 COMPLETED 59Aug 1, 2005Nov 1, 2006Dec 8, 20205 United States, France +2
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Study Endpoints
Primary Endpoints
Disease Control Rate (DCR) in all patients with either sunitinib-resistant GIST or in patients with GIST who are intolerant of sunitinib
24 weeks
To determine the MTD which will be the Phase II dose of AMN107 when given in combination with Imatinib. The MTD is defined to be the highest dose of AMN107 in combination with Imatinib given for at least 21 days in the first treatment cycle
From day 1 cycle 1 until at least six subjects have been treated at the recommended dose level and observed for at least 21 days

MTD is defined to be the highest dose of AMN in combination with imatinib given for at least 21 days in the first treatment cycle

Secondary Endpoints
DCR in patients with sunitinib-resistant GIST, Progression free survival (PFS), overall survival (OS), Objective response rate (ORR)
24 weeks
Safety
24 weeks
PK profile
24 weeks
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Study Design & Arms
AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
NilotinibEXPERIMENTAL -
AMN107 + STI571EXPERIMENTAL -
Interventions
NameTypeDescription
AMN107DRUG -
AMN107, STI571DRUG -
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Eligibility Criteria
Age Range20 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites8

Inclusion Criteria: * Documented disease progression during imatinib and sunitinib therapy OR intolerance to imatinib and/or sunitinib * At least one measurable site of disease on CT/MRI scan * PS≤2 * Normal organ, electrolyte, and bone marrow function Exclusion Criteria: * Previous treatment wit...

Countries:JapanUnited StatesFranceGermanyItaly
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