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catridecacog

Phase 3

Congenital Bleeding Disorder | Small molecule | Rare Disease |Novo Nordisk A/S|Last Updated: Jan 24, 2018

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials8
Total Enrollment252

FDA Designations

No designations recorded

Clinical trial landscape

catridecacog · 11 trials · 5 indications

Phase 3 4Phase 2 1Phase 1 6
NCT01253811Safety and Efficacy of Monthly Replacement Therapy With Recombinant Factor XIII (rFXIII) in Paediatric Subjects With Congenital Factor XIII A-subunit DeficiencyCongenital Bleeding Disorder
COMPLETED6 Analytics
NCT01230021Safety of a Single Intravenous Dose of Recombinant Factor XIII in Children With Congenital FXIII A-subunit DeficiencyCongenital Bleeding Disorder
COMPLETED6 Analytics
NCT00978380Safety of Monthly Recombinant Factor XIII Replacement Therapy in Subjects With Congenital Factor XIII Deficiency: An Extension to Trial F13CD-1725Congenital Bleeding Disorder
COMPLETED63 Analytics
NCT00713648Evaluation of Recombinant Factor XIII for Prevention of Bleeding in Patients With FXIII Inherited DeficiencyCongenital Bleeding Disorder
COMPLETED41 Analytics
PHASE3COMPLETED
Safety and Efficacy of Monthly Replacement Therapy With Recombinant Factor XIII (rFXIII) in Paediatric Subjects With Congenital Factor XIII A-subunit Deficiency
Congenital Bleeding DisorderUnlock trial analytics
PHASE3COMPLETED
Safety of a Single Intravenous Dose of Recombinant Factor XIII in Children With Congenital FXIII A-subunit Deficiency
Congenital Bleeding DisorderUnlock trial analytics
PHASE3COMPLETED
Safety of Monthly Recombinant Factor XIII Replacement Therapy in Subjects With Congenital Factor XIII Deficiency: An Extension to Trial F13CD-1725
Congenital Bleeding DisorderUnlock trial analytics
PHASE3COMPLETED
Evaluation of Recombinant Factor XIII for Prevention of Bleeding in Patients With FXIII Inherited Deficiency
Congenital Bleeding DisorderUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of Treatment Emergent (Serious and Non-serious) Adverse Events
Week 0 to end of trial visit (week 173) for a minimum period of 52 weeks.

An adverse event was described as any untoward medical occurrence in a subject or clinical investigation subject administered a pharmaceutical product, and which does not necessarily have a causal relationship with this treatment. Treatment emergent adverse events (serious and non-serious), defined as adverse events occurring from first trial product administration to the end of the subject's participation in the trial.

Area Under the Concentration vs. Time Curve (AUC)
At pre-dose, 30 minutes, 24 hours, 7, 14, 21 and 30 days after dosing

A measure of the exposure. Blood samples for the PK assessment were drawn pre-dose and up to 30 days after dosing. The PK of FXIII in children was assessed after a single i.v. dose of rFXIII 35 IU/kg.

Adverse Events (AEs)(Serious and Non-serious)
All AEs were collected and reported from screening (week 0) for a minimum period of 52 weeks or until the end of trial visit.

An AE was defined as any unfavourable and unintended sign (including an abnormal laboratory finding, for example), symptom, or disease temporally associated with the use of a medicinal product, whether or not considered related to the medicinal product. Trial AEs (serious) included any event such as death, life-threatening experience, in-subject hospitalisation, significant disability/ congential anomaly experienced from the trial product.

Rate (Number Per Subject Year) of Bleeding Episodes Requiring Treatment With a FXIII Containing Product During the Treatment Period
For a period of 322 days (approximately one year) comprised of a screening visit (Visit 1), treatment period (Visits 2-15), unscheduled visit and end-of-trial visit (Visit 16).

It represents the incidence of bleeding episodes requiring treatment with a FXIII-containing product.

Percentage of Subjects Avoiding Any Allogeneic Transfusions for Seven Days Post-operative or Until Discharge, Whichever Came First
measured ongoing from dosing until day 7 or discharge, whichever came first

Proportion of patients avoiding blood products given via allogeneic transfusion. Blood products were defined as any of the following: RBC, platelets, FFP, fibrinogen concentrate and clotting factor(s) concentrate, including cryoprecipitate.

Occurrence of serious adverse events
from first trial related activity (visit 1) and up to 28 days (visit 8) after dosing
Occurrence of non-serious adverse events
from first trial related activity (visit 1) and up to 28 days (visit 8) after dosing
Plasma concentration-time curve (Area under Curve 0-28 days) for factor XIII activityfor both drug substances measured by the Berichrom® assay
after 4 weeks of treatment
Incidence and severity of adverse events
From dosing up to 5-7 weeks ± 3 days after trial product administration
Incidence of adverse events
Days 0-33

Secondary Endpoints

Percentage of Subjects With Development of Anti-rFXIII Antibodies, Including Inhibitors.
Week 0 to end of trial visit (week 173).
Clinical Laboratory Assessments: Biochemistry: Creatinine
Every 6th month, from week 24 to end of trial visit (week 173).
Clinical Laboratory Assessments: Biochemistry: Urea
Every 6th month, week 24 to end of trial visit (week 173).
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
rFXIII 35 IU/kgEXPERIMENTAL -
recombinant factor XIIIEXPERIMENTAL -
AEXPERIMENTAL -
rFXIIIEXPERIMENTAL -
FXIII17.5IU/KgEXPERIMENTALRecombinant factor XIII at a single dose of 17.5 IU/kg lean body mass (LBM) was administered via slow i.v. push at a rate not exceeding two mL per minute.
FXIII35IU/KgEXPERIMENTALRecombinant factor XIII at a single dose of 35 IU/kg lean body mass (LBM) was administered via slow i.v. push at a rate not exceeding two mL per minute.
PlaceboPLACEBO_COMPARATORRecombinant factor XIII placebo was administered as a single dose via slow i.v. push at a rate not exceeding two mL per minute.
BEXPERIMENTAL -
CPLACEBO_COMPARATOR -
DPLACEBO_COMPARATOR -
Trial part 1EXPERIMENTAL -
Trial part 2EXPERIMENTAL -

Interventions

NameTypeDescription
catridecacogDRUGIntravenous injection of a single dose of recombinant factor XIII, 35 IU/kg body weight every 4th week
placeboDRUGSingle dose via slow intravenous (i.v.) push at a rate not exceeding two mL per minute
recombinant factor XIIIDRUGSingle dose of 35 IU/kg body weight recombinant factor XIII (Avecia) to be administered iv (into the vein) followed by a single dose of 35 IU/kg body weight recombinant factor XIII (catridecacog) (Novo Nordisk) administered iv.
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Eligibility Criteria

Age Range1 Year to 6 Years
SexALL
Healthy VolunteersNo
Study Sites4

Inclusion Criteria: * Completed participation in trial F13CD-3760 (NCT01230021) Exclusion Criteria: * Known or suspected hypersensitivity to trial product or related products * Known history of development of inhibitors against FXIII (factor XIII) * Hereditary or acquired coagulation disorder oth...

Countries:United StatesIsraelUnited KingdomAustriaCanadaFinlandFranceGermanyItalyJapanSpainSwitzerlandDenmarkSweden
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Frequently asked questions about catridecacog

What is catridecacog used for?

Catridecacog is an investigational recombinant factor XIII product being developed for congenital bleeding disorder, specifically congenital factor XIII deficiency, and acquired bleeding disorder. It is a small molecule in the hematology therapeutic area, currently in Phase 2 clinical development by Novo Nordisk.

What does catridecacog target?

Catridecacog targets factor XIII, a key protein in the blood clotting cascade. It is a recombinant form of factor XIII designed to replace or supplement the deficient enzyme in patients with congenital factor XIII deficiency, thereby helping to stabilize blood clots and prevent bleeding episodes.

Who makes catridecacog?

Catridecacog is being developed by Novo Nordisk A/S, a global healthcare company traded under the ticker NVO. The drug is currently in Phase 2 clinical development for congenital and acquired bleeding disorders.

What phase is catridecacog in?

Catridecacog is in Phase 2 clinical development. It is an investigational drug, not yet approved by regulatory authorities. The development program includes eight completed trials, with no active trials currently ongoing, and a total enrollment of 546 participants across those studies.

What clinical trials is catridecacog in?

Catridecacog has been studied in eight completed clinical trials. Notable trials include NCT00056589, a Phase 1 study in patients with congenital factor XIII deficiency, and NCT01082406, NCT01847989, and NCT01848002, which are Phase 1 studies in healthy volunteers. All trials are completed.

Is catridecacog the same as recombinant factor XIII?

Catridecacog is a recombinant factor XIII product, meaning it is a laboratory-made version of the naturally occurring factor XIII protein. It is being developed to treat congenital factor XIII deficiency, a rare bleeding disorder, by providing the missing clotting factor.