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Mazindol

Phase 2

Narcolepsy With Cataplexy | Small molecule | Neurology |NewcelX Ltd.|Last Updated: Mar 13, 2023

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDBiomarker
Total Trials1
Total Enrollment52

FDA Designations

No designations recorded

Clinical trial landscape

Mazindol · 3 trials · 6 indications

Phase 2 3
NCT05055024An Open Label Study of NLS-2 (Mazindol Extended Release) in Subjects With NarcolepsyNarcolepsy With Cataplexy
COMPLETED52 Analytics
NCT04923594Four-week Study of the Safety and Efficacy of NLS-2 (Mazindol Extended Release) in the Treatment of NarcolepsyNarcolepsy
COMPLETED67 Analytics
NCT02808104Mazindol Controlled Release in Adults With Attention Deficit Hyperactivity Disorder (ADHD)Attention Deficit Disorder With Hyperactivity
COMPLETED84 Analytics
PHASE2COMPLETED
An Open Label Study of NLS-2 (Mazindol Extended Release) in Subjects With Narcolepsy
Narcolepsy With CataplexyUnlock trial analytics
PHASE2COMPLETED
Four-week Study of the Safety and Efficacy of NLS-2 (Mazindol Extended Release) in the Treatment of Narcolepsy
NarcolepsyUnlock trial analytics
PHASE2COMPLETED
Mazindol Controlled Release in Adults With Attention Deficit Hyperactivity Disorder (ADHD)
Attention Deficit Disorder With HyperactivityUnlock trial analytics

Study Endpoints

Primary Endpoints

To evaluate the safety and tolerability of NLS-2 in adult subjects with narcolepsy type 1 (NT1) or narcolepsy type 2 (NT2)
24 weeks

Summaries of the number and percentage of subjects who experienced Treatment Emergent Adverse Events (TEAEs), TEAEs related to study drug, SAEs, or discontinued study drug or withdrew from the study due to an AE.

Change in ESS Score From Baseline to Week 4
Baseline to Week 4

Change in Epworth Sleepiness Scale (ESS) score from Baseline to Week 4. A negative change from baseline represents improvement in excessive sleepiness. The ESS is a self-administered questionnaire with 8 questions. Each activity is scored on a scale ranging from 0-3, with 0 = would never fall asleep, and 3 = high chance of falling asleep. The total score ranges from 0-24, with a higher number representing an increased propensity for sleepiness.

ADHD Rating Scale
weekly rating up to six weeks

Secondary Endpoints

Subjects Reported Improved on the Patient Global Impression of Change (PGIc) at Week 4
Baseline to Week 4
Clinical Global Improvement Scale
weekly rating up to six weeks
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
NLS-2 (mazindol extended release)EXPERIMENTALNLS-2 (mazindol extended release) administered once a day.
PlaceboPLACEBO_COMPARATORDosed orally, once daily for up to 4 weeks
Mazindol Controlled ReleaseEXPERIMENTALMazindol controlled release taken once daily. Dosage starting at 1 mg increasing or decreasing in increments of 1 mg depending on efficacy and tolerability. Maximum dose during the study is 3 mg taken once daily.

Interventions

NameTypeDescription
MazindolDRUGDrug: NLS-2
mazindol extended releaseDRUGDosed orally, once daily for up to 3 weeks
PlaceboDRUGDosed orally, once daily for up to 4 weeks.
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Eligibility Criteria

Age Range18 Years to 65 Years
SexALL
Healthy VolunteersNo
Study Sites22

Inclusion Criteria: * The subject must complete all Study NLS-1021 study requirements and assessments up to Visit 6; * The subject is able, in the opinion of the Investigator, to receive NLS-2 for the 24-week Treatment Phase of this study; * Biological females of childbearing potential must agree t...

Countries:United States
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Frequently asked questions about Mazindol

What is Mazindol used for?

Mazindol is an investigational small molecule being developed for narcolepsy with cataplexy and attention deficit disorder with hyperactivity. It is a central nervous system agent studied in adult patients. The drug is in Phase 2 clinical development and is not yet approved by the FDA.

Who makes Mazindol?

Mazindol is being developed by NewcelX Ltd., a biopharmaceutical company. The company's stock ticker is NCEL. NewcelX is conducting clinical trials of Mazindol in the United States for neurological conditions including narcolepsy and ADHD.

What phase is Mazindol in?

Mazindol is in Phase 2 clinical development. It is an investigational drug and has not been approved by the FDA. Two Phase 2 trials have been completed, one in ADHD and one in narcolepsy, but the drug remains in clinical development.

What clinical trials is Mazindol in?

Mazindol has been studied in two completed Phase 2 trials. NCT02808104 evaluated Mazindol controlled release in 84 adults with ADHD. NCT05055024 was an open-label study of NLS-2 (Mazindol extended release) in 52 subjects with narcolepsy, including those with cataplexy.

Is Mazindol the same as NLS-2?

Yes, Mazindol is also known as NLS-2 in its extended release formulation. The clinical trial NCT05055024 studied NLS-2 (Mazindol extended release) in subjects with narcolepsy. This alternative name is used in the context of the extended release version of the drug.