Recent Updates
Recently added Catalysts

AAV2hAQP1: 1 x 10^11 vg/gland

Phase 1

Radiation-Induced Parotid Gland Hypofunction | Small molecule | Oncology |MeiraGTx Holdings plc|Last Updated: Apr 24, 2023

Success Probability
Subscribe to view
Market & Valuation
Subscribe to view
Trial Design
CONTROLLEDDMC
Total Trials1
Total Enrollment24
FDA Designations
RMATORPHAN_DRUGBREAKTHROUGH_THERAPY
Clinical trial landscape

AAV2hAQP1: 1 x 10^11 vg/gland · 1 trial · 3 indications

Phase 1 1
NCT04043104A Phase 1 Open-Label, Dose Escalation Study to Determine the Optimal Dose, Safety, and Activity of AAV2hAQP1 in Subjects With Radiation-Induced Parotid Gland Hypofunction and XerostomiaRadiation-Induced Parotid Gland Hypofunction
COMPLETED24 Analytics
PHASE1COMPLETED
A Phase 1 Open-Label, Dose Escalation Study to Determine the Optimal Dose, Safety, and Activity of AAV2hAQP1 in Subjects With Radiation-Induced Parotid Gland Hypofunction and Xerostomia
Radiation-Induced Parotid Gland HypofunctionUnlock trial analytics
Study Endpoints
Primary Endpoints
The primary outcome is safety of AAV2hAQP1 administered to the parotid gland of adult subjects with radiation-induced xerostomia
one day to one year

Safety will be assessed by number of adverse events occurring with treatment

Unlock Study Endpoints
Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
1 x 10^11 vg/gland (single gland)EXPERIMENTAL -
3 x 10^10 vg/gland (both glands)EXPERIMENTAL -
3 x 10^11 vg/gland (single gland)EXPERIMENTAL -
1 x 10^11 vg/gland (both glands)EXPERIMENTAL -
1 x 10^12 vg/gland (single gland)EXPERIMENTAL -
3 x 10^11 vg/gland (both glands)EXPERIMENTAL -
3 x 10^12 vg/gland (single gland)EXPERIMENTAL -
1 x 10^12 vg/gland (both glands)EXPERIMENTAL -
Interventions
NameTypeDescription
AAV2hAQP1: 1 x 10^11 vg/gland (single gland)DRUGIntra-parotid administration of AAV2hAQP1 via Stensen's duct to a single parotid gland at a dose level of 1 x 10\^11 vg/gland
AAV2hAQP1: 3 x 10^10 vg/gland (both glands)DRUGIntra-parotid administration of AAV2hAQP1 via Stensen's duct to both parotid glands at a dose level of 3 x 10\^10 vg/gland
AAV2hAQP1: 3 x 10^11 vg/gland (single gland)DRUGIntra-parotid administration of AAV2hAQP1 of via Stensen's duct to a single parotid gland at a dose level of 3 x 10\^11 vg/gland
AAV2hAQP1: 1 x 10^11 vg/gland (both glands)DRUGintra-parotid administration of AAV2hAQP1 via Stensen's duct to both parotid glands at a dose level of 1 x 10\^11 vg/gland
AAV2hAQP1: 1 x 10^12 vg/gland (single gland)DRUGIntra-parotid administration of AAV2hAQP1 via Stensen's duct to a single parotid gland at a dose level of 1 x 10\^12 vg/gland
AAV2hAQP1: 3 x 10^11 vg/gland (both glands)DRUGIntra-parotid administration of AAV2hAQP1 via Stensen's duct to both parotid glands at a dose level of 3 x 10\^11 vg/gland
AAV2hAQP1: 3 x 10^12 vg/gland (single gland)DRUGIntra-parotid administration of AAV2hAQP1 via Stensen's duct to a single parotid gland at a dose level of 3 x 10\^12 vg/gland
AAV2hAQP1: 1 x 10^12 vg/gland (both glands)DRUGIntra-parotid administration of AAV2hAQP1 via Stensen's duct to both parotid glands at a dose level of 1 x 10\^12 vg/gland
Unlock Study Design Details
Eligibility Criteria
Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites6

Inclusion Criteria: 1. Male or female subjects ≥18 years of age. 2. History of radiation therapy for head and neck cancer. 3. Abnormal parotid gland function as judged by both absence of unstimulated parotid salivary flow and a stimulated parotid salivary flow in the targeted parotid gland \>0 and ...

Countries:United StatesCanada
Unlock Eligibility Criteria