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KB301

Phase 1

Skin Roughness | Monoclonal antibody | Dermatology |Krystal Biotech, Inc.|Last Updated: May 13, 2025

Success Probability
Approval Probability 71%
TA Base Rate26%
Adjusted LOA41%
ML RiskLOW_RISK
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Market & Valuation
rNPV $3.2B
Market Size $9.4B
Revenue Basis $1.6B
Competitors 6
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Trial Design
PLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment85
FDA Designations
No designations recorded
Clinical Trials (1)
NCT IDTitlePhaseStatusEnrollmentVelocityDesignStartCompletionLast UpdatedSitesCountries
NCT04540900A Phase I Study of KB301, a Replication-Incompetent, Non-Integrating Vector Expressing Human Type III Collagen (COL3) for the Treatment of Superficial Skin DepressionsPHASE1 ACTIVE NOT_RECRUITING 85Oct 7, 2020May 31, 2029May 13, 20254 United States
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Study Endpoints
Primary Endpoints
Assessment of the safety profile of KB301 by recording adverse events using MedDRA System Organ Class and Preferred Term and collection of other clinical study procedures.
4 months

The primary outcome will look at the safety and tolerability of KB301 through the collection and quantification of adverse events, physical examinations, vital signs and clinical laboratory tests.

Secondary Endpoints
Evaluation of COL3A1 transgene expression 2-days post-dose.
12 months
Assessment of skin roughness as compared to baseline, using the Skin Roughness Scale (SRS).
65 Days
Assessment of fine line improvement as compared to baseline, using the Fine Lines Scale (FLS).
65 Days
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Study Design & Arms
AllocationNON_RANDOMIZED
MaskingNONE
ModelSINGLE_GROUP
PurposeTREATMENT
Treatment Arms
ArmTypeDescription
KB301ACTIVE_COMPARATORnon-integrating HSV-1 vector expressing human type III collagen
PlaceboPLACEBO_COMPARATORsterile isotonic saline
Interventions
NameTypeDescription
KB301BIOLOGICALnon-integrating HSV-1 vector expressing human type III collagen
PlaceboOTHERsterile isotonic saline
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Eligibility Criteria
Age Range18 Years — 75 Years
SexALL
Healthy VolunteersYes
Study Sites4

Inclusion Criteria: 1. Male or female in good general health, as determined by the investigator, aged ≥18 and ≤75 at the time of consent (only females for Cohort 4) 2. Regions of suitable skin to be selected as Target Area(s), as determined by a physical examination conducted by the investigator du...

Countries:United States
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Recent Changes (Last 90 Days)
LOWMay 26, 2026NCT04540900primaryCompletionDate: changed
LOWMay 24, 2026NCT04540900studyFirstPostDate: changed