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APX3330

Phase 2

Diabetic Retinopathy | Small molecule | Ophthalmology |Opus Genetics, Inc.|Last Updated: Feb 27, 2023

Success Probability

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Market & Valuation

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Trial Design

RandomizedDouble-BlindPLACEBO_CONTROLLEDDMCBiomarker
Total Trials1
Total Enrollment103

FDA Designations

No designations recorded

Clinical trial landscape

APX3330 · 1 trial · 4 indications

Phase 2 1
NCT04692688Study of the Safety and Efficacy of APX3330 in Diabetic RetinopathyDiabetic Retinopathy
COMPLETED103 Analytics
PHASE2COMPLETED
Study of the Safety and Efficacy of APX3330 in Diabetic Retinopathy
Diabetic RetinopathyUnlock trial analytics

Study Endpoints

Primary Endpoints

Percent of Subjects with an improvement in Diabetic Retinopathy Severity Score (DRSS)
24 Weeks

Percent of subjects with a ≥ 2-step improvement in DRSS in the study eye

Secondary Endpoints

Percent of Subjects with change in Diabetic Retinopathy Severity Scale (DRSS) Scores
Up to 24 Weeks
Mean Change in Diabetic Retinopathy Severity Scale (DRSS) Score
24 Weeks
Percent of Subjects without DR/DME Disease Progression
24 Weeks
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Study Design & Arms

AllocationRANDOMIZED
MaskingQUADRUPLE
ModelPARALLEL
PurposeTREATMENT

Treatment Arms

ArmTypeDescription
APX3330EXPERIMENTALFive 120 mg tablets will be taken by mouth as follows: 3 tablets every morning and 2 tablets every evening.
PlaceboPLACEBO_COMPARATORFive 120 mg tablets will be taken by mouth as follows: 3 tablets every morning and 2 tablets every evening.

Interventions

NameTypeDescription
APX3330DRUGAPX3330, a small-molecule oral tablet, is a Ref-1 inhibitor that can potentially reduce proinflammatory and hypoxic signaling that contributes to several eye diseases.
PlaceboDRUGPlacebo tablets are identical to APX3330 tablets except for the absence of the active pharmaceutical ingredient.
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Eligibility Criteria

Age Range18 Years to N/A
SexALL
Healthy VolunteersYes
Study Sites24

Inclusion Criteria: 1. Males or non-pregnant females ≥ 18 years of age 2. At least one eye with DR graded at least moderately severe to severe NPDR or mild PDR (corresponding to DRSS 47, 53, or 61) 3. BCVA assessed by ETDRS protocol letters score of ≥ 60 letters (Snellen equivalent ≥ 20/63) 4. Body...

Countries:United States
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Frequently asked questions about APX3330

What is APX3330 used for?

APX3330 is an investigational small molecule being developed for diabetic retinopathy, including diabetic macular edema, non-proliferative diabetic retinopathy (NPDR), and proliferative diabetic retinopathy (PDR). It is currently in Phase 2 clinical development and is not yet approved by the FDA.

Who makes APX3330?

APX3330 is being developed by Opus Genetics, Inc., a biopharmaceutical company traded on the stock exchange under the ticker symbol IRD. The company is conducting clinical trials to evaluate the safety and efficacy of APX3330 in patients with diabetic retinopathy.

What phase is APX3330 in?

APX3330 is in Phase 2 clinical development. A Phase 2 clinical trial has been completed, and the drug is not yet approved by the FDA. It remains an investigational agent under evaluation for the treatment of diabetic retinopathy.

What clinical trials is APX3330 in?

APX3330 has one completed Phase 2 clinical trial, identified as NCT04692688, titled 'Study of the Safety and Efficacy of APX3330 in Diabetic Retinopathy.' The trial enrolled 103 participants in the United States and included healthy volunteers.

Is APX3330 FDA approved?

No, APX3330 is not FDA approved. It is an investigational drug currently in Phase 2 clinical development. The completed Phase 2 trial was designed to evaluate its safety and efficacy, but the drug has not yet received regulatory approval for any indication.