Recent Updates
Recently added Catalysts

AEB071

Phase 2

Kidney Transplantation | Small molecule | Nephrology |Novartis AG|Last Updated: Dec 22, 2020

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedACTIVE_CONTROLLED
Total Trials3
Total Enrollment650

FDA Designations

No designations recorded

Clinical trial landscape

AEB071 · 11 trials · 10 indications

Phase 2 4Phase 1 7
NCT00572585Efficacy, Safety and Tolerability of AEB071 in Patients With Active, Moderate to Severe Ulcerative ColitisUlcerative Colitis
COMPLETED60 Analytics
NCT00885196A Dose Finding Study of AEB071 Assessing Psoriasis Area and Severity Index in Patients With Plaque PsoriasisModerate and Severe Plaque Psoriasis
COMPLETED336 Analytics
NCT00615693Safety, Tolerability, and Efficacy of AEB071 in the Treatment of UveitisUveitis
COMPLETED13 Analytics
NCT00504543Efficacy, Safety and Tolerability of AEB071 Versus Cyclosporine in the Novo Renal Transplant RecipientsKidney Transplantation
COMPLETED311 Analytics
PHASE2COMPLETED
Efficacy, Safety and Tolerability of AEB071 in Patients With Active, Moderate to Severe Ulcerative Colitis
Ulcerative ColitisUnlock trial analytics
PHASE2COMPLETED
A Dose Finding Study of AEB071 Assessing Psoriasis Area and Severity Index in Patients With Plaque Psoriasis
Moderate and Severe Plaque PsoriasisUnlock trial analytics
PHASE2COMPLETED
Safety, Tolerability, and Efficacy of AEB071 in the Treatment of Uveitis
UveitisUnlock trial analytics
PHASE2COMPLETED
Efficacy, Safety and Tolerability of AEB071 Versus Cyclosporine in the Novo Renal Transplant Recipients
Kidney TransplantationUnlock trial analytics

Study Endpoints

Primary Endpoints

Rate of induction of remission after 28 days of treatment (using the Partial Mayo Score and the Modified Baron Score), also an Endoscopic biopsy will be taken
Partial Mayo Score throughout entire study, biopsy at end of dosing period
Change from baseline in plaque psoriasis as assessed by PASI response or PASI 75 (a patient that has an improvement from baseline PASI of at least 75%)
to 12 weeks treatment
Safety and tolerability of AEB071
Baseline/Day 1 to Week 8 (Day 56) (end of study)
Primary efficacy failure, defined as a composite efficacy endpoint of treated biopsy proven acute rejection,(BPAR) graft loss, death or loss to follow-up, 3 months after transplantation.
12 months
Phase Ib- Incidence of dose limiting toxicities (DLT) during the first cycle
12 months

Estimate the maximum tolerated dose (MTD) and the recommended phase II dose (RP2D) of the AEB071and EVEROLIMUS combination therapy in patients with DLBCL.

Phase II- Overall response rate (ORR) = complete response (CR) + partial response (PR) according to the non-Hodgkin's Lymphoma International Working Group criteria
12 months

Assess the preliminary evidence for anti-tumor activity at RP2D for AEB071 and EVEROLIMUS in patients with a CD79 mutation and those wild-type for the mutation but of the ABC subtype

Frequency of dose limiting toxicity during cycle 1 (28 days) - Dose Escalation
cycle 1 (28 days)
Number of participants reporting serious adverse events and adverse events - Dose Expansion
Baseline, every 28 days
-Pharmacokinetic of AEB071 & its primary metabolite, AEE800 at predose & up to 72 hours post-operatively -Safety & tolerability (vital signs,ECGs,clinical lab evaluations,seroius/adverse events) -AEB071,AEE800 & tacrolimus in blood for both Periods
at predose & 16 timepoints post-dose
Efficacy will be defined using a composite efficacy failure end point (treated biopsy proven acute rejection (BPAR), graft loss, death or loss to follow-up) between treatment and control arms
Primary efficacy failure, defined as a composite efficacy endpoint of treated biopsy-proven acute rejection (BPAR), graft loss, death or loss to follow-up
at 6 months
To compare the pharmacokinetics between healthy Caucasian and Japanese subjects after a single oral dose of AEB071
To compare the pharmacokinetics between healthy Caucasian and Japanese subjects after 7 days of oral, daily doses of AEB071
To compare the safety and tolerability of single and multiple oral doses of AEB071 in healthy Japanese and Caucasian subjects
Safety and tolerability of ascending single oral doses of AEB071 in healthy subjects.
Maximum Tolerated Dose

Secondary Endpoints

Safety and tolerability assessments (vital signs, electrocardiogram [ECG], blood samples, serious adverse events, adverse events)
Throughout entire study
Measurement of drug concentrations in blood
During the dosing period only
Relationship between drug concentration in blood and disease activity
Dosing period only
Unlock Study Endpoints

Study Design & Arms

AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
AEB071EXPERIMENTAL -
PlaceboPLACEBO_COMPARATOR -
AEB071 200 mg BIDEXPERIMENTAL -
AEB071 400 mg ODEXPERIMENTAL -
AEB071 300 mg BIDEXPERIMENTAL -
Placebo BIDPLACEBO_COMPARATOR -
1EXPERIMENTAL -
NeoralACTIVE_COMPARATOR -
AEB071 high dose with Cetican reduced doseACTIVE_COMPARATOR -
AEB071 low dose with Cetican standard doseACTIVE_COMPARATOR -
AEB071 and EVEROLIMUSEXPERIMENTALAEB071 and EVEROLIMUS will be taken together in this open-label non-randomized study
Mycophenolic Acid / tacrolimusACTIVE_COMPARATOR -
AEB071 / tacrolimus arm 1EXPERIMENTAL -
AEB071 / tacrolimus arm 2EXPERIMENTAL -

Interventions

NameTypeDescription
AEB071DRUG -
PlaceboDRUG -
CerticanDRUGtwice daily
NeoralDRUGtwice daily
EverolimusDRUGmTOR inhibitor
Mycophenolic AcidDRUG -
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to 75 Years
SexALL
Healthy VolunteersNo
Study Sites20

Inclusion Criteria: * 18-75 years males and females * Female subjects of childbearing potential must be using two methods of contraception * Active, moderate to severe disease * Poor response to or no toleration of conventional therapy (e.g. steroids, mesalamine) * Good communication with the inves...

Countries:United StatesDenmarkGermanyPolandArgentinaAustraliaBelgiumGuatemalaItalyTurkey (Türkiye)United KingdomAustriaBrazilColombiaCzechiaFranceNetherlandsNorwaySingaporeSlovakiaSpainSwitzerlandTaiwanHong KongSouth KoreaCanadaSweden
Unlock Eligibility Criteria

Frequently asked questions about AEB071

What is AEB071 used for?

AEB071 is an investigational small molecule being studied for multiple conditions, including uveal melanoma, moderate and severe plaque psoriasis, de novo liver transplantation, uveitis, CD79 mutant or ABC-subtype diffuse large B-cell lymphoma, and kidney transplantation. It has been evaluated in clinical trials for these indications, though it is not approved.

Who makes AEB071?

AEB071 is being developed by Novartis AG, a multinational pharmaceutical company. Novartis is listed on the stock exchange under the ticker symbol NVS. The company has sponsored clinical trials to investigate the safety and efficacy of AEB071 across various patient populations.

What phase is AEB071 in?

AEB071 has been studied in Phase 1 and Phase 2 clinical trials. The most advanced trials completed are Phase 2 studies for uveitis and plaque psoriasis. However, AEB071 remains investigational and is not approved for any use. All three completed trials are finished, with no active trials currently ongoing.

What clinical trials is AEB071 in?

AEB071 has been evaluated in three completed clinical trials. NCT00416546 was a Phase 1 safety study in healthy volunteers. NCT00615693 was a Phase 2 trial for uveitis. NCT00885196 was a Phase 2 dose-finding study in plaque psoriasis. Additionally, NCT01430416 was a Phase 1 trial in metastatic uveal melanoma.

Is AEB071 the same as sotrastaurin?

AEB071 is also known as sotrastaurin. This compound has been investigated under both names in clinical research. It is a small molecule that has been studied for its potential effects in various immune-mediated and oncologic conditions, though it is not yet approved.