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Afrezza

Phase 3

Diabetes Mellitus, Type 1 | Monoclonal antibody | Metabolic |MannKind Corporation|Last Updated: May 6, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedACTIVE_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment319
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04974528Afrezza® INHALE-1 Study in PediatricsPHASE3 COMPLETED 319Sep 29, 2021Apr 29, 2025May 6, 202539 United States
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Study Endpoints
Primary Endpoints
Change in HbA1c
26 weeks

Change in HbA1c from baseline to Week 26, for noninferiority assessment

Secondary Endpoints
Change in Fasting Plasma Glucose (FPG)
26 weeks
Event rate of pooled level 2 and level 3 hypoglycemia
26 weeks
Change in HbA1c
26 weeks
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Study Design & Arms
AllocationRANDOMIZED
MaskingNONE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Afrezza (Technosphere Insulin) + Basal InsulinEXPERIMENTALIndividualized dose of Afrezza (Technosphere Insulin) for each patient before each meal (breakfast, lunch, and dinner) for 26 weeks. Individualized basal insulin (insulin degludec, insulin glargine or insulin detemir) for each patient.
RAA Injection + Basal InsulinACTIVE_COMPARATORIndividualized dose of RAA injection (insulin aspart, insulin lispro or insulin glulisine) for each patient for 26 weeks. Individualized basal insulin (insulin degludec, insulin glargine or insulin detemir) for each patient.
Interventions
NameTypeDescription
AfrezzaBIOLOGICALPharmaceutical form: powder Route of administration: inhalation
Rapid-acting Insulin AnalogBIOLOGICALPharmaceutical form: clear and colorless solution for injection Route of administration: subcutaneous
Basal InsulinBIOLOGICALPharmaceutical form: solution for injection Route of administration: subcutaneous
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Eligibility Criteria
Age Range4 Years — 17 Years
SexALL
Healthy VolunteersNo
Study Sites39

Inclusion Criteria: * Assent from the pediatric subject, as appropriate, and fully informed consent from the parent(s) or legal guardian, as required by both state and federal laws and the local Institutional Review Board (IRB) * Subjects ≥4 and \<18 years of age * Clinical diagnosis of type 1 diab...

Countries:United States
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