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KB803

Phase 3

Dystrophic Epidermolysis Bullosa | Monoclonal antibody | Dermatology |Krystal Biotech, Inc.|Last Updated: Mar 12, 2026

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
RandomizedDouble-BlindPLACEBO_CONTROLLEDBiomarker
Total Trials1
Total Enrollment16
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT07016750A Study Comparing KB803 and Matched Placebo in Patients With Dystrophic Epidermolysis BullosaPHASE3 RECRUITING 16Jun 20, 2025Dec 1, 2026Mar 12, 20265 United States
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Study Endpoints
Primary Endpoints
To evaluate the safety and tolerability of KB803.
24 weeks

Number of subjects with treatment related adverse events as assessed by CTCAE v5.

To evaluate the effect of ophthalmic KB803 on frequency of corneal abrasion symptoms.
24 weeks

Average number of days per month with corneal abrasion symptoms.

Secondary Endpoints
To evaluate the effect of ophthalmic KB803 on eye pain.
24 weeks
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Study Design & Arms
AllocationRANDOMIZED
MaskingQUADRUPLE
ModelCROSSOVER
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
KB803EXPERIMENTALKB803
PlaceboPLACEBO_COMPARATORVehicle
Interventions
NameTypeDescription
KB803BIOLOGICALOphthalmic suspension of replication-defective, non-integrating herpes simplex virus (HSV-1) expressing the human collagen VII protein
PlaceboDRUGVehicle
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Eligibility Criteria
Age Range6 Months — N/A
SexALL
Healthy VolunteersNo
Study Sites5

Inclusion Criteria: 1. The subject and/or their parent/legal guardian must provide informed consent/assent and must be able to and willing to follow study procedures and instructions. 2. Age 6 months or older at time of informed consent/assent. 3. Confirmed diagnosis of DEB with a mutation in the C...

Countries:United States
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT07016750primaryCompletionDate: changed
LOWMay 24, 2026NCT07016750studyFirstPostDate: changed