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Provacel

Phase 1

Myocardial Infarction | Monoclonal antibody | Cardiovascular |Mesoblast Limited|Last Updated: Mar 10, 2020

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment60
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT00114452Safety Study of Adult Mesenchymal Stem Cells (MSC) to Treat Acute Myocardial InfarctionPHASE1 COMPLETED 60Mar 22, 2005Apr 24, 2008Mar 10, 202015 United States
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Study Endpoints
Primary Endpoints
Comparison of treatment adverse event rates between the 0.5, 1.6 and 5.0 million mesenchymal stem cells per kilogram dose cohorts and placebo groups.
6 months
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
Provacel: Cohort 1ACTIVE_COMPARATORex vivo cultured adult mesenchymal stem cells
Provacel: Cohort 2ACTIVE_COMPARATORex vivo cultured adult mesenchymal stem cells
Provacel: Cohort 3ACTIVE_COMPARATORex vivo cultured adult mesenchymal stem cells
Provacel: Cohort 4ACTIVE_COMPARATORex vivo cultured adult mesenchymal stem cells
PlaceboPLACEBO_COMPARATORex vivo cultured adult mesenchymal stem cells
Interventions
NameTypeDescription
ProvacelBIOLOGICALex vivo cultured adult mesenchymal stem cells
PlaceboBIOLOGICALPlacebo
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Eligibility Criteria
Age Range21 Years — 85 Years
SexALL
Healthy VolunteersNo
Study Sites15

Inclusion Criteria: * Male or female between 21 and 85 years old * First heart attack within 1 to 10 days Exclusion Criteria: * Positive for HIV 1 and 2 * Previous heart attack * Pacemaker or other device * Pregnant or breastfeeding * Allergic to cow or pig derived products * Previous bone marrow...

Countries:United States
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