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Liposomal Annamycin

Phase 1

Leukemia, Myeloid, Acute | Small molecule | Oncology |Moleculin Biotech, Inc.|Last Updated: Sep 30, 2025

Success Probability

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Market & Valuation

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Trial Design

UNCONTROLLEDDMC
Total Trials3
Total Enrollment49

FDA Designations

ORPHAN_DRUGFAST_TRACK

Clinical trial landscape

Liposomal Annamycin · 4 trials · 3 indications

Phase 1 4
NCT05319587Study of Liposomal Annamycin in Combination With Cytarabine for the Treatment of Subjects With Acute Myeloid Leukemia (AML)Leukemia, Myeloid, Acute
COMPLETED22 Analytics
NCT04887298Study of Liposomal Annamycin for the Treatment of Subjects with Soft-Tissue Sarcomas (STS) with Pulmonary MetastasesSarcoma,Soft Tissue
COMPLETED36 Analytics
NCT03388749Study of Liposomal Annamycin for the Treatment of Subjects With Acute Myeloid Leukemia (AML)Leukemia, Myeloid, Acute
COMPLETED20 Analytics
NCT03315039Study of Liposomal Annamycin for the Treatment of Subjects With Acute Myeloid Leukemia (AML)Leukemia, Myeloid, Acute
COMPLETED7 Analytics
PHASE1COMPLETED
Study of Liposomal Annamycin in Combination With Cytarabine for the Treatment of Subjects With Acute Myeloid Leukemia (AML)
Leukemia, Myeloid, AcuteUnlock trial analytics
PHASE1COMPLETED
Study of Liposomal Annamycin for the Treatment of Subjects with Soft-Tissue Sarcomas (STS) with Pulmonary Metastases
Sarcoma,Soft TissueUnlock trial analytics
PHASE1COMPLETED
Study of Liposomal Annamycin for the Treatment of Subjects With Acute Myeloid Leukemia (AML)
Leukemia, Myeloid, AcuteUnlock trial analytics
PHASE1COMPLETED
Study of Liposomal Annamycin for the Treatment of Subjects With Acute Myeloid Leukemia (AML)
Leukemia, Myeloid, AcuteUnlock trial analytics

Study Endpoints

Primary Endpoints

Evaluate the safety and identify the MTD/RP2D of L-Annamycin in combination with a standard regimen of cytarabine (Ara-C, cytosine arabinoside)
Day 1 through Day 28

The number of patients who experience dose-limiting toxicities (DLT) will be captured at each dose level of LAnnamycin in order to determine the MTD/RP2D

Dose Limiting Toxicity
21 days

Number of patients with a dose limiting toxicity (DLT) at each dose evaluated

Evaluation of safety and identification of the MTD/RP2D for L-Annamycin
Day 1 through Day 28

The number of patients who experience dose-limiting toxicities (DLT) will be captured at each dose level of L-Annamycin in order to determine the MTD/RP2D

Dose-limiting Toxicity
Day 28

Number of patients with a dose-limiting toxicity (DLT) at each dose evaluated

Secondary Endpoints

Pharmacokinetics - Area under the plasma concentration
Pre-dose and at 0.25, 0.5, 1, 2, 4, 8,12 and 24 hours after the start of liposomal annamycin infusion on Day 1 and Day 3
Anti-leukemic activity
15-35 Days after the start of therapy
Efficacy of L-Annamycin
At the end of every other treatment cycle ( each cycle is 21 days)
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Study Design & Arms

AllocationNA
MaskingNONE
ModelSEQUENTIAL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
Liposomal annamycinEXPERIMENTAL -
Liposomal Annamycin (L-Annamycin)EXPERIMENTAL -

Interventions

NameTypeDescription
Liposomal AnnamycinDRUG2-hour intravenous infusion liposomal annamycin daily for 3 consecutive days followed by 18 days off study drug (i.e., one treatment cycle = 21 days).
CytarabineDRUGAdministered during cycle 1 at a dose of 2.0 g/m2/day by 4 hours IV infusion for 5 consecutive days and this dose will remain constant for all cohorts, including the expansion phase.
Liposomal Annamycin (L-Annamycin)DRUG2-hour intravenous (IV) infusion of L-Annamycin on Day 1 followed by 20 days off of study drug (i.e., 1 treatment cycle= 21 days)
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites9

Inclusion Criteria: 1. The subject has a pathologically confirmed diagnosis of AML by World Health Organization classification. This must be in the form of either a bone marrow aspirate or biopsy or a CBC that demonstrates \>5% myeloblasts. 2. The subject has AML and has not received prior therapy ...

Countries:ItalyPolandUnited States
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Frequently asked questions about Liposomal Annamycin

What is Liposomal Annamycin used for?

Liposomal Annamycin is an investigational small molecule being studied for the treatment of acute myeloid leukemia (AML) and soft tissue sarcoma with pulmonary metastases. It is in Phase 1 clinical development and has not been approved by the FDA.

Who makes Liposomal Annamycin?

Liposomal Annamycin is being developed by Moleculin Biotech, Inc. (NASDAQ: MBRX). The company is conducting clinical trials of the drug for acute myeloid leukemia and soft tissue sarcoma.

What phase is Liposomal Annamycin in?

Liposomal Annamycin is in Phase 1 clinical development. It is investigational and has not been approved by regulatory authorities. The drug has received orphan drug and fast track designations from the FDA.

What clinical trials is Liposomal Annamycin in?

Liposomal Annamycin has been studied in four completed Phase 1 trials. These include NCT03315039 and NCT03388749 for acute myeloid leukemia, NCT04887298 for soft tissue sarcoma with pulmonary metastases, and NCT05319587 combining Liposomal Annamycin with Cytarabine for AML.

Is Liposomal Annamycin the same as Liposomal Annamycin in combination with Cytarabine?

Liposomal Annamycin is also known as Liposomal Annamycin Injection in combination with Cytarabine Injection. The drug is being studied both as a single agent and in combination with Cytarabine for acute myeloid leukemia.