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Birabresib

Phase 1

NUT Midline Carcinoma | Small molecule | Oncology |Merck & Company, Inc.|Last Updated: Jan 26, 2021

Success Probability

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Market & Valuation

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Trial Design

CONTROLLEDBiomarker
Total Trials1
Total Enrollment47

FDA Designations

No designations recorded

Clinical trial landscape

Birabresib · 1 trial · 6 indications

Phase 1 1
NCT02259114A Dose-Finding Study of Birabresib (MK-8628), a Small Molecule Inhibitor of the Bromodomain and Extra-Terminal (BET) Proteins, in Adults With Selected Advanced Solid Tumors (MK-8628-003)NUT Midline Carcinoma
COMPLETED47 Analytics
PHASE1COMPLETED
A Dose-Finding Study of Birabresib (MK-8628), a Small Molecule Inhibitor of the Bromodomain and Extra-Terminal (BET) Proteins, in Adults With Selected Advanced Solid Tumors (MK-8628-003)
NUT Midline CarcinomaUnlock trial analytics

Study Endpoints

Primary Endpoints

Number of Participants Who Experienced a Dose Limiting Toxicity (DLT) During Cycle 1
Up to Cycle 1 Day 21 (Up to 21 days)

A DLT was defined as any of the following toxicities that were considered by the investigator to be related to MK-8628: Hematologic toxicity: Grade 4 hematologic toxicity or febrile neutropenia, Grade 3 neutropenia with infection, Grade 3 thrombocytopenia with bleeding or lasting \>7 days; Non-hematologic toxicity: Grade 3 or 4 non-hematologic toxicity (regardless of duration) unless it was not optimally managed with supportive care, Grade 3 or 4 laboratory abnormality, with or without symptoms, lasting \>48 hours, Intolerable Grade 2 non-hematologic toxicity resulting in study drug discontinuation or delay \>7 days with or without dose reduction, Designated alanine aminotransferase (ALT) or aspartate aminotransferase (AST) liver test abnormalities; Treatment delay \>2 weeks or dose reduction requirement for initiating Cycle 2.

Secondary Endpoints

Number of Participants Who Experienced at Least One Adverse Event (AE)
Up to approximately 17.5 months (Up to 30 days after last dose of study treatment)
Number of Participants Who Discontinued Study Treatment Due to an AE
Up to approximately 16.5 months
Best Overall Response as Assessed in Solid Tumors by Response Evaluation Criteria in Solid Tumors Version 1.1 (RECIST 1.1) or in Castration-resistant Prostate Cancer (CRPC) by Prostate Cancer Clinical Trials Working Group (PCWG2) Response Criteria
Up to approximately 16.5 months
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Study Design & Arms

AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Continuous Dosing RegimenEXPERIMENTALParticipants receive birabresib capsules once daily in a fasted state in the morning on Days 1-21 of each 21-day cycle. Starting dose for dose escalation is 80 mg.
Days 1-7 Dosing RegimenEXPERIMENTALParticipants receive birabresib capsules once daily in a fasted state in the morning on Days 1-7 of each 21-day cycle. Starting dose for dose escalation is 100 mg.

Interventions

NameTypeDescription
BirabresibDRUGBirabresib 10, 20 and/or 40 mg oral capsules
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo

Inclusion Criteria: 1. Signed informed consent obtained prior to initiation of any study-specific procedures and treatment; 2. Histologically or cytologically confirmed diagnosis of one of the following advanced or metastatic solid tumors for which standard therapy either does not exist or has prov...

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Frequently asked questions about Birabresib

What is Birabresib used for in NUT Midline Carcinoma?

Birabresib is an investigational small molecule being studied for the treatment of NUT Midline Carcinoma, a rare and aggressive cancer. It is also being evaluated in other advanced solid tumors, including triple negative breast cancer, non-small cell lung cancer with ALK rearrangement or KRAS mutation, castrate-resistant prostate cancer, and pancreatic ductal adenocarcinoma.

What does Birabresib target?

Birabresib targets bromodomain and extra-terminal (BET) proteins. It is a small molecule inhibitor of these proteins, which play a role in regulating gene expression that can drive tumor growth. By inhibiting BET proteins, Birabresib aims to disrupt cancer cell proliferation.

Who makes Birabresib?

Birabresib is being developed by Merck & Company, Inc., a pharmaceutical company traded on the New York Stock Exchange under the ticker symbol MRK. The drug is also known as MK-8628.

What phase is Birabresib in?

Birabresib is in Phase 1 clinical development. It is an investigational drug, meaning it has not been approved by regulatory authorities and is still being studied in clinical trials to evaluate its safety and efficacy.

What clinical trials is Birabresib in?

Birabresib has been studied in one completed Phase 1 clinical trial, identified as NCT02259114. This dose-finding study enrolled 47 adults with selected advanced solid tumors, including NUT Midline Carcinoma, and was designed to evaluate the safety and tolerability of the drug.

Is Birabresib the same as MK-8628?

Yes, Birabresib is also known as MK-8628. The clinical trial NCT02259114, titled 'A Dose-Finding Study of Birabresib (MK-8628), a Small Molecule Inhibitor of the Bromodomain and Extra-Terminal (BET) Proteins, in Adults With Selected Advanced Solid Tumors,' uses both names to refer to the same drug.