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NLS-2

Phase 3

Narcolepsy Type 1 | Small molecule | Other |NewcelX Ltd.|Last Updated: May 21, 2024

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment48
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT05914194A Eight-Week Study of NLS-2 (Mazindol Extended Release) in Participants With Narcolepsy Type 1PHASE3 NOT YET_RECRUITING 48Jul 15, 2024Jul 30, 2025May 21, 2024 -
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Study Endpoints
Primary Endpoints
Number of cataplexy episodes at Week 8
8 weeks

Cataplexy episodes is a clinical outcome measure that assesses the frequency of cataplexy episodes.

Secondary Endpoints
Patient Reported Outcomes Measurement Information System-Sleep Related Impairment (PROMIS-SRI): change from baseline
8 weeks
Patient Reported Outcomes Measurement Information System-Sleep Disturbance (PROMIS-SD): change from baseline
8 weeks
Epworth Sleepiness Scale (ESS): change from baseline
8 weeks
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Study Design & Arms
AllocationRANDOMIZED
MaskingDOUBLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
NLS-2EXPERIMENTALParticipants will receive a single NLS-2 tablet orally once daily from Day 1 to Day 56 (until the end of Week 8).
PlaceboPLACEBO_COMPARATORParticipants will receive a single NLS-2 placebo matching tablet orally once daily from Day 1 to Day 56 (until the end of Week 8).
Interventions
NameTypeDescription
NLS-2DRUGParticipants will receive NLS-2 tablets orally.
PlaceboDRUGParticipants will receive NLS-2 matching placebo tablets orally.
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Eligibility Criteria
Age Range18 Years — N/A
SexALL
Healthy VolunteersNo

Key Inclusion Criteria: * Adults ≥ 18 years of age at the time of signing the informed consent. * Documented primary diagnosis of Narcolepsy Type 1 (NT1) according to the International Classification of Sleep Disorders-Third Edition (ICSD-3) criteria. * Willing and able to safely discontinue all pr...

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Recent Changes (Last 90 Days)
LOWMay 24, 2026NCT05914194studyFirstPostDate: changed