Recent Updates
Recently added Catalysts

KB801

Phase 1

Neurotrophic Keratitis | Monoclonal antibody | Ophthalmology |Krystal Biotech, Inc.|Last Updated: Feb 27, 2026

Target and mechanism

Molecular targetHSV-1
Target classViral Vector
ModalityMonoclonal antibody

Success Probability

Subscribe to view

Market & Valuation

Subscribe to view

Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMC
Total Trials1
Total Enrollment60

FDA Designations

No designations recorded

Clinical trial landscape

KB801 · 1 trial · 1 indication

Phase 1 1
NCT06999733A Study Comparing KB801 Verse Placebo in Patients With Stage 2 or 3 Neurotrophic KeratitisNeurotrophic Keratitis
RECRUITING60 Analytics
PHASE1RECRUITING
A Study Comparing KB801 Verse Placebo in Patients With Stage 2 or 3 Neurotrophic Keratitis
Neurotrophic KeratitisUnlock trial analytics

Study Endpoints

Primary Endpoints

To evaluate safety and tolerability of KB801 based upon assessment of adverse events (frequency, severity, relatedness).
8 weeks

Number of subjects with treatment related adverse events as assessed by CTCAE v5.

To evaluate the effect of KB801 on complete healing of the Persistent Corneal Epithelial Defect (PCED) in subjects with Stage 2 or Stage 3 NK
8 weeks

Proportion of subjects receiving KB801 exhibiting complete PCED closure at Week 8 compared to those receiving placebo.

Secondary Endpoints

To evaluate the effect of KB801 on complete healing of the PCED in subjects with Stage 2 or 3 NK
10 weeks
To evaluate the effect of KB801 on conventional healing of the PCED in subjects with Stage 2 or 3 NK
10 weeks
Unlock Study Endpoints

Study Design & Arms

AllocationRANDOMIZED
MaskingTRIPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
KB801EXPERIMENTAL -
PlaceboPLACEBO_COMPARATOR -

Interventions

NameTypeDescription
KB801BIOLOGICALOphthalmic suspension of replication-defective, non-integrating herpes simplex virus type 1 (HSV-1)-based vector delivering functional, full-length human nerve growth factor (NGF)
PlaceboDRUGVehicle
Unlock Study Design Details

Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites9

Inclusion Criteria: 1. The subject must have read, understood, and signed an Institutional Review Board (IRB) approved Informed Consent Form and must be willing and able to comply with study procedures and instructions. 2. Aged ≥ 18 years at the time of informed consent. 3. Diagnosis of Stage 2 or ...

Countries:United States
Unlock Eligibility Criteria

Frequently asked questions about KB801

What is KB801 used for?

KB801 is an investigational monoclonal antibody being developed for the treatment of neurotrophic keratitis, a degenerative corneal disease. It is currently in Phase 1 clinical development and is not yet approved by the FDA.

What does KB801 target?

KB801 targets HSV-1, the herpes simplex virus type 1, using a viral vector delivery system. The drug is designed to address the underlying viral cause of neurotrophic keratitis, a condition that affects the cornea of the eye.

Who makes KB801?

KB801 is being developed by Krystal Biotech, Inc., a biopharmaceutical company traded on the NASDAQ under the ticker symbol KRYS. The company is conducting clinical trials to evaluate the safety and efficacy of KB801 in patients with neurotrophic keratitis.

What phase is KB801 in?

KB801 is currently in Phase 1 clinical development. It is an investigational drug, meaning it has not been approved by regulatory authorities. The ongoing Phase 1 trial is recruiting patients to assess the treatment's safety and preliminary efficacy.

What clinical trials is KB801 in?

KB801 is being evaluated in a Phase 1 clinical trial with the identifier NCT06999733. This randomized, double-blind, placebo-controlled study is recruiting approximately 60 patients with Stage 2 or 3 neurotrophic keratitis in the United States.

Is KB801 the same as any other drug?

KB801 is a distinct investigational drug developed by Krystal Biotech. It is not known to be the same as any other approved or investigational medication. Its unique mechanism targets HSV-1 using a viral vector approach for the treatment of neurotrophic keratitis.