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Crofelemer

Phase 3

Cancer Therapy-Related Diarrhea | Small molecule | Oncology |Jaguar Health, Inc.|Last Updated: Jul 26, 2024

Target and mechanism

Molecular targetANO1, CFTR
Target classBlocker
ModalitySmall molecule

Also known as Crofelemer Powder for Oral Solution, Crofelemer for

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLED
Total Trials1
Total Enrollment287

FDA Designations

BREAKTHROUGH_THERAPY

Clinical trial landscape

Crofelemer · 2 trials · 7 indications

Phase 3 1Phase 2 1
NCT04538625Prophylaxis of Diarrhea in Adult Cancer Patients Receiving Targeted Cancer TherapyCancer Therapy-Related Diarrhea
COMPLETED287 Analytics
PHASE3COMPLETED
Prophylaxis of Diarrhea in Adult Cancer Patients Receiving Targeted Cancer Therapy
Cancer Therapy-Related DiarrheaUnlock trial analytics

Study Endpoints

Primary Endpoints

Frequency of Number of Loose/watery Stools
For the entire 12-week double-blind placebo-controlled treatment period (The Stage 1 Primary Treatment Phase).

The frequency of diarrhea as measured by the average number of loose/watery stools per week will be evaluated as a continuous endpoint.

Diarrhea for >= 2 Consecutive Days
Cycle 1, Cycle 2 (each cycle is 21 days)

Percentage of participants with any grade (based on CTCAE 4.0) diarrhea lasting 2 or more consecutive days during cycles 1 and 2 of chemotherapy.

Secondary Endpoints

Proportion of Durable, Clinical Responders
Initial 12-week (Stage 1) period of the study.
Maximum Number of Weekly Loose/Watery Stools
Initial 12-week (Stage 1) period of the study.
Fecal Incontinence
Initial 12-week (Stage 1) period of the study.
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposePREVENTION

Treatment Arms

ArmTypeDescription
PlaceboPLACEBO_COMPARATORSubjects randomized to the placebo arm, will receive oral doses of matching placebo tablets twice daily with or without food.
CrofelemerEXPERIMENTALSubjects randomized to the crofelemer arm, will receive oral doses of crofelemer 125mg delayed-release tablets twice daily with or without food.
ControlNO_INTERVENTIONPatients on the control arm will be on the study for cycles 1-3 of THP or TCHP. Patients on the control arm will not receive crofelemer at any time on this study.

Interventions

NameTypeDescription
Crofelemer 125 MG [Mytesi]DRUGRandomized, Double-blind, Placebo-controlled, two arm trial
PlaceboDRUGMatching placebo tablets
CrofelemerDRUGCrofelemer 125 mg BID during cycles 1-2 of THP or TCHP
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersNo
Study Sites52

Inclusion Criteria: * 1\. Patients to receive targeted cancer therapy drugs that have a reported an all grade diarrhea incidence of 50% or higher (e.g., tyrosine kinase inhibitors, cdk inhibitors, anti-EGFR, etc., for treatment of solid tumors. 2\. Patients able to provide written informed conse...

Countries:United StatesArgentinaGeorgiaSerbiaTaiwan
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Frequently asked questions about Crofelemer

What is Crofelemer used for?

Crofelemer is an investigational small molecule being studied for Short Bowel Syndrome, Cancer Therapy-Related Diarrhea, Microvillus Inclusion Disease, and Breast Cancer. It is in Phase 2 clinical development for these indications. Crofelemer is not FDA approved and remains under investigation.

What does Crofelemer target?

Crofelemer targets and blocks two ion channels, ANO1 and CFTR. By blocking these channels, it is being studied for its potential to reduce fluid secretion in the gut, which may help manage diarrhea associated with various conditions.

Who makes Crofelemer?

Crofelemer is being developed by Jaguar Health, Inc., a company traded on NASDAQ under the ticker JAGX. The company is conducting clinical trials to evaluate the drug's safety and efficacy across multiple patient populations.

What phase is Crofelemer in?

Crofelemer is in Phase 2 clinical development. It is an investigational drug and has not received FDA approval. Active trials are evaluating it for Short Bowel Syndrome and Microvillus Inclusion Disease, while completed trials have studied it in breast cancer and cancer therapy-related diarrhea.

What clinical trials is Crofelemer in?

Crofelemer has been studied in several trials. NCT02910219 was a completed Phase 2 trial in HER2 positive breast cancer patients. NCT04538625 was a completed Phase 3 trial for cancer therapy-related diarrhea. NCT06721871 is an active Phase 2 trial in pediatric Microvillus Inclusion Disease, and NCT06904872 is a recruiting Phase 2 trial in Short Bowel Syndrome.

Is Crofelemer the same as Crofelemer Powder for Oral Solution?

Yes, Crofelemer is also known as Crofelemer Powder for Oral Solution. This formulation is being tested in clinical trials, including a study of ascending doses in pediatric patients with Microvillus Inclusion Disease.