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FT-1101

Phase 1

Acute Myeloid Leukemia | Small molecule | Oncology |Novo Nordisk A/S|Last Updated: Nov 21, 2023

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
CONTROLLEDBiomarker
Total Trials1
Total Enrollment94
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT02543879Study of a Novel BET Inhibitor FT-1101 in Patients With Relapsed or Refractory Hematologic MalignanciesPHASE1 COMPLETED 94Sep 1, 2015Mar 1, 2019Nov 21, 20238 United States
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Study Endpoints
Primary Endpoints
Maximum Tolerated Dose (MTD)
Within first 4 weeks of treatment
Dose Limiting Toxicities (DLT)
Within first 4 weeks of treatment
Recommended Phase 2 Dose (RP2D)
Participants to be followed for duration of participation, an expected average of 12 weeks
Secondary Endpoints
Area under the plasma concentration versus time curve (AUC)
PK collected at multiple visits during the first 30 days of treatment
Peak Plasma Concentration (Cmax)
PK collected at multiple visits during the first 30 days of treatment
Time of peak plasma concentration (TMax)
PK collected at multiple visits during the first 30 days of treatment
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Dose Escalation FT-1101EXPERIMENTALFollowing a 3+3 dose escalation strategy, the first cohort of patients will be administered FT-1101 at 10 mg, oral capsules, once weekly on a continuous basis. Subsequent cohorts dose and frequency will be determined by investigators and sponsor following observations of previous cohorts. Dose escalation will continue until the MTD is determined.
Dose Expansion FT-1101EXPERIMENTALOnce the MTD is determined, the Recommended Phase 2 Dose (RP2D) will be identified. 3 Expansion cohorts of up to 20 patients each will be treated with the RP2D of FT-1101
Dose Escalation FT-1101 + azacitidineEXPERIMENTALFollowing a 3+3 dose escalation strategy, the first cohort of AML/MDS patients will be administered FT-1101 at approximately 50% or lower than the MTD identified for the single agent FT-1101. Subsequent cohorts dose will be determined by investigators and sponsor following observations of previous cohorts. Dose escalation will not exceed the dose determined to be the single agent MTD for that schedule.
Dose Expansion FT-1101 + azacitidineEXPERIMENTALOnce the MTD is determined, the Recommended Phase 2 Dose (RP2D) will be identified. 1 Expansion cohorts of up to 20 AML/MDS patients each will be treated with the RP2D of FT-1101 in combination with azacitidine.
Interventions
NameTypeDescription
FT-1101DRUGFT-1101 will be supplied as 5 mg, 20 mg or 100 mg capsules and will be administered per the protocol defined frequency and dose level
AzacitidineDRUGAzacitidine will be administered per site's standard of care
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo
Study Sites8

Key Inclusion Criteria: * Single agent (SA) Dose Escalation: Histologically or cytologically proven acute leukemia or high-risk MDS as defined by the World Health Organization (WHO) criteria and IPSS-R, respectively, that is relapsed or refractory (R/R) to standard therapy or for whom standard trea...

Countries:United States
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