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Miransertib

Phase 2

PIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS) | Small molecule | Rare Disease |Merck & Company, Inc.|Last Updated: Feb 7, 2025

Target and mechanism

Molecular targetAKT2, AKT3, AKT1
Target classInhibitor
ModalitySmall molecule

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLED
Total Trials1
Total Enrollment60

FDA Designations

No designations recorded

Clinical trial landscape

Miransertib · 1 trial · 1 indication

Phase 2 1
NCT04980872A Study of the Safety and Tolerability in Participants With PIK3CA-related Overgrowth Spectrum or Proteus Syndrome Who Are Being Treated With Miransertib (MK-7075) in Other Studies (MK-7075-006)PIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS)
ACTIVE NOT_RECRUITING60 Analytics
PHASE2ACTIVE NOT_RECRUITING
A Study of the Safety and Tolerability in Participants With PIK3CA-related Overgrowth Spectrum or Proteus Syndrome Who Are Being Treated With Miransertib (MK-7075) in Other Studies (MK-7075-006)
PIK3CA-Related Overgrowth Spectrum (PROS)/Proteus Syndrome (PS)Unlock trial analytics

Study Endpoints

Primary Endpoints

Number of participants experiencing a Serious Adverse Event (SAE)
Up to approximately 94 months

An SAE is defined as any untoward medical occurrence associated with the use of a drug in a participant, whether or not considered drug related. An SAE can therefore be any such event that results in death, is life-threatening, requires inpatient hospitalization or prolongation of existing hospitalizations, results in persistent or significant disability/incapacity, is a congenital anomaly/birth defect, or is considered by the investigator to be an important medical event.

Number of participants discontinuing study treatment due to an Adverse Event (AE)
Up to approximately 90 months

An AE is defined as any untoward medical occurrence associated with the use of a drug in a participant, whether or not considered drug related. An AE can therefore be any unfavorable and unintended sign (including an abnormal laboratory finding, for example), symptom, or disease temporally associated with the use of a medicinal product and does not imply any judgment about causality.

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Study Design & Arms

AllocationNA
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
MiransertibEXPERIMENTALParticipants with either PROS or PS receive miransertib orally once daily between 5 and 35 mg/m\^2 based on prior approved dosing for up to 96 cycles. A cycle is 28 days long.

Interventions

NameTypeDescription
MiransertibDRUGMiransertib capsules administered orally either 1 hour before or 2 hours after a meal.
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Eligibility Criteria

Age Range2 Years to 120 Years
SexALL
Healthy VolunteersNo
Study Sites11

Inclusion Criteria: * Has PROS or PS and has been screened in Study MK-7075-002 (or has been approved by the Sponsor to screen for MK-7075-002) or is currently being treated with miransertib as part of Study MK-7075-002 (NCT03094832) or ArQule's CU/EAP (NCT03317366) * For males, agrees to be abstin...

Countries:United StatesAustraliaBrazilItalyUnited Kingdom
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Frequently asked questions about Miransertib

What is Miransertib used for?

Miransertib is an investigational small molecule being studied for PIK3CA-Related Overgrowth Spectrum (PROS) and Proteus Syndrome (PS), which are rare diseases. It is currently in Phase 2 clinical development and has not been approved by the FDA.

Who makes Miransertib?

Miransertib is being developed by Merck & Company, Inc., which trades under the ticker MRK. The drug is also known as MK-7075.

What phase is Miransertib in?

Miransertib is in Phase 2 clinical development. It is an investigational drug and has not been approved by the FDA. There is one active Phase 2 trial, which is not yet recruiting participants.

What clinical trials is Miransertib in?

Miransertib is being studied in a Phase 2 trial with the identifier NCT04980872. This trial is active but not recruiting and has an estimated enrollment of 60 participants with PROS or Proteus Syndrome.

Is Miransertib the same as MK-7075?

Yes, Miransertib is also known as MK-7075. The clinical trial NCT04980872 refers to the drug as MK-7075, and it is being studied for the treatment of PIK3CA-Related Overgrowth Spectrum and Proteus Syndrome.